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Total: 6532
Small molecule
Approved
Unknown
Unknown
Unknown
GABA-B receptor agonist
Small molecule
Approved
Unknown
Unknown
Amyotrophic Lateral Sclerosis; Glycogen Storage Disease Type I; Metabolic Diseases; Migraine Disorders; Pyruvate Dehydrogenase Complex Deficiency Disease; Ataxia Telangiectasia; Glycogen Storage Disease Type V; Glycogen Storage Disease Type VII; Hemiplegia; Huntington Disease; Hypoadrenocorticism, Familial; Rett Syndrome
Supplement
Small molecule
Approved
Unknown
Unknown
Anesthesia; Liver Diseases; Substance-Related Disorders; Parkinson Disease; Precursor Cell Lymphoblastic Leukemia-Lymphoma; Atrial Fibrillation
Unknown
Small molecule
Approved
Unknown
Unknown
Atrophy; Muscular Atrophy, Spinal
SMN2 pre-mRNA positive modulator
Small molecule
Approved
Unknown
Unknown
Breast Neoplasms; Carcinoma, Hepatocellular; Friedreich Ataxia; Idiopathic Pulmonary Fibrosis; Neoplasms; Colorectal Neoplasms; Conjunctivitis, Allergic; Crohn Disease; Intestinal Neoplasms; Cytomegalovirus Infections; Fever; Malaria, Falciparum; Malaria, Vivax; Schistosomiasis; Schistosomiasis haematobia; Severe Acute Respiratory Syndrome; Malaria
Unknown
Small molecule
Approved
Unknown
Unknown
Breast Neoplasms; Carcinoma, Lobular; Uterine Neoplasms
Unknown
Small molecule
Approved
Unknown
Unknown
Gastrointestinal Stromal Tumors; Neoplasms
Platelet-derived growth factor receptor alpha inhibitor
Small molecule
Approved
Unknown
Unknown
Unknown
GABA-B receptor agonist
Small molecule
Approved
Unknown
Unknown
Autoimmune Diseases; HIV Infections
Envelope polyprotein GP160 inhibitor
Small molecule
Approved
Unknown
Unknown
Angioedema; Angioedemas, Hereditary
Plasma kallikrein inhibitor
Small molecule
Approved
Unknown
Unknown
Hypogonadism; Endometriosis; Leiomyoma; Pain; Prostatic Neoplasms, Castration-Resistant; Neoplasms; Prostatic Neoplasms
Gonadotropin-releasing hormone receptor antagonist
Small molecule
Approved
Unknown
Unknown
Liver Diseases; Renal Insufficiency; Adenocarcinoma, Follicular; Carcinoma, Medullary; Carcinoma, Non-Small-Cell Lung; Neoplasms; Thyroid Neoplasms
Coiled-coil domain-containing protein 6/Tyrosine-protein kinase receptor RET inhibitor
Small molecule
Approved
Unknown
Unknown
Cushing Syndrome; Pituitary ACTH Hypersecretion
Cytochrome P450 11B1 inhibitor
Small molecule
Approved
Unknown
Unknown
Neuroblastoma; Trypanosomiasis, African; Chagas Disease; Leishmaniasis; Trypanosomiasis
DNA inhibitor
Small molecule
Approved
Unknown
Unknown
Glioma; Leukemia, Mast-Cell; Leukemia, Myeloid, Acute; Mastocytosis, Systemic; Gastrointestinal Stromal Tumors; Neoplasms
Platelet-derived growth factor receptor alpha inhibitor
Small molecule
Approved
Unknown
Unknown
Breast Neoplasms
Diagnostic agent
Small molecule
Approved
Unknown
Unknown
Anorexia Nervosa; Depressive Disorder, Major; Obsessive-Compulsive Disorder; Renal Insufficiency, Chronic; Bipolar Disorder; Nausea; Anxiety; Dementia; Depressive Disorder; Schizophrenia; Postoperative Nausea and Vomiting; Psychotic Disorders
Dopamine receptors; D2 & D3 antagonist
Small molecule
Approved
Unknown
Unknown
Unknown
GABA-B receptor agonist
Small molecule
Approved
Unknown
Unknown
Astrocytoma; Colonic Neoplasms; Glioma; Heart Failure; Leukemia, Myelogenous, Chronic, BCR-ABL Positive; Optic Nerve Glioma; Precursor Cell Lymphoblastic Leukemia-Lymphoma; Rectal Neoplasms; Sarcoma, Kaposi; Urinary Bladder Neoplasms; Adenocarcinoma; Adenocarcinoma, Follicular; Bile Duct Neoplasms; Biliary Tract Neoplasms; Breast Neoplasms; Carcinoma, Squamous Cell; Cholangiocarcinoma; Colorectal Neoplasms; Gallbladder Neoplasms; Liver Neoplasms; Lung Neoplasms; Lymphoma, Large B-Cell, Diffuse; Melanoma; Multiple Myeloma; Neurilemmoma; Neurofibroma, Plexiform; Neurofibromatosis 1; Pancreatic Neoplasms; Sarcoma; Stomach Neoplasms; Triple Negative Breast Neoplasms; Uterine Neoplasms; Carcinoma, Non-Small-Cell Lung; Thyroid Neoplasms; Uveal Melanoma; Neoplasms
Unknown
Small molecule
Approved
Unknown
Unknown
Kidney Diseases; Liver Diseases; Sleep Apnea, Obstructive; Alzheimer Disease; Sleep Disorders, Circadian Rhythm; Alcoholism; Epilepsy; Sleep Wake Disorders; Sleep Initiation and Maintenance Disorders
Orexin receptor 1 antagonist
Small molecule
Approved
Unknown
Unknown
Migraine Disorders
Calcitonin gene-related peptide type 1 receptor antagonist
Small molecule
Approved
Unknown
ORAL
Substance-Related Disorders; Migraine Disorders
Serotonin 1f (5-HT1f) receptor agonist
Small molecule
Approved
Unknown
Unknown
Diabetes Mellitus, Type 2; Lipid Metabolism Disorders; Hyperlipidemias; Atherosclerosis; Cardiovascular Diseases; Coronary Artery Disease; Dyslipidemias; Hypercholesterolemia; Hyperlipoproteinemia Type II
ATP-citrate synthase inhibitor
Small molecule
Approved
Unknown
Unknown
Acute Pain; Pain
Mu opioid receptor agonist
Small molecule
Approved
Unknown
Unknown
Migraine Disorders
Serotonin 1f (5-HT1f) receptor agonist
Small molecule
Approved
Unknown
Unknown
Parkinson Disease
Catechol O-methyltransferase inhibitor
Small molecule
Approved
Unknown
Unknown
Carcinoma, Squamous Cell; Leukemia; Leukemia, Myeloid; Leukemia, Myelomonocytic, Chronic; Lymphoma, T-Cell, Peripheral; Mastocytosis, Systemic; Neoplasms; Prostatic Neoplasms; Triple Negative Breast Neoplasms; Leukemia, Myeloid, Acute; Myelodysplastic Syndromes
Cytidine deaminase inhibitor
Small molecule
Approved
Unknown
Unknown
Unknown
Unknown
Small molecule
Approved
Unknown
Unknown
Leukemia, Myeloid, Acute; Breast Neoplasms; Carcinoma, Non-Small-Cell Lung; Colorectal Neoplasms; Endometrial Neoplasms; Liposarcoma; Myeloproliferative Disorders; Pancreatic Neoplasms; Stomach Neoplasms; Urinary Bladder Neoplasms; Urogenital Neoplasms; Cholangiocarcinoma; Neoplasms
Fibroblast growth factor receptor 1 inhibitor
Small molecule
Approved
Unknown
Unknown
Colitis, Ulcerative; Multiple Sclerosis; Multiple Sclerosis, Relapsing-Remitting
Sphingosine 1-phosphate receptor Edg-1 modulator
Small molecule
Approved
Unknown
Unknown
Breast Neoplasms; Glioblastoma; Liver Diseases; Carcinoma, Hepatocellular; Kidney Neoplasms; Lung Neoplasms; Melanoma; Carcinoma, Non-Small-Cell Lung; Sarcoma; Neoplasms
Hepatocyte growth factor receptor inhibitor
Small molecule
Approved
Unknown
Unknown
Carcinoma, Non-Small-Cell Lung; Carcinoma, Squamous Cell; Leukemia, Myeloid, Acute; Lymphoma, Large B-Cell, Diffuse; Multiple Myeloma; Prostatic Neoplasms; Urinary Bladder Neoplasms; Lymphoma; Mesothelioma; Lymphoma, Follicular; Sarcoma; Neoplasms
Unknown
Small molecule
Approved
Unknown
Unknown
Neurodegenerative Diseases; Alzheimer Disease; Chronic Traumatic Encephalopathy; Cognitive Dysfunction
Diagnostic agent
Small molecule
Approved
Unknown
Unknown
Carcinoma, Non-Small-Cell Lung
Hepatocyte growth factor receptor inhibitor
Small molecule
Approved
Unknown
Unknown
Ectoparasitic Infestations; Lice Infestations
Copper sequestering agent