Pharmacology

Action Mechanism of Action Reference
RNAI INHIBITOR Transthyretin mRNA rnai inhibitor

Indications

Mesh Heading Maximum Phase Mesh ID Reference
Amyloid Neuropathies, Familial 4 D028227 ClinicalTrials
Polyneuropathies 4 D011115 FDA

Cross References

Resources Reference
ChEMBL CHEMBL4594511
FDA SRS GB4I2JI8UI