| Synonyms: | |
| Status: | Phase 3 |
| Entry Type: | Gene |
| Molecule Category: | UNKNOWN |
| ATC: | M09AX09 |
| UNII: | MLU3LU3EVV |
| Action | Mechanism of Action | Reference |
|---|---|---|
| EXOGENOUS GENE | Survival motor neuron protein exogenous gene |
| Mesh Heading | Maximum Phase | Mesh ID | Reference |
|---|---|---|---|
| Muscular Atrophy, Spinal | 4 | D009134 | ClinicalTrials |
| Muscular Atrophy, Spinal | 4 | D009134 | ClinicalTrials |
| Spinal Muscular Atrophies of Childhood | 3 | D014897 | ClinicalTrials |
| Spinal Muscular Atrophies of Childhood | 3 | D014897 | ClinicalTrials |
| Resources | Reference |
|---|---|
| ChEMBL | CHEMBL4297240 |
| FDA SRS | MLU3LU3EVV |