Display Options:
Total: 6532
Small molecule
Approved
Unknown
Unknown
Unknown
Unknown
Small molecule
Approved
OTHER
ORAL; TOPICAL
Carcinoma, Intraductal, Noninfiltrating; Multiple Myeloma; Pituitary ACTH Hypersecretion; Thyroid Neoplasms; Triple Negative Breast Neoplasms; Alopecia Areata; Alzheimer Disease; Breast Neoplasms; Leukemia; Leukemia, Myeloid, Acute; Lung Neoplasms; Myelodysplastic-Myeloproliferative Diseases; Myelodysplastic Syndromes; Parapsoriasis; Psoriasis; Sezary Syndrome; Carcinoma, Non-Small-Cell Lung; Cognitive Dysfunction; Lymphoma; Lymphoma, Large-Cell, Anaplastic; Mycosis Fungoides; Psychotic Disorders; Schizophrenia; Lymphoma, T-Cell; Lymphoma, T-Cell, Cutaneous; Neoplasms
Retinoid X receptor agonist
Small molecule
Approved
EYE; OTHER
OPHTHALMIC
Cataract; Osteomyelitis; Corneal Ulcer; Tuberculosis; Bacterial Infections; Conjunctivitis, Bacterial; Eye Infections; Infections
DNA gyrase inhibitor
Small molecule
Approved
Unknown
Unknown
Asthma; Pulmonary Disease, Chronic Obstructive
Unknown
Small molecule
Approved
OTHER
ORAL
Metabolic Syndrome; Hyperlipoproteinemia Type I; Polycystic Ovary Syndrome; Infertility; Obesity
Gastric lipase inhibitor
Small molecule
Approved
NEUROLOGY DRUGS & NERVOUS SYSTEM; OTHER
INTRAVENOUS; ORAL
Aphasia; Canavan Disease; Essential Tremor; Lymphoma, Follicular; Stroke; Alzheimer Disease; Anemia, Sickle Cell; Bipolar Disorder; Brain Neoplasms; Cocaine-Related Disorders; Cognitive Dysfunction; Dyskinesia, Drug-Induced; Epilepsy, Absence; Epilepsy, Reflex; Glioblastoma; Leukemia, Myeloid, Acute; Neuralgia, Postherpetic; Neuroblastoma; Obsessive-Compulsive Disorder; Opioid-Related Disorders; Paraganglioma; Parkinson Disease; Polyneuropathies; Psychotic Disorders; Restless Legs Syndrome; Stress Disorders, Post-Traumatic; Torticollis; Alcoholism; Anxiety; Dementia; Depressive Disorder; Epilepsies, Partial; Movement Disorders; Panic Disorder; Schizophrenia; Status Epilepticus; Subarachnoid Hemorrhage; Substance Withdrawal Syndrome; Epilepsy; Epilepsy, Tonic-Clonic; Seizures
Synaptic vesicle glycoprotein 2A modulator
Small molecule
Approved
OTHER; RESPIRATORY
ORAL
Romano-Ward Syndrome; Heart Failure; Arrhythmias, Cardiac; Atrial Fibrillation; Atrial Flutter
HERG blocker
Small molecule
Approved
Unknown
Unknown
Alzheimer Disease; Atrial Fibrillation; Brain Ischemia; Chronic Pain; Cocaine-Related Disorders; Cognitive Dysfunction; Cough; Epilepsy; Heart Diseases; Hernia, Inguinal; Hypotension; Nasal Polyps; Neuralgia; Neural Tube Defects; Postoperative Complications; Radius Fractures; Renal Insufficiency; Scoliosis; Tobacco Use Disorder; Vascular Diseases; Acute Kidney Injury; Amyotrophic Lateral Sclerosis; Brain Neoplasms; Burns; Child Development Disorders, Pervasive; Coronary Disease; Dental Anxiety; Dysautonomia, Familial; Hernias, Diaphragmatic, Congenital; Hypertension, Pulmonary; Hypertrophy; Mental Disorders; Pheochromocytoma; Pre-Eclampsia; Pregnancy; Shoulder Pain; Temporomandibular Joint Disorders; Anxiety; Brain Diseases; Brain Injuries; Breast Neoplasms; Cleft Palate; Colorectal Neoplasms; Delirium; Fractures, Bone; Headache; Heart Septal Defects, Atrial; Hypertension; Inflammation; Lung Diseases; Neoplasms; Obesity; Obesity, Morbid; Opioid-Related Disorders; Pain; Pharyngitis; Postoperative Nausea and Vomiting; Psychomotor Agitation; Rectal Diseases; Respiratory Insufficiency; Retinopathy of Prematurity; Rib Fractures; Shock, Septic; Sleep Apnea, Obstructive; Sleep Initiation and Maintenance Disorders; Stomach Neoplasms; Subarachnoid Hemorrhage; Tremor; Wounds and Injuries
Unknown
Small molecule
Approved
Unknown
Unknown
Anemia; Brain Ischemia; Candidiasis, Oral; Colorectal Neoplasms; Idiopathic Pulmonary Fibrosis; Neoplasms; Pressure Ulcer; Pulmonary Disease, Chronic Obstructive; Anemia, Sickle Cell; Coronary Disease; Coronavirus Infections; Cystic Fibrosis; Death, Sudden, Cardiac; Dyspnea; Heart Arrest; Heart Failure; Infections; Inflammation; Malaria; Myocardial Infarction; Myocardial Ischemia; Neuralgia; Opioid-Related Disorders; Pneumonia, Viral; Pulmonary Embolism; Sinusitis; Skin Ulcer; ST Elevation Myocardial Infarction; Stroke; Substance-Related Disorders; Tinea Pedis; Varicose Ulcer; Acute Kidney Injury; Brain Injuries; Bronchiolitis; Bronchopulmonary Dysplasia; Diabetic Foot; Hernias, Diaphragmatic, Congenital; Hypoxia; Leishmaniasis, Cutaneous; Lung Diseases; Persistent Fetal Circulation Syndrome; Pneumonia; Pneumonia, Aspiration; Premature Birth; Reperfusion Injury; Respiratory Distress Syndrome; Respiratory Distress Syndrome, Newborn; Sepsis; Severe Acute Respiratory Syndrome; Hypertension, Pulmonary; Respiratory Insufficiency; Respiratory Tract Diseases
Soluble guanylate cyclase activator
Small molecule
Approved
NEUROLOGY DRUGS & NERVOUS SYSTEM; OTHER; PREGNANCY AND GYNECOLOGY
ORAL; VAGINAL
Atrophy; Menopause
Estrogen receptor agonist
Small molecule
Approved
IMMUNE SYSTEM
TOPICAL
Breast Neoplasms; Lichen Planus; Lupus Erythematosus, Cutaneous; Psoriasis; Hand Dermatoses; Eczema; Neoplasms; Sarcoma, Kaposi
Retinoid receptor agonist
Small molecule
Approved
HEMATOLOGY
ORAL
Cerebellar Ataxia; Cognitive Dysfunction; HIV Infections; Myocardial Infarction; Amyotrophic Lateral Sclerosis; Friedreich Ataxia; Parkinson Disease; Stroke; Acute Kidney Injury; Hemochromatosis; Pantothenate Kinase-Associated Neurodegeneration; Anemia, Sickle Cell; beta-Thalassemia; Iron Overload; Thalassemia
Unknown
Small molecule
Approved
Unknown
Unknown
Contracture; Peanut Hypersensitivity; Conjunctivitis, Allergic; Dyspepsia; Fibromyalgia; Peripheral Nervous System Diseases; Rhinitis, Allergic, Perennial; Severe Acute Respiratory Syndrome; Eye Manifestations; Hypersensitivity
Unknown
Small molecule
Approved
CANCER; OTHER
INTRAVENOUS; ORAL
Cytomegalovirus Infections; Desmoplastic Small Round Cell Tumor; Ependymoma; Fallopian Tube Neoplasms; Meningitis, Aseptic; Prostatic Neoplasms; Prostatic Neoplasms, Castration-Resistant; Wilms Tumor; Biliary Tract Neoplasms; Brain Diseases; Brain Stem Neoplasms; Breast Neoplasms; Carcinoid Tumor; Carcinoma, Hepatocellular; Carcinoma, Islet Cell; Carcinoma, Neuroendocrine; Colorectal Neoplasms; Gastrointestinal Stromal Tumors; Hereditary Breast and Ovarian Cancer Syndrome; Leiomyosarcoma; Leukemia; Leukemia, Myeloid, Acute; Lung Neoplasms; Lymphoma; Lymphoma, Non-Hodgkin; Medulloblastoma; Myelodysplastic Syndromes; Neuroectodermal Tumors, Primitive, Peripheral; Neuroendocrine Tumors; Neurofibromatosis 1; Ovarian Neoplasms; Pancreatic Neoplasms; Pheochromocytoma; Pinealoma; Pituitary Neoplasms; Rectal Neoplasms; Retinoblastoma; Rhabdomyosarcoma; Rhabdomyosarcoma, Alveolar; Rhabdomyosarcoma, Embryonal; Sarcoma; Skin Neoplasms; Small Cell Lung Carcinoma; Spinal Cord Neoplasms; Uveal Melanoma; Astrocytoma; Brain Neoplasms; Carcinoma, Non-Small-Cell Lung; Central Nervous System Neoplasms; Choroid Plexus Neoplasms; Diffuse Intrinsic Pontine Glioma; Ganglioneuroblastoma; Gliosarcoma; Melanoma; Neoplasm Metastasis; Neuroblastoma; Oligodendroglioma; Optic Nerve Glioma; Paraganglioma; Sarcoma, Ewing; Glioblastoma; Glioma; Neoplasms
DNA inhibitor
Small molecule
Approved
Unknown
Unknown
Abdominal Pain; Cleft Palate; Postoperative Complications; Back Pain; Neoplasms; Pain; Pregnancy
Unknown
Small molecule
Approved
OTHER
ORAL
CADASIL; Fatty Liver; Osteoarthritis; Pain; Cerebral Small Vessel Diseases; Cognitive Dysfunction; Heart Failure; Intermittent Claudication; Stroke; Urticaria; Wounds and Injuries; Arthritis, Rheumatoid; Atherosclerosis; Cardiovascular Diseases; Cerebral Infarction; Cerebrovascular Disorders; Coronary Disease; Ischemic Stroke; Peripheral Arterial Disease; Peripheral Vascular Diseases; Thrombosis
Phosphodiesterase 3A inhibitor
Small molecule
Approved
Unknown
Unknown
Obesity; Renal Insufficiency, Chronic; Infections; Influenza in Birds; Thrombocytopenia; Influenza, Human; Pneumonia; Purpura, Thrombocytopenic, Idiopathic; Severe Acute Respiratory Syndrome; Virus Diseases
Unknown
Small molecule
Approved
Unknown
Unknown
Acquired Immunodeficiency Syndrome; Acute Coronary Syndrome; Alzheimer Disease; Amyotrophic Lateral Sclerosis; Anemia; Arthritis, Rheumatoid; Asthma; Carcinoma, Renal Cell; Cardiotoxicity; Constipation; Coronary Disease; Cystic Fibrosis; Diabetes Mellitus; Diabetes Mellitus, Type 2; Dyspepsia; Epilepsy; Erectile Dysfunction; Fibromyalgia; Heart Failure; Hepatitis C; HIV Infections; Hypertension; Hypoglycemia; Hypotension, Orthostatic; Immune System Diseases; Lice Infestations; Lipid Metabolism Disorders; Lupus Erythematosus, Systemic; Lymphoma; Malaria, Vivax; Myocardial Ischemia; Nausea; Non-alcoholic Fatty Liver Disease; Obesity; Osteomyelitis; Pain; Phenylketonurias; Postpartum Hemorrhage; Premature Birth; Psychotic Disorders; Respiratory Tract Infections; Restless Legs Syndrome; Schizophrenia; Smoking Cessation; Cholangitis; Corneal Ulcer; Lung Diseases; Muscle Spasticity; Neoplasms; Parkinson Disease; Tuberculosis, Meningeal; Tuberculosis, Multidrug-Resistant; Abscess; Acanthamoeba Keratitis; Breast Neoplasms; Bronchitis, Chronic; Cataract; Cellulitis; Cholecystitis, Acute; Conjunctivitis, Bacterial; Endophthalmitis; Helicobacter Infections; Infections; Inflammation; Influenza, Human; Keratitis; Meningitis; Otitis Media; Pelvic Inflammatory Disease; Pneumonia; Pneumonia, Bacterial; Pulmonary Disease, Chronic Obstructive; Severe Acute Respiratory Syndrome; Sinusitis; Skin Diseases; Tuberculosis; Tuberculosis, Pulmonary; Bacterial Infections; Eye Infections
Unknown
Small molecule
Approved
Unknown
Unknown
Unknown
Tyrosinase inhibitor
Small molecule
Approved
MUSCULOSKELETAL; OTHER; RHEUMATOLOGY
ORAL
Brain Neoplasms; Paraganglioma; Alzheimer Disease; Carcinoma, Non-Small-Cell Lung; Adenoma; Colorectal Neoplasms; Joint Diseases; Osteoarthritis; Osteoarthritis, Knee; Pain; Prostatic Neoplasms, Castration-Resistant; Stomach Neoplasms; Rheumatic Diseases
Cyclooxygenase-2 inhibitor
Small molecule
Approved
IMMUNE SYSTEM; OTHER
ORAL
Virus Diseases; Influenza, Human; Kidney Failure, Chronic
Neuraminidase inhibitor
Small molecule
Approved
Unknown
Unknown
Acne Vulgaris; Astrocytoma; Colonic Neoplasms; Colorectal Neoplasms; Crohn Disease; Dermatitis, Seborrheic; Glioma; Gliosarcoma; Oligodendroglioma; Sarcoma; Basal Cell Nevus Syndrome; Brain Neoplasms; Carcinoma, Basal Cell; Desmoid Tumors; Glioblastoma; Neurofibromatosis 1; Infections; Keratosis, Actinic; Paraganglioma; Neoplasms
Unknown
Small molecule
Approved
Unknown
Unknown
Pain; Pregnancy
Sodium channel protein type IV alpha subunit blocker
Small molecule
Approved
Unknown
Unknown
Osteomyelitis
Bacterial 70S ribosome inhibitor
Small molecule
Approved
OTHER
INJECTION
Magnetic Resonance Imaging
Diagnostic agent
Small molecule
Approved
IMMUNE SYSTEM
INHALATION
Dengue; Diabetes Mellitus, Type 2; Infections; Influenza, Human; Virus Diseases
Neuraminidase inhibitor
Small molecule
Approved
OTHER; PHARMACOLOGY
INJECTION
Unknown
Muscle-type nicotinic acetylcholine receptor antagonist
Small molecule
Approved
EYE; OTHER
OPHTHALMIC
Chronic Pain; Conjunctivitis, Allergic; Dermatitis; Fractures, Bone; Rhinitis, Allergic, Perennial
Histamine H1 receptor antagonist
Small molecule
Approved
NEUROLOGY DRUGS & NERVOUS SYSTEM; OTHER
ORAL
Sleep Wake Disorders; Anxiety; Dementia; Depressive Disorder; Schizophrenia; Sleep Initiation and Maintenance Disorders
GABA A receptor alpha-1/beta-1/gamma-2 positive allosteric modulator
Small molecule
Approved
Unknown
Unknown
Unknown
Unknown
Small molecule
Approved
DIABETES DRUGS & ENDOCRINOLOGY; OTHER; UROLOGY AND KIDNEY
INJECTION; ORAL
Neoplasms; Prostatic Neoplasms, Castration-Resistant; Psoriasis; Hyperparathyroidism, Secondary; Parathyroid Diseases; Renal Insufficiency, Chronic
Vitamin D receptor agonist
Small molecule
Approved
Unknown
Unknown
Adrenoleukodystrophy; Anemia, Sickle Cell; Barrett Esophagus; Burns; Carcinoma in Situ; Carcinoma, Intraductal, Noninfiltrating; Gingivitis; Glioblastoma; Hyperlipidemias; Irritable Bowel Syndrome; Nasal Obstruction; Pneumonia; Primary Immunodeficiency Diseases; Skin Diseases; Skin Neoplasms; Tibial Fractures; Acquired Immunodeficiency Syndrome; Aging; Autistic Disorder; Bronchiolitis; Colonic Neoplasms; Common Cold; Conjunctivitis, Allergic; Depressive Disorder; Dermatitis, Atopic; Diabetes Mellitus; Glucose Intolerance; Hematologic Neoplasms; Hereditary Breast and Ovarian Cancer Syndrome; Hypersensitivity; Infertility, Male; Keratosis, Actinic; Leukemia, Myeloid, Acute; Malnutrition; Metabolic Syndrome; Multiple Sclerosis; Neoplasms; Neurofibromatosis 1; Optic Neuritis; Ovarian Neoplasms; Parkinson Disease; Prediabetic State; Psoriasis; Psychotic Disorders; Pulmonary Disease, Chronic Obstructive; Rectal Neoplasms; Respiratory Insufficiency; Staphylococcal Infections; Urinary Tract Infections; Adenoma; Arthritis, Juvenile; Asthma; Bone Diseases, Metabolic; Breast Neoplasms; Cardiovascular Diseases; Cognitive Dysfunction; Colitis, Ulcerative; Colorectal Neoplasms; Crohn Disease; Diabetes, Gestational; Diabetes Mellitus, Type 1; Diabetes Mellitus, Type 2; Epilepsy; Fractures, Bone; Heart Failure; Helicobacter Infections; Hepatitis C; Hip Fractures; HIV Infections; Hyperparathyroidism; Hypogonadism; Infections; Inflammatory Bowel Diseases; Influenza, Human; Leukemia, Lymphocytic, Chronic, B-Cell; Lipid Metabolism Disorders; Lupus Erythematosus, Systemic; Lymphoma, Large B-Cell, Diffuse; Melanoma; Multiple Sclerosis, Relapsing-Remitting; Non-alcoholic Fatty Liver Disease; Obesity; Osteoporosis, Postmenopausal; Polycystic Ovary Syndrome; Pregnancy; Prostatic Neoplasms; Prostatic Neoplasms, Castration-Resistant; Renal Insufficiency, Chronic; Schizophrenia; Severe Acute Respiratory Syndrome; Tuberculosis; Tuberculosis, Pulmonary; Urticaria; Vitamin D Deficiency; Anemia; Anemia, Iron-Deficiency; Osteoporosis
Vitamin D receptor agonist
Small molecule
Approved
Unknown
Unknown
Aortic Aneurysm, Abdominal; Asthma; Muscular Dystrophy, Duchenne
Unknown
Small molecule
Approved
IMMUNE SYSTEM; OTHER; UROLOGY AND KIDNEY
ORAL
Acute Lung Injury; Adenocarcinoma of Lung; Alcoholism; Alzheimer Disease; Carcinoma, Non-Small-Cell Lung; Carcinoma, Squamous Cell; Central Nervous System Neoplasms; Desmoid Tumors; Diabetic Retinopathy; Eosinophilic Esophagitis; Fallopian Tube Neoplasms; Frontotemporal Dementia; Gangliosidoses; Gaucher Disease; Glioma; Glycogen Storage Disease Type II; Granulomatous Disease, Chronic; Heart Failure; Hematologic Neoplasms; HIV Infections; Hypercholesterolemia; Hyperinsulinism; Hypertension, Pulmonary; Kidney Diseases; Leiomyosarcoma; Leukemia, Lymphoid; Leukemia, Myelogenous, Chronic, BCR-ABL Positive; Leukemia, Plasma Cell; Lung Neoplasms; Multiple Sclerosis, Relapsing-Remitting; Neoplasms, Plasma Cell; Neurilemmoma; Panuveitis; Parkinson Disease; Pemphigus; Port-Wine Stain; Primary Immunodeficiency Diseases; Prostatic Neoplasms; Rectal Neoplasms; Respiratory Distress Syndrome; Respiratory Insufficiency; Sarcopenia; Scleritis; Sjogren's Syndrome; Small Cell Lung Carcinoma; Thalassemia; Uveitis, Anterior; Adenomatous Polyposis Coli; Aging; Amyotrophic Lateral Sclerosis; Anemia; Anemia, Aplastic; Anemia, Hemolytic, Autoimmune; Anemia, Sickle Cell; beta-Thalassemia; Blood Platelet Disorders; Bronchiolitis Obliterans Syndrome; Bronchitis; Carcinoma, Renal Cell; Castleman Disease; Choroidal Neovascularization; Depressive Disorder; Dry Eye Syndromes; Fanconi Anemia; Geographic Atrophy; Glioblastoma; Gliosarcoma; Glomerulonephritis, IGA; Glomerulosclerosis, Focal Segmental; Graves Ophthalmopathy; Hemangioendothelioma; Hematologic Diseases; Hemorrhage; Hypertension; Immunologic Deficiency Syndromes; Intracranial Aneurysm; Intracranial Arteriovenous Malformations; Leukemia; Leukemia, Lymphocytic, Chronic, B-Cell; Leukemia, Myeloid, Acute; Liver Diseases; Liver Neoplasms; Lupus Erythematosus, Systemic; Lupus Nephritis; Lymphoma; Lymphoma, Large B-Cell, Diffuse; Lymphoma, Mantle-Cell; Lymphoma, T-Cell, Cutaneous; Macular Degeneration; Multiple Myeloma; Multiple System Atrophy; Myelodysplastic Syndromes; Neoplasm Metastasis; Neoplasms, Germ Cell and Embryonal; Neuroblastoma; Neurofibromatosis 1; Osteosarcoma; Ovarian Neoplasms; Pancreatic Neoplasms; Paraganglioma; Perivascular Epithelioid Cell Neoplasms; Pinealoma; Polycystic Kidney Diseases; Precursor Cell Lymphoblastic Leukemia-Lymphoma; Prostatic Neoplasms, Castration-Resistant; Renal Insufficiency; Retroperitoneal Fibrosis; Sarcoidosis; Sarcoma; Scleroderma, Systemic; Severe Acute Respiratory Syndrome; Severe Combined Immunodeficiency; Sturge-Weber Syndrome; Thyroid Neoplasms; Uveitis, Intermediate; Uveitis, Posterior; Vascular Malformations; Vitiligo; Birt-Hogg-Dube Syndrome; Breast Neoplasms; Carcinoma, Hepatocellular; Cardiovascular Abnormalities; Diabetes Mellitus, Type 1; Diabetic Nephropathies; Fibroma; Graft vs Host Disease; Hodgkin Disease; Influenza, Human; Kidney Failure, Chronic; Lichen Planus, Oral; Lymphangioleiomyomatosis; Lymphedema; Lymphoma, Non-Hodgkin; Myositis, Inclusion Body; Neurofibromatoses; Pachyonychia Congenita; Polycystic Kidney, Autosomal Dominant; Renal Insufficiency, Chronic; Skin Neoplasms; Urinary Bladder Neoplasms; Angiofibroma; Delayed Graft Function; Eye Diseases; Kidney Transplantation; Neoplasms; Tuberous Sclerosis
FK506-binding protein 1A inhibitor
Small molecule
Approved
Unknown
Unknown
Renal Insufficiency; Pain; Periodontitis; Pulpitis
Unknown