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Total: 6532
Small molecule
Approved
Unknown
ORAL
Esophageal Neoplasms; Gastrointestinal Stromal Tumors; Liver Diseases; Meningioma; Multiple Myeloma; Oropharyngeal Neoplasms; Pancreatic Neoplasms; Rectal Neoplasms; Stomach Neoplasms; Uveal Melanoma; Carcinoma, Squamous Cell; Colorectal Neoplasms; Endometrial Neoplasms; Head and Neck Neoplasms; Lymphedema; Ovarian Neoplasms; Squamous Cell Carcinoma of Head and Neck; Triple Negative Breast Neoplasms; Breast Neoplasms; Neoplasms
PI3-kinase p110-alpha subunit inhibitor
Small molecule
Approved
Unknown
INTRAVENOUS
Alcoholism; Parkinson Disease; Psychotic Disorders; Alzheimer Disease; Brain Injuries; Essential Tremor; Stress Disorders, Post-Traumatic; Tinnitus; Status Epilepticus; Depression, Postpartum; Depressive Disorder
GABA-A receptor; anion channel positive allosteric modulator
Small molecule
Approved
Unknown
Unknown
Unknown
Unknown
Small molecule
Approved
Unknown
Unknown
Unknown
Membrane staining aid in ophthalmic surgery
Small molecule
Approved
Unknown
Unknown
Cystic Fibrosis
Cystic fibrosis transmembrane conductance regulator positive modulator
Small molecule
Approved
Unknown
ORAL
Fascioliasis; Helminthiasis
Unknown
Small molecule
Approved
Unknown
ORAL
Amyotrophic Lateral Sclerosis; Liver Diseases; Substance-Related Disorders; Parkinson Disease
Adenosine A2a receptor antagonist
Small molecule
Approved
Unknown
Unknown
Unknown
Unknown
Small molecule
Approved
Unknown
Unknown
Borderline Personality Disorder; Schizophrenia
Unknown
Small molecule
Approved
Unknown
ORAL
Amyloid Neuropathies, Familial; Amyloidosis; Amyloidosis, Familial; Cardiomyopathies
Transthyretin stabiliser
Small molecule
Approved
Unknown
Unknown
Leukemia; Anemia, Hemolytic, Autoimmune; Castleman Disease; Immunoglobulin G4-Related Disease; Kidney Diseases; Leukemia, Lymphoid; Lupus Nephritis; Lymphoma; Lymphoma, B-Cell, Marginal Zone; Neuromyelitis Optica; Paraproteinemias; Purpura, Thrombocytopenic, Idiopathic; Severe Acute Respiratory Syndrome; Leukemia, Lymphocytic, Chronic, B-Cell; Lymphohistiocytosis, Hemophagocytic; Lymphoma, Follicular; Lymphoma, Large B-Cell, Diffuse; Lymphoma, Non-Hodgkin; Lymphoma, Mantle-Cell; Neoplasms; Waldenstrom Macroglobulinemia
Tyrosine-protein kinase BTK inhibitor
Small molecule
Approved
Unknown
Unknown
Hyperphosphatemia; Irritable Bowel Syndrome; Constipation
Unknown
Small molecule
Approved
Unknown
Unknown
Kidney Diseases; Substance-Related Disorders; Alcoholism; Child Development Disorders, Pervasive; Prader-Willi Syndrome; Schizophrenia; Idiopathic Hypersomnia; Narcolepsy; Parkinson Disease
Histamine H3 receptor inverse agonist
Small molecule
Approved
Unknown
Unknown
Unknown
Unknown
Small molecule
Approved
Unknown
ORAL
Glioma; Leukemia, Myeloid, Acute; Uveal Melanoma; Carcinoma, Lobular; Hematologic Neoplasms; Melanoma; Thyroid Neoplasms; Carcinoma, Non-Small-Cell Lung; Neoplasms
ALK tyrosine kinase receptor inhibitor
Small molecule
Approved
Unknown
ORAL
Breast Neoplasms; Granulosa Cell Tumor; Salivary Gland Neoplasms; Neoplasms; Prostatic Neoplasms; Prostatic Neoplasms, Castration-Resistant
Androgen Receptor antagonist
Small molecule
Approved
Unknown
Unknown
Migraine Disorders
Calcitonin gene-related peptide type 1 receptor antagonist
Small molecule
Approved
Unknown
ORAL
Amyloidosis; Amyloidosis, Familial; Carcinoma, Hepatocellular; Carcinoma, Non-Small-Cell Lung; Colorectal Neoplasms; Diabetic Foot; Fallopian Tube Neoplasms; Gliosarcoma; Hematologic Neoplasms; Leukemia; Leukemia, Biphenotypic, Acute; Leukemia, Myelogenous, Chronic, BCR-ABL Positive; Precursor Cell Lymphoblastic Leukemia-Lymphoma; Rectal Neoplasms; Sarcoma; Triple Negative Breast Neoplasms; Urinary Bladder Neoplasms; Breast Neoplasms; Carcinoma, Squamous Cell; Glioblastoma; Liposarcoma; Lymphoma; Lymphoma, Follicular; Lymphoma, T-Cell, Peripheral; Melanoma; Myelodysplastic Syndromes; Ovarian Neoplasms; Paraganglioma; Prostatic Neoplasms, Castration-Resistant; Severe Acute Respiratory Syndrome; Small Cell Lung Carcinoma; Thymoma; Thymus Neoplasms; Endometrial Neoplasms; Leukemia, Myeloid, Acute; Primary Myelofibrosis; Lymphoma, Large B-Cell, Diffuse; Multiple Myeloma; Neoplasms
Exportin-1 inhibitor
Small molecule
Approved
Unknown
ORAL
Amyloid Neuropathies, Familial; Polyneuropathies; Amyloidosis; Amyloidosis, Familial; Cardiomyopathies
Transthyretin stabiliser
Small molecule
Approved
Unknown
Unknown
Pneumonia, Bacterial; Sepsis; Gram-Negative Bacterial Infections; Infections; Urinary Tract Infections; Pneumonia; Bacterial Infections
Bacterial penicillin-binding protein inhibitor
Small molecule
Approved
Unknown
Unknown
Kidney Diseases; Liver Diseases; Acute Lung Injury; Idiopathic Pulmonary Fibrosis; Anemia; Anemia, Hemolytic; Anemia, Sickle Cell
Hemoglobin HbA positive modulator
Small molecule
Approved
Unknown
Unknown
Kidney Diseases; Liver Diseases; Dermatomyositis; Multiple Sclerosis, Relapsing-Remitting; Polymyositis; Multiple Sclerosis, Chronic Progressive; Multiple Sclerosis
Sphingosine 1-phosphate receptor Edg-1 agonist
Small molecule
Approved
Unknown
Unknown
Unknown
Ultrasound contrast agent
Small molecule
Approved
Unknown
Unknown
Cystic Fibrosis; Pneumonia; Bacterial Infections
Unknown
Small molecule
Approved
Unknown
Unknown
Arthritis, Rheumatoid; Gastrointestinal Stromal Tumors; Leukemia, Myeloid, Acute; Liver Diseases; Neurilemmoma; Prostatic Neoplasms; Breast Neoplasms; Glioblastoma; Hemangiosarcoma; Hodgkin Disease; Melanoma; Prostatic Neoplasms, Castration-Resistant; Synovitis, Pigmented Villonodular; Neoplasms
Macrophage colony stimulating factor receptor inhibitor
Small molecule
Approved
Unknown
ORAL
Disorders of Excessive Somnolence; Feeding and Eating Disorders; Narcolepsy; Sleep Apnea, Obstructive; Attention Deficit Disorder with Hyperactivity
Unknown
Small molecule
Approved
Unknown
Unknown
Gram-Negative Bacterial Infections; Pneumonia, Bacterial; Urinary Tract Infections
Bacterial penicillin-binding protein inhibitor
Small molecule
Approved
Unknown
Unknown
Peripheral Arterial Disease; Immune System Diseases; Multiple Sclerosis; Multiple Sclerosis, Relapsing-Remitting
Kelch-like ECH-associated protein 1 inhibitor
Small molecule
Approved
Unknown
Unknown
Cushing Syndrome; Glioblastoma; Glioma; Parkinson Disease; Pheochromocytoma; Paraganglioma
Diagnostic agent
Small molecule
Approved
Unknown
ORAL
Breast Neoplasms; Carcinoma, Hepatocellular; Liver Diseases; Lymphoma; Carcinoma, Non-Small-Cell Lung; Carcinoma, Squamous Cell; Multiple Myeloma; Prostatic Neoplasms; Prostatic Neoplasms, Castration-Resistant; Carcinoma, Transitional Cell; Neoplasms; Urinary Bladder Neoplasms
Fibroblast growth factor receptor inhibitor
Small molecule
Approved
Unknown
Unknown
Hypertension; Cardiovascular Diseases
Unknown
Small molecule
Approved
Unknown
Unknown
Hypertension
Voltage-gated L-type calcium channel blocker
Small molecule
Approved
Unknown
ORAL
Lupus Erythematosus, Systemic; Alopecia Areata; Arthritis, Juvenile; Arthritis, Psoriatic; Arthritis, Rheumatoid; Colitis, Ulcerative; Crohn Disease; Dermatitis, Atopic; Giant Cell Arteritis; Hidradenitis Suppurativa; Spondylitis, Ankylosing; Takayasu Arteritis; Vitiligo
Unknown
Small molecule
Approved
Unknown
Unknown
Communicable Diseases; Sepsis; Hematologic Neoplasms; Bacterial Infections; Pneumonia, Bacterial; Intraabdominal Infections; Pyelonephritis; Urinary Tract Infections
Bacterial beta-lactamase TEM inhibitor
Small molecule
Approved
Unknown
Unknown
Alzheimer Disease; Bipolar Disorder; Depressive Disorder, Major; Schizophrenia; Psychotic Disorders
Dopamine D2 receptor antagonist