Display Options:
Total: 6532
Small molecule
Approved
Unknown
Unknown
Amyloidosis; Amyloid Neuropathies, Familial; Cardiovascular Diseases
Transthyretin stabiliser
Small molecule
Approved
Unknown
Unknown
Liver Diseases; Lung Neoplasms; Carcinoma, Non-Small-Cell Lung; Neoplasms
Epidermal growth factor receptor erbB1 inhibitor
Small molecule
Approved
Unknown
Unknown
Unknown
Unknown
Small molecule
Investigational
Unknown
Unknown
Bone Marrow Failure Disorders; Carcinoma, Non-Small-Cell Lung; Carcinoma, Squamous Cell; Graft vs Host Disease; Hematologic Neoplasms; Hemoglobinuria; Hodgkin Disease; Lymphoma, Non-Hodgkin; Multiple Myeloma; Nijmegen Breakage Syndrome; Shwachman-Diamond Syndrome; Leukemia, Myeloid, Acute; Melanoma; Myelodysplastic Syndromes; Ovarian Neoplasms; Precursor Cell Lymphoblastic Leukemia-Lymphoma; Sarcoma, Ewing; Hematopoietic Stem Cell Transplantation; Neoplasms
DNA cross-linking agent
Small molecule
Approved
Unknown
Unknown
Colorectal Neoplasms; Glioma; Carcinoma, Non-Small-Cell Lung; Neoplasms; Neurofibromatosis 1
Dual specificity mitogen-activated protein kinase kinase 1 inhibitor
Small molecule
Investigational
Unknown
Unknown
Unknown
Unknown
Small molecule
Investigational
Unknown
Unknown
Hepatitis C
Unknown
Small molecule
Investigational
Unknown
Unknown
Unknown
Glutamate receptor ionotropic AMPA antagonist
Small molecule
Investigational
Unknown
Unknown
Unknown
Unknown
Small molecule
Investigational
Unknown
Unknown
Unknown
Unknown
Small molecule
Investigational
Unknown
Unknown
Depressive Disorder, Major; Depressive Disorder, Treatment-Resistant
Unknown
Small molecule
Investigational
Unknown
Unknown
Glioblastoma
Unknown
Small molecule
Investigational
Unknown
Unknown
Breast Neoplasms
Unknown
Small molecule
Investigational
Unknown
Unknown
Unknown
Unknown
Small molecule
Investigational
Unknown
Unknown
Venous Thrombosis
Unknown
Small molecule
Investigational
Unknown
Unknown
Unknown
Unknown
Small molecule
Investigational
Unknown
Unknown
Unknown
Adenosine A2b receptor antagonist
Small molecule
Investigational
Unknown
Unknown
Adrenoleukodystrophy
Unknown
Small molecule
Investigational
Unknown
Unknown
Multiple Myeloma
Unknown
Small molecule
Investigational
Unknown
Unknown
Unknown
Unknown
Small molecule
Investigational
Unknown
Unknown
Unknown
Vanilloid receptor antagonist
Small molecule
Investigational
Unknown
Unknown
Unknown
Tyrosine-protein kinase JAK1 inhibitor
Small molecule
Investigational
Unknown
Unknown
Lymphoma
Unknown
Small molecule
Investigational
Unknown
Unknown
Unknown
Unknown
Small molecule
Investigational
Unknown
Unknown
Unknown
Glucocorticoid receptor antagonist
Small molecule
Investigational
Unknown
Unknown
Unknown
Unknown
Small molecule
Investigational
Unknown
Unknown
Unknown
Unknown
Small molecule
Investigational
Unknown
Unknown
Desmoplastic Small Round Cell Tumor; Fibroma; Fibrosarcoma; Histiocytoma; Liposarcoma, Myxoid; Myoepithelioma; Neoplasms; Sarcoma; Sarcoma, Clear Cell; Sarcoma, Ewing
Unknown
Small molecule
Investigational
Unknown
Unknown
Sunburn
Unknown
Small molecule
Investigational
Unknown
Unknown
Unknown
Unknown
Small molecule
Investigational
Unknown
Unknown
Gram-Negative Bacterial Infections; Kidney Diseases; Urinary Tract Infections
Unknown
Small molecule
Investigational
Unknown
Unknown
Central Nervous System Neoplasms; Head and Neck Neoplasms
Unknown
Small molecule
Investigational
Unknown
Unknown
Diabetes Mellitus; Diabetes Mellitus, Type 2
Unknown
Small molecule
Investigational
Unknown
Unknown
Lymphedema; Lymphoma
Serine/threonine-protein kinase mTOR inhibitor
Small molecule
Investigational
Unknown
Unknown
Neoplasms
Dual specificity protein kinase TTK inhibitor