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Total: 1496
Small molecule
Approved
IMMUNE SYSTEM; OTHER; UROLOGY AND KIDNEY
INTRAVENOUS
Meningitis; Appendicitis; Cholecystitis; Pancreatitis; Peritonitis; Pneumonia; Pneumonia, Ventilator-Associated; Bacterial Infections; Intraabdominal Infections; Pyelonephritis; Urinary Tract Infections
Bacterial penicillin-binding protein inhibitor
Small molecule
Approved
OTHER
ORAL
Head and Neck Neoplasms; Hepatitis C; Leukemia, Biphenotypic, Acute; Paraparesis, Tropical Spastic; HTLV-I Infections; Liver Cirrhosis, Biliary; Multiple Sclerosis, Relapsing-Remitting; Acquired Immunodeficiency Syndrome; HIV Infections; Infections; Virus Diseases
Unknown
Small molecule
Approved
NEUROLOGY DRUGS & NERVOUS SYSTEM; OTHER
TRANSDERMAL
Alzheimer Disease; Fibromyalgia; Stroke; Substance-Related Disorders; Parkinson Disease; Restless Legs Syndrome
D2-like dopamine receptor agonist
Small molecule
Approved
OTHER
INTRAVENOUS
Astrocytoma; Gliosarcoma; Head and Neck Neoplasms; Bile Duct Neoplasms; Breast Neoplasms, Male; Burkitt Lymphoma; Carcinoma, Non-Small-Cell Lung; Carcinoma, Renal Cell; Carcinoma, Verrucous; Cholangiocarcinoma; Colorectal Neoplasms; Gallbladder Neoplasms; Hypopharyngeal Neoplasms; Leukemia; Liver Neoplasms; Lung Neoplasms; Lymphoma; Lymphoma, Follicular; Lymphoma, Large B-Cell, Diffuse; Lymphoma, Large-Cell, Anaplastic; Lymphoma, Mantle-Cell; Melanoma; Oropharyngeal Neoplasms; Ovarian Neoplasms; Pancreatic Neoplasms; Peritoneal Neoplasms; Prostatic Neoplasms; Prostatic Neoplasms, Castration-Resistant; Retroviridae Infections; Sarcoma; Squamous Cell Carcinoma of Head and Neck; Stomach Neoplasms; Tongue Neoplasms; Urethral Neoplasms; Urinary Bladder Neoplasms; Endometrial Neoplasms; Breast Neoplasms; Neoplasms
Tubulin inhibitor
Small molecule
Approved
CARDIOVASCULAR; OTHER; RESPIRATORY
ORAL
Anemia, Sickle Cell; Altitude Sickness; Asthma; Hypoplastic Left Heart Syndrome; Severe Acute Respiratory Syndrome; Idiopathic Pulmonary Fibrosis; Vascular Diseases; Familial Primary Pulmonary Hypertension; Hypertension; Hypertension, Pulmonary; Pulmonary Arterial Hypertension
Endothelin receptor, ET-A/ET-B antagonist
Small molecule
Approved
NEUROLOGY DRUGS & NERVOUS SYSTEM; OTHER
ORAL
Carcinoma, Non-Small-Cell Lung; Head and Neck Neoplasms; Esophageal Neoplasms; Glioma; Multiple Sclerosis; Neoplasms; Schizophrenia; Sleep Initiation and Maintenance Disorders; Stroke; Brain Injuries; Depressive Disorder; Disorders of Excessive Somnolence; Fatigue; Obesity; Sleep Apnea Syndromes; Attention Deficit Disorder with Hyperactivity; Narcolepsy; Sleep Apnea, Obstructive; Sleep Wake Disorders
Dopamine transporter inhibitor
Enzyme
Approved
OTHER
INJECTION
Empyema, Pleural; Pulmonary Embolism; ST Elevation Myocardial Infarction; Empyema; Infections; Stroke; Thrombosis
Urokinase-type plasminogen activator exogenous protein
Small molecule
Approved
IMMUNE SYSTEM; OTHER
ORAL
Hypertriglyceridemia; AIDS Dementia Complex; Arthritis, Rheumatoid; Cognitive Dysfunction; Graft vs Host Disease; Hematologic Neoplasms; Hodgkin Disease; Leukemia, Lymphocytic, Chronic, B-Cell; Leukemia, Myelogenous, Chronic, BCR-ABL Positive; Lymphoma, Follicular; Lymphoma, Large B-Cell, Diffuse; Myelodysplastic Syndromes; Sarcoma, Kaposi; Severe Acute Respiratory Syndrome; Stroke; Acquired Immunodeficiency Syndrome; Infections; HIV Infections; Virus Diseases
C-C chemokine receptor type 5 antagonist
Small molecule
Approved
HEMATOLOGY; OTHER
ORAL
Lymphoma; Myelodysplastic Syndromes; Anemia, Aplastic; Hepatitis C, Chronic; Purpura, Thrombocytopenic, Idiopathic; Thrombocytopenia
Thrombopoietin receptor agonist
Small molecule
Approved
OTHER
INTRAVENOUS
Cardiovascular Diseases; Myocardial Perfusion Imaging
Adenosine A2a receptor agonist
Small molecule
Approved
OTHER
ORAL
Fibromyalgia; Hepatitis C, Chronic; Depressive Disorder; Depressive Disorder, Major
Norepinephrine transporter inhibitor
Small molecule
Approved
OTHER
ORAL
Premature Ejaculation; Prostatitis; Kidney Calculi; Prostatic Neoplasms, Castration-Resistant; Urolithiasis; Prostatic Hyperplasia
Alpha-1a adrenergic receptor antagonist
Protein
Approved
OTHER
SINGLE-USE
Diabetes Mellitus, Type 1; Hearing Loss; Scleroderma, Diffuse; Arthritis, Juvenile; Cold Urticaria; Familial Mediterranean Fever; Hepatitis, Alcoholic; Gout; Cryopyrin-Associated Periodic Syndromes; Immune System Diseases; Pericarditis
Interleukin-1 beta inhibitor
Small molecule
Approved
OTHER; UROLOGY AND KIDNEY
ORAL
Urinary Incontinence; Urinary Bladder, Overactive; Urinary Incontinence, Urge
Muscarinic acetylcholine receptor M2 antagonist
Small molecule
Approved
IMMUNE SYSTEM; OTHER
ORAL
Infections; Acquired Immunodeficiency Syndrome; Friedreich Ataxia; HIV; HIV Infections; Virus Diseases
Human immunodeficiency virus type 1 reverse transcriptase inhibitor
Small molecule
Approved
CARDIOVASCULAR; OTHER
INTRAVENOUS
Vascular Diseases; Scoliosis; Hypertension; Hypertension, Malignant; Stroke; Cardiovascular Diseases
Voltage-gated L-type calcium channel blocker
Small molecule
Approved
NEUROLOGY DRUGS & NERVOUS SYSTEM; OTHER; PEDIATRICS
ORAL
Pain; Epilepsy; Lennox Gastaut Syndrome; Seizures
Sodium channel alpha subunit blocker
Small molecule
Approved
MUSCULOSKELETAL; OTHER
ORAL
Tourette Syndrome; Movement Disorders; Chorea; Huntington Disease
Synaptic vesicular amine transporter inhibitor
Small molecule
Approved
CARDIOVASCULAR; OTHER
ORAL
Coronary Disease; Hypercholesterolemia; Hyperlipidemia, Familial Combined; Lipid Metabolism Disorders; Cardiovascular Diseases
Peroxisome proliferator-activated receptor alpha agonist
Small molecule
Approved
CANCER; OTHER
INJECTION; INTRAVENOUS
Fallopian Tube Neoplasms; Lymphoma, Large-Cell, Anaplastic; Lymphoma, T-Cell, Cutaneous; Multiple Myeloma; Mycosis Fungoides; Ovarian Neoplasms; Peritoneal Neoplasms; Sezary Syndrome; Breast Neoplasms; Carcinoma, Non-Small-Cell Lung; Head and Neck Neoplasms; Leukemia-Lymphoma, Adult T-Cell; Lung Neoplasms; Lymphoma; Lymphoma, T-Cell; Lymphoma, T-Cell, Peripheral; Neoplasms
Dihydrofolate reductase inhibitor
Small molecule
Approved
OTHER
ORAL
Liver Diseases; Stress Disorders, Post-Traumatic; Bipolar Disorder; Psychotic Disorders; Schizophrenia
Dopamine D2 receptor antagonist
Antibody
Approved
DERMATOLOGY; OTHER
INJECTION
Ichthyosis; Sjogren's Syndrome; Arthritis, Rheumatoid; Behcet Syndrome; Dermatitis, Atopic; Diabetes Mellitus, Type 1; Giant Cell Arteritis; Graft vs Host Disease; Hematologic Diseases; Hematologic Neoplasms; Hidradenitis Suppurativa; Liver Cirrhosis, Biliary; Multiple Sclerosis; Pemphigoid, Bullous; Sarcoidosis; Uveitis; Arthritis, Juvenile; Colitis; Dermatomyositis; Inflammatory Bowel Diseases; Lupus Erythematosus, Systemic; Polymyositis; Pouchitis; Spondylitis, Ankylosing; Takayasu Arteritis; Arthritis, Psoriatic; Colitis, Ulcerative; Crohn Disease; Immune System Diseases; Psoriasis
Interleukin-12 inhibitor
Antibody
Approved
OTHER; RHEUMATOLOGY
INJECTION
Asthma; Crohn Disease; Diabetes Mellitus, Type 1; Prostatic Neoplasms; Sarcoidosis; Arthritis, Juvenile; Osteoarthritis; Spondylarthropathies; Arthritis, Psoriatic; Arthritis, Rheumatoid; Colitis, Ulcerative; Immune System Diseases; Spondylitis; Spondylitis, Ankylosing
TNF-alpha inhibitor
Small molecule
Approved
IMMUNE SYSTEM; OTHER; RESPIRATORY
INJECTION
Renal Insufficiency, Chronic; Gram-Positive Bacterial Infections; Infections; Bacteremia; Bacterial Infections; Pneumonia, Bacterial; Staphylococcal Skin Infections
Unknown
Small molecule
Approved
OTHER
TOPICAL
Ectoparasitic Infestations; Lice Infestations; Otitis Externa
Unknown
Small molecule
Approved
HEMATOLOGY; OTHER
ORAL
Carcinoma; Kidney Diseases; Kidney Failure, Chronic; Dyspnea; Edema, Cardiac; Liver Cirrhosis; Cardiovascular Diseases; Heart Failure; Hyponatremia; Inappropriate ADH Syndrome; Polycystic Kidney, Autosomal Dominant; Polycystic Kidney Diseases
Vasopressin V2 receptor antagonist
Small molecule
Approved
OTHER
ORAL
Barrett Esophagus; Esophagitis, Peptic; Esophagitis; Gastroesophageal Reflux; Heartburn; Peptic Ulcer
Potassium-transporting ATPase inhibitor
Small molecule
Approved
OTHER; PEDIATRICS
ORAL
Tourette Syndrome; Alcoholism; Amphetamine-Related Disorders; Cocaine-Related Disorders; Obesity; Tuberous Sclerosis; Epilepsies, Partial; Epilepsy; Epilepsy, Complex Partial; Spasms, Infantile
Gamma-amino-N-butyrate transaminase inhibitor
Small molecule
Approved
OTHER
SUBLINGUAL
Psychotic Disorders; Stuttering; Bipolar Disorder; Schizophrenia
Dopamine D2 receptor antagonist
Small molecule
Approved
CANCER; IMMUNE SYSTEM; OTHER; UROLOGY AND KIDNEY
ORAL
Acute Coronary Syndrome; Adenocarcinoma; Aging; Breast Neoplasms, Male; Carcinoma, Ovarian Epithelial; Central Nervous System Neoplasms; Esophageal Neoplasms; Fallopian Tube Neoplasms; Gastrointestinal Stromal Tumors; Hamartoma Syndrome, Multiple; Hematologic Diseases; Leukemia; Leukemia, Lymphoid; Leukemia, Myelogenous, Chronic, BCR-ABL Positive; Lymphoma, Non-Hodgkin; Nasopharyngeal Neoplasms; Neoplasm Metastasis; Neoplasms, Plasma Cell; Peritoneal Neoplasms; Precursor Cell Lymphoblastic Leukemia-Lymphoma; Progeria; Sarcoma, Synovial; Uterine Cervical Neoplasms; Adenoma, Islet Cell; Bile Duct Neoplasms; Brain Neoplasms; Carcinoma, Adenoid Cystic; Carcinoma, Hepatocellular; Carcinoma, Medullary; Carcinoma, Neuroendocrine; Carcinoma, Non-Small-Cell Lung; Carcinoma, Squamous Cell; Carcinoma, Transitional Cell; Cholangiocarcinoma; Chondrosarcoma; Colonic Neoplasms; Colorectal Neoplasms; Diffuse Intrinsic Pontine Glioma; Endometrial Neoplasms; Ependymoma; Epilepsy; Gallbladder Neoplasms; Glioblastoma; Glioma; Head and Neck Neoplasms; Hepatitis C; Hodgkin Disease; Hyperaldosteronism; Kidney Diseases; Leukemia, Myeloid, Acute; Liver Neoplasms; Lung Neoplasms; Lymphangioleiomyomatosis; Lymphoma; Lymphoma, B-Cell, Marginal Zone; Lymphoma, Mantle-Cell; Lymphoma, T-Cell, Cutaneous; Macular Degeneration; Mastocytosis, Systemic; Melanoma; Meningioma; Mesothelioma; Multiple Myeloma; Myelodysplastic Syndromes; Neoplasms, Germ Cell and Embryonal; Neurilemmoma; Neurofibromatosis 1; Neurofibromatosis 2; Oligodendroglioma; Osteosarcoma; Ovarian Neoplasms; Paraganglioma; Peutz-Jeghers Syndrome; Polycystic Kidney Diseases; Sarcoma; Sarcoma, Kaposi; Small Cell Lung Carcinoma; Sturge-Weber Syndrome; Thymus Neoplasms; Thyroid Neoplasms; Triple Negative Breast Neoplasms; Tuberculosis; Urinary Bladder Neoplasms; Uterine Neoplasms; Uveal Melanoma; Uveitis; Waldenstrom Macroglobulinemia; Carcinoid Tumor; Carcinoma; Coronary Disease; Coronary Restenosis; Cytomegalovirus Infections; Endocardial Cushion Defects; Graft vs Host Disease; Infections; Kidney Failure, Chronic; Kidney Neoplasms; Lymphoma, Large B-Cell, Diffuse; Malignant Carcinoid Syndrome; Polycystic Kidney, Autosomal Dominant; Prostatic Neoplasms, Castration-Resistant; Renal Insufficiency; Renal Insufficiency, Chronic; Skin Neoplasms; Stomach Neoplasms; Angiomyolipoma; Astrocytoma; Breast Neoplasms; Carcinoma, Renal Cell; Neoplasms; Neuroendocrine Tumors; Pancreatic Neoplasms; Tuberous Sclerosis
FK506-binding protein 1A inhibitor
Enzyme
Approved
NEUROLOGY DRUGS & NERVOUS SYSTEM; OTHER
INTRAVENOUS
Gaucher Disease
Glucocerebroside hydrolytic enzyme
Small molecule
Approved
OTHER; RESPIRATORY
INTRAVENOUS
Kidney Diseases; Systemic Inflammatory Response Syndrome; Sepsis; Urinary Tract Infections; Infections; Pneumonia, Bacterial; Bacterial Infections
Bacterial penicillin-binding protein inhibitor
Small molecule
Approved
DERMATOLOGY; OTHER
INTRAVENOUS
Neurofibromatosis 1; Hemorrhoids; Macular Degeneration; Melanoma; Tendinopathy; Tennis Elbow; Venous Insufficiency; Telangiectasis; Varicose Veins
Unknown
Small molecule
Approved
CANCER; DERMATOLOGY; OTHER
TOPICAL
Cheilitis; Molluscum Contagiosum; Warts; Carcinoma; Carcinoma, Basal Cell; Carcinoma, Squamous Cell; Condylomata Acuminata; Keratosis; Keratosis, Seborrheic; Skin Diseases; Keratosis, Actinic
Unknown
Small molecule
Approved
OTHER
INJECTION; INTRAVENOUS; IV (INFUSION)
Brain Neoplasms; Glioma; Adrenal Cortex Neoplasms; Breast Neoplasms; Carcinoma, Non-Small-Cell Lung; Carcinoma, Squamous Cell; Carcinoma, Transitional Cell; Colorectal Neoplasms; Glioblastoma; Head and Neck Neoplasms; Liposarcoma; Ovarian Neoplasms; Penile Neoplasms; Small Cell Lung Carcinoma; Stomach Neoplasms; Testicular Neoplasms; Urinary Bladder Neoplasms; Neoplasms; Prostatic Neoplasms; Prostatic Neoplasms, Castration-Resistant
Tubulin inhibitor