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Total: 6532
Small molecule
Approved
Unknown
Unknown
Brain Injuries; Heart Failure; Liver Cirrhosis; Hyponatremia; Cardiovascular Diseases
Unknown
Small molecule
Approved
Unknown
Unknown
Chronic Pain; Immunologic Deficiency Syndromes; Severe Acute Respiratory Syndrome; Malaria, Falciparum; Malaria
Unknown
Small molecule
Approved
IMMUNE SYSTEM; OTHER
ORAL
Colorectal Neoplasms; Hepatitis C, Chronic; Hepatitis D; Infections; Liver Failure; Liver Neoplasms; Stomach Neoplasms; Carcinoma, Hepatocellular; Hepatitis B; Hepatitis B, Chronic; Liver Diseases; Virus Diseases
DNA polymerase/reverse transcriptase inhibitor
Small molecule
Approved
NEUROLOGY DRUGS & NERVOUS SYSTEM; OTHER; PEDIATRICS
ORAL
Neuralgia; Epilepsy; Dementia; Depressive Disorder; Epilepsia Partialis Continua; Low Back Pain; Pain; Schizophrenia; Anxiety; Lennox Gastaut Syndrome; Seizures
GABA-A receptor; anion channel positive allosteric modulator
Small molecule
Approved
Unknown
ORAL
Astrocytoma; Biliary Tract Neoplasms; Brain Neoplasms; Carcinoma, Small Cell; Carcinoma, Squamous Cell; Cholangiocarcinoma; Hypertension, Pulmonary; Leukemia, Myeloid; Leukemia, Promyelocytic, Acute; Liver Diseases; Lymphoma; Multiple Myeloma; Neoplasms, Plasma Cell; Oligodendroglioma; Precursor Cell Lymphoblastic Leukemia-Lymphoma; Rectal Neoplasms; Sarcoma, Kaposi; Thrombosis; Uterine Cervical Neoplasms; Adenocarcinoma; Adenocarcinoma, Follicular; Adrenal Cortex Neoplasms; Bile Duct Neoplasms; Carcinoma, Medullary; Colorectal Neoplasms; Diabetes Mellitus, Type 1; Gallbladder Neoplasms; Gastrointestinal Stromal Tumors; Glioblastoma; Gliosarcoma; Head and Neck Neoplasms; Hermanski-Pudlak Syndrome; Hypertension, Portal; Keloid; Kidney Diseases; Leukemia; Leukemia, Biphenotypic, Acute; Leukemia, Lymphocytic, Chronic, B-Cell; Leukemia, Myelogenous, Chronic, BCR-ABL Positive; Leukemia, Myeloid, Acute; Lung Neoplasms; Mesothelioma; Myelodysplastic Syndromes; Nasopharyngeal Neoplasms; Neuroblastoma; Neuroendocrine Tumors; Osteosarcoma; Ovarian Neoplasms; Pancreatic Neoplasms; Prostatic Neoplasms; Prostatic Neoplasms, Castration-Resistant; Rhabdomyosarcoma; Salivary Gland Neoplasms; Sarcoma; Small Cell Lung Carcinoma; Stomach Neoplasms; Testicular Neoplasms; Urinary Bladder Neoplasms; Uveal Melanoma; Breast Neoplasms; Carcinoma; Carcinoma, Hepatocellular; Carcinoma, Non-Small-Cell Lung; Carcinoma, Renal Cell; Hepatoblastoma; Kidney Neoplasms; Liver Neoplasms; Melanoma; Neoplasms; Thyroid Neoplasms
Unknown
Small molecule
Approved
OTHER
ORAL
Liver Diseases; Precursor Cell Lymphoblastic Leukemia-Lymphoma; Anemia; Hemochromatosis; Leukemia, Myeloid, Acute; Mucormycosis; Osteoporosis, Postmenopausal; Anemia, Diamond-Blackfan; Anemia, Sickle Cell; Hemosiderosis; Porphyria Cutanea Tarda; Thalassemia; beta-Thalassemia; Iron Overload; Myelodysplastic Syndromes
Iron chelating agent
Small molecule
Approved
Unknown
Unknown
Asthma; Proteinuria; Renal Insufficiency, Chronic; Hypertension, Pulmonary; Hypertension
Endothelin receptor, ET-A/ET-B antagonist
Small molecule
Approved
Unknown
ORAL
Alzheimer Disease; Amyotrophic Lateral Sclerosis; Restless Legs Syndrome; Supranuclear Palsy, Progressive; Parkinson Disease
Unknown
Small molecule
Approved
Unknown
Unknown
Marijuana Abuse; Pain; Alcohol Drinking; Spinal Cord Injuries; Tobacco Use Disorder; Arteriosclerosis; Cardiovascular Diseases; Coronary Artery Disease; Diabetes Mellitus, Type 2; Fatty Liver; Lipid Metabolism Disorders; Metabolic Syndrome; Prader-Willi Syndrome; Prediabetic State; Smoking Cessation; Weight Loss; Obesity
Cannabinoid CB1 receptor antagonist
Small molecule
Approved
OTHER
ORAL
Alzheimer Disease; Anus Neoplasms; Burkitt Lymphoma; Carcinoma, Ovarian Epithelial; Carcinoma, Squamous Cell; Carcinoma, Verrucous; Crohn Disease; Diffuse Intrinsic Pontine Glioma; Esophageal Neoplasms; Fallopian Tube Neoplasms; Glioma; Hypopharyngeal Neoplasms; Leukemia, Lymphoid; Leukemia, Myelogenous, Chronic, BCR-ABL Positive; Leukemia, Myelomonocytic, Juvenile; Leukemia, Promyelocytic, Acute; Liver Neoplasms; Lymphoma, Large B-Cell, Diffuse; Lymphoma, T-Cell, Peripheral; Medulloblastoma; Melanoma; Neoplasms, Plasma Cell; Niemann-Pick Diseases; Oligodendroglioma; Oropharyngeal Neoplasms; Pancreatic Neoplasms; Peritoneal Neoplasms; Precursor T-Cell Lymphoblastic Leukemia-Lymphoma; Salivary Gland Neoplasms; Schizophrenia; Skin Neoplasms; Small Cell Lung Carcinoma; Squamous Cell Carcinoma of Head and Neck; Stomach Neoplasms; Adenocarcinoma, Follicular; Anemia, Sickle Cell; Astrocytoma; Brain Diseases; Brain Neoplasms; Breast Neoplasms; Breast Neoplasms, Male; Carcinoma, Medullary; Carcinoma, Non-Small-Cell Lung; Carcinoma, Renal Cell; Colonic Neoplasms; Colorectal Neoplasms; Glioblastoma; Gliosarcoma; HIV Infections; Hodgkin Disease; Leukemia; Leukemia, Biphenotypic, Acute; Leukemia, Lymphocytic, Chronic, B-Cell; Lymphoma, B-Cell, Marginal Zone; Lymphoma, Follicular; Lymphoma, Mantle-Cell; Lymphoma, Non-Hodgkin; Mycosis Fungoides; Myelodysplastic Syndromes; Neuroblastoma; Ovarian Neoplasms; Pituitary ACTH Hypersecretion; Polycythemia Vera; Precursor Cell Lymphoblastic Leukemia-Lymphoma; Prostatic Neoplasms; Prostatic Neoplasms, Castration-Resistant; Rectal Neoplasms; Sarcoma; Sezary Syndrome; Thrombocythemia, Essential; Thyroid Neoplasms; Urinary Bladder Neoplasms; Uveal Melanoma; Leukemia, Myeloid, Acute; Lung Neoplasms; Lymphoma; Mesothelioma; Multiple Myeloma; Lymphoma, T-Cell; Lymphoma, T-Cell, Cutaneous; Neoplasms
Histone deacetylase 1 inhibitor
Small molecule
Approved
IMMUNE SYSTEM; OTHER
INJECTION; INTRAVENOUS
Mycoses; Neutropenia; Leukemia; Leukemia, Myeloid, Acute; Myelodysplastic Syndromes; Neoplasms; Aspergillosis; Candidiasis, Invasive; Neuroaspergillosis; Candidemia; Candidiasis; Peritonitis
1,3-beta-glucan synthase inhibitor
Small molecule
Approved
Unknown
Unknown
Melanosis
Sunscreen
Small molecule
Approved
IMMUNE SYSTEM; OTHER
INTRAVENOUS; ORAL
Glioblastoma; Leukemia; Leukemia, Myeloid, Acute; Neoplasms; Chagas Disease; Granulomatous Disease, Chronic; Mucormycosis; Onychomycosis; Candidiasis, Oral; Leukopenia; Aspergillosis; Candidiasis; Coccidioidomycosis; Mycoses; Neutropenia
Cytochrome P450 51 inhibitor
Small molecule
Approved
HEMATOLOGY; OTHER
INTRAVENOUS
Burkitt Lymphoma; Carcinoma, Squamous Cell; Head and Neck Neoplasms; Hematologic Neoplasms; HIV Infections; Leukemia, Promyelocytic, Acute; Lymphoma, Follicular; Lymphoma, Mantle-Cell; Lymphoma, Non-Hodgkin; Lymphoma, T-Cell, Cutaneous; Mastocytosis, Systemic; Medulloblastoma; Multiple Myeloma; Neuroblastoma; Paraganglioma; Precursor Cell Lymphoblastic Leukemia-Lymphoma; Precursor T-Cell Lymphoblastic Leukemia-Lymphoma; Prostatic Neoplasms; Sarcoma, Synovial; Triple Negative Breast Neoplasms; Adenocarcinoma, Follicular; Anemia, Aplastic; Anemia, Sickle Cell; Breast Neoplasms; Carcinoma, Non-Small-Cell Lung; Carcinoma, Renal Cell; Esophageal Neoplasms; Fallopian Tube Neoplasms; Granuloma, Lethal Midline; Hodgkin Disease; Leukemia, Myelogenous, Chronic, BCR-ABL Positive; Lung Neoplasms; Lymphoma; Melanoma; Ovarian Neoplasms; Peritoneal Neoplasms; Primary Myelofibrosis; Severe Acute Respiratory Syndrome; Thalassemia; Thyroid Neoplasms; Graft vs Host Disease; Hematologic Diseases; Leukemia; Leukemia, Myeloid, Acute; Lymphoma, Large B-Cell, Diffuse; Lymphoma, T-Cell, Peripheral; Myeloproliferative Disorders; Purpura, Thrombocytopenic, Idiopathic; Thrombocytopenia; Anemia; Anemia, Refractory, with Excess of Blasts; Leukemia, Myeloid; Leukemia, Myelomonocytic, Chronic; Myelodysplastic Syndromes; Neoplasms
DNA (cytosine-5)-methyltransferase 1 inhibitor
Small molecule
Approved
Unknown
Unknown
Hepatitis; Liver Cirrhosis; Hepatitis B, Chronic; Virus Diseases
DNA polymerase/reverse transcriptase inhibitor
Small molecule
Approved
OTHER
ORAL
Amyotrophic Lateral Sclerosis; Hepatitis C; Insulin Resistance; Acquired Immunodeficiency Syndrome; Infections; Pneumonia, Pneumocystis; Severe Acute Respiratory Syndrome; HIV Infections; Virus Diseases
Human immunodeficiency virus type 1 protease inhibitor
Small molecule
Approved
CANCER; OTHER
ORAL
Leukemia, Myelogenous, Chronic, BCR-ABL Positive; Precursor Cell Lymphoblastic Leukemia-Lymphoma
Bcr/Abl fusion protein inhibitor
Small molecule
Approved
Unknown
Unknown
Ductus Arteriosus, Patent
Cyclooxygenase inhibitor
Small molecule
Approved
OTHER
ORAL
Alcohol Drinking; Alzheimer Disease; Amphetamine-Related Disorders; Cocaine-Related Disorders; Friedreich Ataxia; Machado-Joseph Disease; Marijuana Abuse; Parkinson Disease; Psychotic Disorders; Schizophrenia; Substance-Related Disorders; Acute Coronary Syndrome; Alcoholism; Dry Eye Syndromes; Lung Neoplasms; Neoplasms; Smoking Cessation; Eye Diseases; Tobacco Use Disorder
Neuronal acetylcholine receptor; alpha4/beta2 partial agonist
Small molecule
Approved
Unknown
Unknown
Gliosarcoma; Hemorrhagic Fever, Ebola; Kidney Diseases; Leukemia, Myeloid, Acute; Osteosarcoma; Adenocarcinoma; Adrenal Cortex Neoplasms; Ascites; Brain Neoplasms; Carcinoid Tumor; Carcinoma; Carcinoma, Hepatocellular; Carcinoma, Islet Cell; Carcinoma, Squamous Cell; Cholangiocarcinoma; Colorectal Neoplasms; Esophageal Neoplasms; Fallopian Tube Neoplasms; Glioblastoma; Glioma; Liver Neoplasms; Lung Neoplasms; Melanoma; Nasopharyngeal Carcinoma; Neoplasms, Germ Cell and Embryonal; Ovarian Neoplasms; Pancreatic Neoplasms; Peritoneal Neoplasms; Pheochromocytoma; Prostatic Neoplasms, Castration-Resistant; Sarcoma; Sarcoma, Alveolar Soft Part; Small Cell Lung Carcinoma; Stomach Neoplasms; Thymoma; Thymus Neoplasms; Thyroid Neoplasms; Urinary Bladder Neoplasms; Uveal Melanoma; von Hippel-Lindau Disease; Breast Neoplasms; Carcinoma, Non-Small-Cell Lung; Kidney Neoplasms; Prostatic Neoplasms; Urogenital Neoplasms; Carcinoma, Renal Cell; Gastrointestinal Stromal Tumors; Neoplasms; Neuroendocrine Tumors
Macrophage colony stimulating factor receptor inhibitor
Small molecule
Approved
OTHER; PEDIATRICS; RESPIRATORY
INHALATION; NASAL
Pulmonary Disease, Chronic Obstructive; Chronic Disease; Hypersensitivity; Respiratory Tract Diseases; Severe Acute Respiratory Syndrome; Asthma; Lung Diseases, Obstructive; Nasal Obstruction; Rhinitis, Allergic, Perennial; Rhinitis, Allergic, Seasonal
Glucocorticoid receptor agonist
Small molecule
Approved
CARDIOVASCULAR; OTHER
ORAL
Hypertension, Pulmonary; Kidney Diseases; Myotonic Disorders; Acute Coronary Syndrome; Amyotrophic Lateral Sclerosis; Cardiomyopathy, Dilated; Crohn Disease; Heart Failure, Diastolic; Irritable Bowel Syndrome; Romano-Ward Syndrome; Vascular Diseases; Atrial Fibrillation; Coronary Disease; Diabetes Mellitus, Type 2; Myocardial Ischemia; Angina Pectoris; Cardiovascular Diseases
Sodium channel protein type IV alpha subunit blocker
Small molecule
Approved
Unknown
Unknown
Tonsillitis; Pain; Acid-Base Imbalance; Fluid Therapy
pH lowering agent
Small molecule
Approved
GASTROINTESTINAL; OTHER
ORAL
HIV Infections; Chronic Pain; Constipation; Irritable Bowel Syndrome
Chloride channel protein 2 opener
Small molecule
Approved
Unknown
Unknown
Asthma; Bronchitis; Bronchitis, Chronic; Emphysema; Pulmonary Disease, Chronic Obstructive
Unknown
Small molecule
Approved
NEUROLOGY DRUGS & NERVOUS SYSTEM; OTHER
ORAL
Obsessive-Compulsive Disorder; Anxiety; Autistic Disorder; Bipolar Disorder; Dementia; Depressive Disorder; Mood Disorders; Psychotic Disorders; Schizophrenia
Dopamine D2 receptor antagonist
Small molecule
Approved
IMMUNE SYSTEM; OTHER
ORAL
Autoimmune Diseases; HIV Infections; Infections
Human immunodeficiency virus type 1 protease inhibitor
Small molecule
Approved
Unknown
Unknown
Unknown
Sunscreen
Small molecule
Approved
Unknown
Unknown
Pulpitis; Wounds and Injuries; Anemia; Anemia, Iron-Deficiency; Burns; Dermatitis; Diaper Rash; Exanthema; Fever; Hemorrhage; Hemorrhoids; Lymphedema; Neoplasms; Pruritus; Psoriasis; Skin Neoplasms; Sprains and Strains; Sunburn; Thrombophlebitis; Varicose Ulcer
Sunscreen/skin protectant
Small molecule
Approved
Unknown
Unknown
Urticaria; Metabolic Syndrome; Skin Neoplasms; Sunburn
Unknown
Small molecule
Approved
Unknown
Unknown
Carcinoma, Hepatocellular; Heart Failure; Hepatitis C; Carcinoma, Pancreatic Ductal; Cystic Fibrosis; Diabetes Mellitus, Type 1; Glucose Intolerance; HIV Infections; Hyperlipidemias; Non-alcoholic Fatty Liver Disease; Obesity; Polycystic Ovary Syndrome; Prediabetic State; Psoriasis; Diabetes Mellitus, Type 2; Diabetic Foot; Graft vs Host Disease; Myocardial Infarction; Renal Insufficiency, Chronic; Severe Acute Respiratory Syndrome; Diabetes Mellitus
Unknown
Small molecule
Approved
Unknown
Unknown
Idiopathic Pulmonary Fibrosis; Osteoporosis; Essential Hypertension; Stroke; Hypertension; Marfan Syndrome; Severe Acute Respiratory Syndrome; Cardiovascular Diseases
Unknown
Small molecule
Approved
Unknown
Unknown
Diabetes Mellitus, Type 2; Renal Insufficiency, Chronic; Acute Coronary Syndrome; Atherosclerosis; Diabetic Nephropathies; Kidney Diseases; Atrial Fibrillation; Coronary Artery Disease; Diabetes Mellitus; Essential Hypertension; Glomerulonephritis, IGA; Heart Failure; Hypertension; Hypertrophy, Left Ventricular; Marfan Syndrome; Myocardial Infarction; Cardiovascular Diseases
Unknown
Small molecule
Approved
CARDIOVASCULAR; OTHER; RESPIRATORY
ORAL
Anemia, Sickle Cell; Altitude Sickness; Asthma; Hypoplastic Left Heart Syndrome; Severe Acute Respiratory Syndrome; Idiopathic Pulmonary Fibrosis; Vascular Diseases; Familial Primary Pulmonary Hypertension; Hypertension; Hypertension, Pulmonary; Pulmonary Arterial Hypertension
Endothelin receptor, ET-A/ET-B antagonist
Small molecule
Approved
Unknown
Unknown
Coronary Disease; Coronary Artery Disease
Diagnostic agent