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GOLODIRSEN
Search structure
Synonyms:
Golodirsen
NG-12-0163
SRP-4053
Vyondys 53
Status:
Approved (2019)
Entry Type:
Oligonucleotide
Molecule Category:
UNKNOWN
ATC:
M09AX08
UNII:
033072U4MZ
Pharmacology
Action
Mechanism of Action
Reference
POSITIVE MODULATOR
Dystrophin pre-mRNA positive modulator
Other
Other
Other
Indications
Mesh Heading
Maximum Phase
Mesh ID
Reference
Muscular Dystrophy, Duchenne
4
D020388
FDA
Cross References
Resources
Reference
CAS NUMBER
1422959-91-8
ChEMBL
CHEMBL4297762
FDA SRS
033072U4MZ
CONTENTS
Structure
Indications
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SubStructure
Threshold (%) >=
70