| Synonyms: | |
| Status: | Phase 3 |
| Entry Type: | Protein |
| Molecule Category: | UNKNOWN |
| UNII: | OMD1OJM5L7 |
Indications
| Mesh Heading | Maximum Phase | Mesh ID | Reference |
|---|---|---|---|
| Hemophilia B | 3 | D002836 | ClinicalTrials |
| Niemann-Pick Disease, Type C | 2 | D052556 | ClinicalTrials |
| Sandhoff Disease | 2 | D012497 | ClinicalTrials |
| Tay-Sachs Disease | 2 | D013661 | ClinicalTrials |
Cross References
| Resources | Reference |
|---|---|
| ChEMBL | CHEMBL3039538 |
| FDA SRS | OMD1OJM5L7 |
CONTENTS