ETEPLIRSEN

Search structure
Trade Names:
Synonyms:
Status: Approved (2016)
Entry Type: Oligonucleotide
Molecule Category: UNKNOWN
ATC: M09AX06
UNII: AIW6036FAS

Pharmacology

Action Mechanism of Action Reference
POSITIVE MODULATOR Dystrophin pre-mRNA positive modulator Other PubMed

Indications

Mesh Heading Maximum Phase Mesh ID Reference
Muscular Dystrophy, Duchenne 4 D020388 ClinicalTrials

Adverse Reactions

SOC By Demographic Distribution
System Organ Classification (SOC)
Relative Frequency (%)
General disorders and administration site conditions
17.48
Respiratory, thoracic and mediastinal disorders
13.16
Injury, poisoning and procedural complications
12.87
Infections and infestations
7.3
Skin and subcutaneous tissue disorders
6.72
Vascular disorders
6.63
Gastrointestinal disorders
5.86
Cardiac disorders
5.48
Nervous system disorders
5.38
Psychiatric disorders
5.38
Investigations
4.9
Musculoskeletal and connective tissue disorders
3.94

Cross References

Resources Reference
CAS NUMBER 1173755-55-9
ChEMBL CHEMBL2108278
FDA SRS AIW6036FAS
Guide to Pharmacology 7534
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