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Total: 27
Small molecule
Approved
OTHER; PEDIATRICS; RESPIRATORY
DENTAL; INHALATION; INJECTION; INTRA-ARTICULAR; INTRAMUSCULAR; INTRAVITREAL; NASAL; SUSPENSION; TOPICAL
Fibroma; Hearing Loss; Mucositis; Neuroma, Acoustic; Papilledema; Rotator Cuff Injuries; Tendon Entrapment; Alopecia Areata; Breast Neoplasms; Cataract; Complex Regional Pain Syndromes; Dermatitis, Atopic; Glaucoma; Hand Dermatoses; Humeral Fractures; Keloid; Lichen Planus; Pemphigoid, Benign Mucous Membrane; Psoriasis; Shoulder Pain; Ulnar Neuropathies; Uveal Melanoma; Uveomeningoencephalitic Syndrome; Vitiligo; Wet Macular Degeneration; Chalazion; Choroidal Neovascularization; Cough; Cystitis, Interstitial; Diabetic Retinopathy; Dupuytren Contracture; Eye Injuries; Lichen Planus, Oral; Macular Degeneration; Macular Edema; Optic Neuropathy, Ischemic; Osteoarthritis, Hip; Osteoarthritis, Knee; Otitis Media with Effusion; Pemphigus; Radiculopathy; Retinal Vein Occlusion; Rhinitis; Tendinopathy; Uveitis; Vitreoretinopathy, Proliferative; Anemia; Arthritis, Gouty; Arthritis, Rheumatoid; Asthma; Bursitis; Dermatitis; Multiple Sclerosis; Mycoses; Nasal Obstruction; Osteoarthritis; Pain; Rhinitis, Allergic, Seasonal; Serum Sickness; Skin Diseases; Tennis Elbow; Tenosynovitis; Tuberculosis, Pulmonary; Wounds and Injuries
Glucocorticoid receptor agonist
Small molecule
Approved
OTHER; PEDIATRICS
INHALATION; INJECTION; INTRAMUSCULAR; INTRAVENOUS; ORAL
Unknown
Unknown
Small molecule
Approved
NEUROLOGY DRUGS & NERVOUS SYSTEM; OTHER; PEDIATRICS
INTRAVENOUS; ORAL
Hepatitis B, Chronic; Parkinson Disease; Severe Acute Respiratory Syndrome; Cocaine-Related Disorders; Epilepsy, Reflex; HIV Infections; Nausea; Substance-Related Disorders; Anxiety; Dementia; Depressive Disorder; Schizophrenia; Bipolar Disorder; Epilepsies, Partial; Epilepsy; Glossopharyngeal Nerve Diseases; Seizures; Trigeminal Neuralgia
Sodium channel alpha subunit blocker
Small molecule
Approved
IMMUNE SYSTEM; OTHER; PEDIATRICS
ORAL
Astrocytoma; Brain Neoplasms; Central Serous Chorioretinopathy; Cholangitis, Sclerosing; Diarrhea; Glioblastoma; Inflammation; Obesity; Obesity, Morbid; Osteomyelitis; Postoperative Complications; Pregnancy; Prostatic Neoplasms, Castration-Resistant; Tooth Diseases; Asthma; Bacteremia; Buruli Ulcer; Chlamydia Infections; Colitis, Ulcerative; Head and Neck Neoplasms; Lymphoma; Lymphoma, B-Cell, Marginal Zone; Mastitis; Periapical Periodontitis; Periodontal Diseases; Pneumonia, Bacterial; Pseudomyxoma Peritonei; Tuberculosis; Tuberculosis, Pulmonary; Vaginosis, Bacterial; Bronchitis; Bronchitis, Chronic; Cholecystitis; Clostridium Infections; Communicable Diseases; Cystitis, Hemorrhagic; Dyspepsia; Endocarditis; Enterobacteriaceae Infections; Fever; Gastritis; Helicobacter Infections; Hemorrhage; Hepatitis, Alcoholic; Hernia; Hypersensitivity; Influenza, Human; Liver Diseases, Alcoholic; Low Back Pain; Lymphoma, Non-Hodgkin; Malaria, Falciparum; Malnutrition; Neutropenia; Otitis Media, Suppurative; Pain; Periodontitis; Pyelonephritis; Severe Acute Respiratory Syndrome; Stomach Ulcer; Urinary Bladder Neoplasms; Bacterial Infections; Duodenal Ulcer; Gonorrhea; Infections; Otitis Media; Pharyngitis; Pneumonia; Respiratory Tract Infections; Sinusitis; Soft Tissue Infections; Tonsillitis; Urinary Tract Infections
Bacterial penicillin-binding protein inhibitor
Protein
Approved
DIABETES DRUGS & ENDOCRINOLOGY; OTHER; PEDIATRICS
INJECTION
Unknown
Growth hormone-releasing hormone receptor agonist
Small molecule
Approved
ENT; EYE; OTHER; PEDIATRICS; PREGNANCY AND GYNECOLOGY
INJECTION; OPHTHALMIC; ORAL; OTIC
Hearing Loss; Osteomyelitis; Conjunctivitis, Bacterial; Diabetic Foot; Glaucoma; Glaucoma, Open-Angle; Ocular Hypertension; Otitis Media; Pelvic Inflammatory Disease; Urinary Tract Infections; Acne Vulgaris; Bacterial Infections; Bronchitis, Chronic; Corneal Ulcer; Eye Infections; Infections; Otitis Externa
Bacterial DNA gyrase inhibitor
Protein
Approved
DIABETES DRUGS & ENDOCRINOLOGY; OTHER; PEDIATRICS
INJECTION; SUBCUTANEOUS
Prostatic Neoplasms
Gonadotropin-releasing hormone receptor agonist
Small molecule
Approved
IMMUNE SYSTEM; NEUROLOGY DRUGS & NERVOUS SYSTEM; OTHER; PEDIATRICS
ORAL
Alopecia; Child Development Disorders, Pervasive; Glioblastoma; Premature Birth; Psychotic Disorders; Abortion, Spontaneous; Anemia, Sickle Cell; Breast Neoplasms; HIV Infections; Hyperemesis Gravidarum; Intervertebral Disc Displacement; Low Back Pain; Marijuana Abuse; Mucositis; Multiple Sclerosis; Neoplasms; Paget Disease, Extramammary; Peripheral Nervous System Diseases; Postoperative Complications; Prostatic Neoplasms, Castration-Resistant; Rotator Cuff Injuries; Sleep Wake Disorders; Substance-Related Disorders; Substance Withdrawal Syndrome; Tinnitus; Tobacco Use Disorder; Urinary Bladder Neoplasms; Wounds and Injuries; Alcohol Drinking; Alcoholism; Anxiety; Azoospermia; Brain Injuries; Carpal Tunnel Syndrome; Chronic Pain; Cystitis, Interstitial; Delirium; Dementia; Depressive Disorder; Diabetic Neuropathies; Dyspepsia; Epilepsies, Partial; Fibromyalgia; Head and Neck Neoplasms; Herpes Zoster; Hot Flashes; Intervertebral Disc Degeneration; Liver Cirrhosis; Lung Diseases; Neuralgia; Opioid-Related Disorders; Oropharyngeal Neoplasms; Pain; Pelvic Organ Prolapse; Postoperative Nausea and Vomiting; Pruritus; Schizophrenia; Scoliosis; Sleep Initiation and Maintenance Disorders; Tremor; Vomiting; Epilepsy; Neuralgia, Postherpetic; Restless Legs Syndrome; Seizures
Voltage-gated calcium channel modulator
Small molecule
Approved
DIABETES DRUGS & ENDOCRINOLOGY; OTHER; PEDIATRICS
ORAL
Acidosis, Lactic; Acquired Immunodeficiency Syndrome; AIDS-Associated Nephropathy; AIDS Dementia Complex; HIV Infections; Virus Diseases
Human immunodeficiency virus type 1 reverse transcriptase inhibitor
Small molecule
Approved
IMMUNE SYSTEM; OTHER; PEDIATRICS
ORAL
Amyotrophic Lateral Sclerosis; Anus Neoplasms; Erectile Dysfunction; Glioblastoma; Glioma; Hypertension; Hypertension, Pulmonary; Insulin Resistance; Kidney Diseases; Liver Diseases; Malaria; Neoplasm Metastasis; Prostatic Neoplasms; Prostatic Neoplasms, Castration-Resistant; Respiratory Distress Syndrome; Tuberculosis; Hepatitis B, Chronic; Mycobacterium avium-intracellulare Infection; Neoplasms; Post-Acute COVID-19 Syndrome; Pregnancy; Sarcoma; Sarcoma, Kaposi; Acquired Immunodeficiency Syndrome; Coronavirus Infections; Hepatitis D; Infections; Influenza, Human; Pneumonia; Severe Acute Respiratory Syndrome; Hepatitis C; Hepatitis C, Chronic; HIV Infections; Virus Diseases
Cytochrome P450 3A inhibitor
Small molecule
Approved
NEUROLOGY DRUGS & NERVOUS SYSTEM; OTHER; PEDIATRICS
ORAL
Bulimia Nervosa; Cognitive Dysfunction; Feeding and Eating Disorders; Hernias, Diaphragmatic, Congenital; HIV Infections; Liver Diseases; Alcohol Drinking; Amphetamine-Related Disorders; Brain Ischemia; Deafness; Diabetes Mellitus; Hearing Loss, Sudden; Marijuana Abuse; Multiple Sclerosis; Parkinson Disease; Sciatica; Stress Disorders, Post-Traumatic; Alcoholism; Anxiety; Bipolar Disorder; Bulimia; Cocaine-Related Disorders; Dementia; Depressive Disorder; Diabetes Mellitus, Type 2; Epilepsies, Partial; Epilepsy, Tonic-Clonic; Essential Tremor; Gambling; Headache; Hyperlipidemias; Hypertension; Hypertriglyceridemia; Metabolic Syndrome; Mood Disorders; Obesity; Obsessive-Compulsive Disorder; Pain; Prader-Willi Syndrome; Schizophrenia; Smoking Cessation; Tobacco Use Disorder; Tourette Syndrome; Epilepsy; Lennox Gastaut Syndrome; Migraine Disorders; Seizures
Carbonic anhydrase II inhibitor
Unknown
Approved
DERMATOLOGY; IMMUNE SYSTEM; OTHER; PEDIATRICS
ORAL; TOPICAL
Alcoholism; Infections; Leishmaniasis; Triple Negative Breast Neoplasms; Acne Vulgaris; Anosmia; Dengue; Dermatitis, Atopic; Onchocerciasis, Ocular; Severe Dengue; Trichuriasis; Blepharitis; Elephantiasis, Filarial; Influenza, Human; Malaria; Pneumonia; Severe Acute Respiratory Syndrome; Helminthiasis; Lice Infestations; Onchocerciasis; Rosacea; Strongyloidiasis
Glutamate-gated chloride channel modulator
Small molecule
Approved
NEUROLOGY DRUGS & NERVOUS SYSTEM; OTHER; PEDIATRICS
ORAL
Neoplasms; Multiple Sclerosis; Aggression; Anxiety; Dementia; Depressive Disorder; Epilepsies, Partial; Neuralgia; Psychomotor Agitation; Schizophrenia; Epilepsy; Seizures
Sodium channel alpha subunit blocker
Small molecule
Approved
IMMUNE SYSTEM; OTHER; PEDIATRICS
ORAL
HIV Infections; Irritable Bowel Syndrome; Kidney Diseases; Liver Diseases; Bronchiolitis; Crohn Disease; Diabetes Mellitus, Type 2; Gastroenteritis; Hepatitis B, Chronic; Hepatitis C; Hepatitis C, Chronic; Malnutrition; Periodontitis; Sexually Transmitted Diseases; Tuberculosis; Arthritis, Rheumatoid; Brain Diseases; Clostridium Infections; Cryptosporidiosis; Dyspepsia; Enterocolitis, Pseudomembranous; Helicobacter Infections; Influenza, Human; Peritonitis; Respiratory Tract Diseases; Severe Acute Respiratory Syndrome; Amebiasis; Diarrhea
Pyruvate:ferredoxin oxidoreductase inhibitor
Small molecule
Approved
OTHER; PEDIATRICS
ORAL
Albinism; Alkaptonuria; Tyrosinemias
4-hydroxyphenylpyruvate dioxygenase inhibitor
Small molecule
Approved
NEUROLOGY DRUGS & NERVOUS SYSTEM; OTHER; PEDIATRICS
ORAL
Neuralgia; Epilepsy; Dementia; Depressive Disorder; Epilepsia Partialis Continua; Low Back Pain; Pain; Schizophrenia; Anxiety; Lennox Gastaut Syndrome; Seizures
GABA-A receptor; anion channel positive allosteric modulator
Small molecule
Approved
OTHER; PEDIATRICS
ORAL
Hemorrhage; HIV Infections; Virus Diseases
Human immunodeficiency virus type 1 protease inhibitor
Enzyme
Approved
OTHER; PEDIATRICS
IV (INFUSION)
Glycogen Storage Disease; Glycogen Storage Disease Type II
Starch hydrolytic enzyme
Small molecule
Approved
OTHER; PEDIATRICS; RESPIRATORY
INHALATION; NASAL
Pulmonary Disease, Chronic Obstructive; Chronic Disease; Hypersensitivity; Respiratory Tract Diseases; Severe Acute Respiratory Syndrome; Asthma; Lung Diseases, Obstructive; Nasal Obstruction; Rhinitis, Allergic, Perennial; Rhinitis, Allergic, Seasonal
Glucocorticoid receptor agonist
Small molecule
Approved
NEUROLOGY DRUGS & NERVOUS SYSTEM; OTHER; PEDIATRICS
ORAL
Pain; Epilepsy; Lennox Gastaut Syndrome; Seizures
Sodium channel alpha subunit blocker
Small molecule
Approved
OTHER; PEDIATRICS
ORAL
Tourette Syndrome; Alcoholism; Amphetamine-Related Disorders; Cocaine-Related Disorders; Obesity; Tuberous Sclerosis; Epilepsies, Partial; Epilepsy; Epilepsy, Complex Partial; Spasms, Infantile
Gamma-amino-N-butyrate transaminase inhibitor
Small molecule
Approved
NEUROLOGY DRUGS & NERVOUS SYSTEM; OTHER; PEDIATRICS
ORAL
Alcoholism; Bipolar Disorder; Depressive Disorder, Major; Torticollis; Amyotrophic Lateral Sclerosis; Diabetic Neuropathies; Essential Tremor; Migraine Disorders; Neuralgia; Small Fiber Neuropathy; Epilepsy, Tonic-Clonic; Lennox Gastaut Syndrome; Parkinson Disease; Epilepsies, Partial; Epilepsy; Seizures
Glutamate receptor ionotropic AMPA antagonist
Unknown
Approved
PEDIATRICS
INTRATRACHEAL
Cystic Fibrosis; Respiratory Distress Syndrome; Respiratory Distress Syndrome, Newborn; Respiratory Insufficiency; Meconium Aspiration Syndrome
Surfactant agent
Enzyme
Approved
PEDIATRICS
INJECTION
Mucopolysaccharidoses; Mucopolysaccharidosis IV
Chondroitin-6-sulfate hydrolytic enzyme
Combination
Approved
OTHER; PEDIATRICS; RESPIRATORY
INHALATION
Unknown
Unknown
Combination
Approved
OTHER; PEDIATRICS
TOPICAL
Unknown
Unknown
Combination
Approved
OTHER; PEDIATRICS
INJECTION
Unknown
Unknown