| Synonyms: | |
| Status: | Approved (2022) |
| Entry Type: | Oligonucleotide |
| Molecule Category: | UNKNOWN |
| UNII: | GB4I2JI8UI |
| Action | Mechanism of Action | Reference |
|---|---|---|
| RNAI INHIBITOR | Transthyretin mRNA rnai inhibitor |
| Mesh Heading | Maximum Phase | Mesh ID | Reference |
|---|---|---|---|
| Amyloid Neuropathies, Familial | 4 | D028227 | ClinicalTrials |
| Polyneuropathies | 4 | D011115 | FDA |
| Resources | Reference |
|---|---|
| ChEMBL | CHEMBL4594511 |
| FDA SRS | GB4I2JI8UI |