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Total: 6532
Small molecule
Approved
Unknown
Unknown
Cholestasis; Liver Cirrhosis, Biliary; Non-alcoholic Fatty Liver Disease; Alagille Syndrome; Biliary Atresia; Cholestasis, Intrahepatic
Ileal bile acid transporter inhibitor
Small molecule
Approved
Unknown
Unknown
Kidney Diseases; Liver Diseases; Lung Neoplasms; Carcinoma, Non-Small-Cell Lung; Neoplasms
Epidermal growth factor receptor erbB1 inhibitor
Small molecule
Approved
Unknown
Unknown
Invasive Fungal Infections; Candidiasis, Vulvovaginal
1,3-beta-glucan synthase inhibitor
Small molecule
Approved
Unknown
Unknown
Migraine Disorders
Calcitonin gene-related peptide type 1 receptor antagonist
Small molecule
Approved
Unknown
Unknown
Liver Diseases; Renal Insufficiency, Chronic; Carcinoma, Renal Cell; Hemangioblastoma; Neoplasms; Neuroendocrine Tumors; von Hippel-Lindau Disease
Endothelial PAS domain-containing protein 1 inhibitor
Small molecule
Approved
Unknown
Unknown
Hodgkin Disease; Leukemia, Lymphocytic, Chronic, B-Cell; Lymphoma, Follicular; Lymphoma, Large B-Cell, Diffuse; Lymphoma, Mantle-Cell; Lymphoma, Non-Hodgkin; Waldenstrom Macroglobulinemia; Neoplasms
Unknown
Small molecule
Approved
Unknown
Unknown
Autoimmune Diseases; Liver Diseases; Multiple Myeloma; Graft vs Host Disease; Idiopathic Pulmonary Fibrosis; Psoriasis; Scleroderma, Diffuse; Bronchiolitis Obliterans Syndrome; Immune System Diseases
Rho-associated protein kinase 2 inhibitor
Small molecule
Approved
Unknown
Unknown
Breast Neoplasms; Carcinoma, Non-Small-Cell Lung; Cholangiocarcinoma; Carcinoma, Hepatocellular; Colorectal Neoplasms; Fallopian Tube Neoplasms; Glioblastoma; Ovarian Neoplasms; Prostatic Neoplasms, Castration-Resistant; Sarcoma; Carcinoma, Renal Cell; Neoplasms
Vascular endothelial growth factor receptor inhibitor
Small molecule
Approved
Unknown
Unknown
Neoplasms; Breast Neoplasms; Carcinoma, Hepatocellular; Diagnostic Imaging; Genital Neoplasms, Female; Positron-Emission Tomography; Prostatic Neoplasms
Diagnostic agent
Small molecule
Approved
Unknown
Unknown
Depressive Disorder
Unknown
Small molecule
Approved
Unknown
Unknown
Contraception; Hot Flashes; Menopause; Vulvovaginitis; Breast Neoplasms; Prostatic Neoplasms; Pregnancy
Estrogen receptor agonist
Small molecule
Approved
Unknown
Unknown
Multiple Myeloma; Neoplasms
Unknown
Small molecule
Approved
Unknown
Unknown
Idiopathic Hypersomnia
Dopamine transporter inhibitor
Small molecule
Approved
Unknown
Unknown
Chagas Disease; Infections; Leishmaniasis, Visceral; Leishmaniasis; Trypanosomiasis; Trypanosomiasis, African
Cytotoxic
Small molecule
approved
Unknown
Unknown
Cytomegalovirus Infections; Virus Diseases
Phosphotransferase pUL97 inhibitor
Small molecule
Approved
Unknown
Unknown
Diabetes Mellitus; Diabetic Nephropathies; Heart Failure; Cardiovascular Diseases; Diabetes Mellitus, Type 2; Renal Insufficiency, Chronic
Mineralocorticoid receptor antagonist
Small molecule
Approved
Unknown
Unknown
Invasive Fungal Infections; Mycoses; Aspergillosis; Aspergillosis, Allergic Bronchopulmonary; Blastomycosis; Candidemia; Candidiasis, Invasive; Candidiasis, Vulvovaginal; Coccidioidomycosis; Histoplasmosis; Vulvovaginitis
1,3-beta-glucan synthase inhibitor
Small molecule
Approved
Unknown
Unknown
Attention Deficit Disorder with Hyperactivity
Norepinephrine transporter inhibitor
Small molecule
Approved
Unknown
Unknown
Metal Metabolism, Inborn Errors
Unknown
Small molecule
Approved
Unknown
Unknown
Liver Diseases; Renal Insufficiency, Chronic; Atypical Hemolytic Uremic Syndrome; Glomerulonephritis, IGA; Hidradenitis Suppurativa; Vasculitis; Anti-Neutrophil Cytoplasmic Antibody-Associated Vasculitis; Granulomatosis with Polyangiitis; Microscopic Polyangiitis
C5a anaphylatoxin chemotactic receptor antagonist
Small molecule
Approved
Unknown
Unknown
Mycoses; Onychomycosis; Tinea Pedis; Candidiasis, Vulvovaginal
Lanosterol 14-alpha demethylase inhibitor
Small molecule
Approved
Unknown
Unknown
Central Nervous System Diseases; Brain Neoplasms; Hernias, Diaphragmatic, Congenital; Magnetic Resonance Imaging
Diagnostic agent
Small molecule
Approved
Unknown
Unknown
Dermatitis, Atopic; Psoriasis
Aryl hydrocarbon receptor agonist
Small molecule
Approved
Unknown
Unknown
Food Hypersensitivity; Kidney Diseases; Liver Diseases; Stevens-Johnson Syndrome; Diabetes Mellitus, Type 1; Granuloma Annulare; Psoriasis; Sarcoidosis; Dermatitis, Atopic; Eczema
Tyrosine-protein kinase JAK1 inhibitor
Small molecule
Approved
Unknown
Unknown
Liver Diseases; Anemia, Sickle Cell; Thalassemia; alpha-Thalassemia; beta-Thalassemia
Pyruvate kinase isozymes R/L activator
Small molecule
Investigational
Unknown
Unknown
Carcinoma, Non-Small-Cell Lung; Carcinoma, Hepatocellular; Urinary Bladder Neoplasms; Biliary Tract Neoplasms; Sarcoma; Cholangiocarcinoma; Neoplasms
Fibroblast growth factor receptor inhibitor
Small molecule
Approved
Unknown
Unknown
Liver Diseases; Pulmonary Disease, Chronic Obstructive; Renal Insufficiency; Sleep Apnea, Obstructive; Stress Disorders, Post-Traumatic; Sleep Initiation and Maintenance Disorders
Orexin receptor antagonist
Small molecule
Approved
Unknown
Unknown
HIV Infections; Virus Diseases
Structural capsid protein inhibitor
Small molecule
Approved
Unknown
Unknown
Breast Neoplasms; Carcinoma, Non-Small-Cell Lung; Graft vs Host Disease; Leukemia, Lymphocytic, Chronic, B-Cell; Leukemia, Myelomonocytic, Chronic; Liver Diseases; Myelodysplastic Syndromes; Colorectal Neoplasms; Hodgkin Disease; Leukemia; Leukemia, Myeloid, Acute; Lymphoma; Lymphoma, Mantle-Cell; Myeloproliferative Disorders; Primary Myelofibrosis; Prostatic Neoplasms, Castration-Resistant; Severe Acute Respiratory Syndrome; Neoplasms
Tyrosine-protein kinase JAK2 inhibitor
Small molecule
Approved
Unknown
Unknown
Epilepsies, Partial; Epilepsy, Complex Partial; Fragile X Syndrome; Smoking Cessation; Stress Disorders, Post-Traumatic; Status Epilepticus; Tuberous Sclerosis; Epilepsy; Epileptic Syndromes; Seizures; Spasms, Infantile
GABA-A receptor; anion channel positive allosteric modulator
Small molecule
Approved
Unknown
Unknown
Heart Failure; Cardiomyopathy, Hypertrophic; Cardiovascular Diseases
Cardiac myosin inhibitor
Small molecule
Small molecule
Unknown
Unknown
Myelodysplastic Syndromes; Leukemia, Myeloid, Acute
Isocitrate dehydrogenase [NADP] cytoplasmic inhibitor
Small molecule
Approved
Unknown
Unknown
Immune System Diseases; Inflammation; Kidney Diseases; Liver Diseases; Pyoderma; Alopecia Areata; Colitis, Ulcerative; Hidradenitis Suppurativa; Lichen Planus; Lupus Erythematosus, Cutaneous; Lupus Erythematosus, Systemic; Lupus Nephritis; Pityriasis Rubra Pilaris; Arthritis, Psoriatic; Sjogren's Syndrome; Vitiligo; Psoriasis
Tyrosine-protein kinase TYK2 negative allosteric modulator
Small molecule
Approved
Unknown
Unknown
Adenocarcinoma; Breast Neoplasms; Endometrial Neoplasms; Kidney Diseases; Liver Diseases; Carcinoma, Hepatocellular; Carcinoma, Renal Cell; Colonic Neoplasms; Esophageal Neoplasms; Lung Neoplasms; Pancreatic Neoplasms; Rectal Neoplasms; Sarcoma; Carcinoma, Non-Small-Cell Lung; Stomach Neoplasms; Colorectal Neoplasms; Neoplasms
Vascular endothelial growth factor receptor inhibitor
Small molecule
Approved
Unknown
Unknown
Breast Neoplasms; Fibroma; Multiple Myeloma; Pancreatic Neoplasms; Desmoid Tumors; Neoplasms
Gamma-secretase inhibitor