Synonyms:
Status: Phase 3
Entry Type: Gene
Molecule Category: UNKNOWN
ATC: M09AX09
UNII: MLU3LU3EVV

Pharmacology

Action Mechanism of Action Reference
EXOGENOUS GENE Survival motor neuron protein exogenous gene

Indications

Mesh Heading Maximum Phase Mesh ID Reference
Muscular Atrophy, Spinal 4 D009134 ClinicalTrials
Muscular Atrophy, Spinal 4 D009134 ClinicalTrials
Spinal Muscular Atrophies of Childhood 3 D014897 ClinicalTrials
Spinal Muscular Atrophies of Childhood 3 D014897 ClinicalTrials

Cross References

Resources Reference
ChEMBL CHEMBL4297240
FDA SRS MLU3LU3EVV