Display Options:
Total: 6532
Small molecule
Approved
Unknown
Unknown
Acute Pain
Opioid receptors; mu/kappa/delta agonist
Small molecule
Approved
Unknown
ORAL
Liver Diseases; Thrombocytopenia
Thrombopoietin receptor agonist
Small molecule
Approved
Unknown
Unknown
Unknown
Unknown
Small molecule
Approved
Unknown
ORAL
Bronchiolitis Obliterans Syndrome; Dermatitis, Allergic Contact; Graft vs Host Disease; Neuromyelitis Optica; Brain Injuries; Diabetes Mellitus, Type 1; Diabetic Nephropathies; Giant Cell Arteritis; HIV Infections; Lichen Planus; Liver Cirrhosis, Biliary; Mastitis; Myalgia; Myositis; Psoriasis; Purpura, Thrombocytopenic, Idiopathic; Renal Insufficiency, Chronic; Sjogren's Syndrome; Subarachnoid Hemorrhage; Vitiligo; Alopecia Areata; Arthritis, Juvenile; Dermatitis, Atopic; Dermatomyositis; Influenza, Human; Lupus Erythematosus, Systemic; Pneumonia; Sepsis; Severe Acute Respiratory Syndrome; Uveitis; Arthritis, Rheumatoid
Tyrosine-protein kinase JAK1 inhibitor
Small molecule
Approved
Unknown
Unknown
Carcinoma, Non-Small-Cell Lung; Kidney Diseases; Leukemia; Liver Diseases; Myelodysplastic Syndromes; Leukemia, Myeloid; Leukemia, Myeloid, Acute; Neoplasms
Tyrosine-protein kinase receptor FLT3 inhibitor
Small molecule
Approved
Unknown
ORAL
Kidney Diseases; Liver Diseases; Lung Neoplasms; Lymphoma, Large-Cell, Anaplastic; Ganglioneuroblastoma; Neuroblastoma; Carcinoma, Non-Small-Cell Lung; Lymphoma; Neoplasms
ALK tyrosine kinase receptor inhibitor
Small molecule
Approved
Unknown
INHALATION
Kidney Diseases; Liver Diseases; Lung Diseases, Obstructive; Pulmonary Disease, Chronic Obstructive
Muscarinic acetylcholine receptor M3 antagonist
Small molecule
Approved
Unknown
Unknown
Cystic Fibrosis
Cystic fibrosis transmembrane conductance regulator positive modulator
Small molecule
Approved
Unknown
Unknown
Bronchiolitis Obliterans Syndrome; Hematologic Neoplasms; Lymphoma; Ovarian Neoplasms; Pneumonia; Anemia, Hemolytic, Autoimmune; Glomerulonephritis, IGA; Hidradenitis Suppurativa; Lymphoma, Large B-Cell, Diffuse; Primary Myelofibrosis; Severe Acute Respiratory Syndrome; Arthritis, Rheumatoid; Purpura, Thrombocytopenic, Idiopathic; Hemorrhage
Tyrosine-protein kinase SYK inhibitor
Small molecule
Approved
Unknown
ORAL
Botulism; Multiple Sclerosis; Myasthenia Gravis; Lambert-Eaton Myasthenic Syndrome
Voltage-gated potassium channel blocker
Small molecule
Approved
Unknown
ORAL
Purpura, Thrombocytopenic, Idiopathic; Hemorrhage; Thrombocytopenia
Thrombopoietin receptor agonist
Small molecule
Approved
Unknown
ORAL
Pneumonia; Severe Acute Respiratory Syndrome; Influenza, Human; Virus Diseases
Polymerase acidic protein inhibitor
Small molecule
Approved
Unknown
ORAL
Carcinoma, Pancreatic Ductal; Leukemia; Leukemia, Myeloid; Liver Diseases; Chondrosarcoma; Neoplasms; Paraganglioma; Biliary Tract Neoplasms; Myelodysplastic Syndromes; Cholangiocarcinoma; Leukemia, Myeloid, Acute
Isocitrate dehydrogenase [NADP] cytoplasmic inhibitor
Small molecule
Approved
Unknown
Unknown
Fabry Disease
Alpha-galactosidase A stabiliser
Small molecule
Approved
Unknown
ORAL
Carcinoma, Non-Small-Cell Lung; Neoplasms
Epidermal growth factor receptor erbB1 inhibitor
Small molecule
Approved
Unknown
ORAL
Carcinoma, Pancreatic Ductal; Skin Neoplasms; Carcinoma, Non-Small-Cell Lung; Leukemia, Hairy Cell; Multiple Myeloma; Pancreatic Neoplasms; Pulmonary Disease, Chronic Obstructive; Thyroid Neoplasms; Biliary Tract Neoplasms; Colorectal Neoplasms; Melanoma; Neoplasms
Serine/threonine-protein kinase B-raf inhibitor
Small molecule
Approved
Unknown
Unknown
Liver Diseases; Renal Insufficiency, Chronic; Urinary Tract Infections; Bacterial Infections; Infections
Bacterial 70S ribosome inhibitor
Small molecule
Approved
Unknown
ORAL
Leukemia, Myeloid; Leukemia, Myeloid, Acute
Tyrosine-protein kinase receptor FLT3 inhibitor
Small molecule
Approved
Unknown
Unknown
Diarrhea
DNA-directed RNA polymerase inhibitor
Small molecule
Approved
Unknown
Unknown
Nausea; Vomiting
Neurokinin 1 receptor antagonist
Small molecule
Approved
Unknown
ORAL
Brain Neoplasms; Colonic Neoplasms; Gastrointestinal Stromal Tumors; Glioma; Leukemia; Liver Diseases; Lung Neoplasms; Rectal Neoplasms; Skin Neoplasms; Arthritis, Rheumatoid; Breast Neoplasms; Carcinoma, Non-Small-Cell Lung; Cardiomegaly; Colorectal Neoplasms; Klatskin Tumor; Leukemia, Hairy Cell; Multiple Myeloma; Pancreatic Neoplasms; Thyroid Neoplasms; Triple Negative Breast Neoplasms; Uveal Melanoma; Biliary Tract Neoplasms; Fallopian Tube Neoplasms; Ovarian Neoplasms; Peritoneal Neoplasms; Melanoma; Neoplasms
Dual specificity mitogen-activated protein kinase kinase 1 inhibitor
Small molecule
Approved
Unknown
Unknown
Polycystic Ovary Syndrome; Endometriosis
Gonadotropin-releasing hormone receptor antagonist
Small molecule
Approved
Unknown
Unknown
Acquired Immunodeficiency Syndrome; HIV Infections
Human immunodeficiency virus type 1 integrase inhibitor
Small molecule
Approved
Unknown
Unknown
Colorectal Neoplasms; Leukemia; Leukemia, Myeloid, Acute; Neuroendocrine Tumors; Pancreatic Neoplasms; Carcinoma, Non-Small-Cell Lung; Carcinoma, Renal Cell; Carcinoma, Squamous Cell; Endometrial Neoplasms; Glioblastoma; Hemangiosarcoma; Hereditary Breast and Ovarian Cancer Syndrome; Melanoma; Pheochromocytoma; Prostatic Neoplasms; Small Cell Lung Carcinoma; Triple Negative Breast Neoplasms; Urinary Bladder Neoplasms; Breast Neoplasms; Neoplasms; Ovarian Neoplasms; Prostatic Neoplasms, Castration-Resistant
Poly [ADP-ribose] polymerase-1 inhibitor
Small molecule
Approved
Unknown
Unknown
Diffuse Intrinsic Pontine Glioma; Multiple Myeloma; Thyroid Neoplasms; Neoplasms
Neurotrophic tyrosine kinase receptor inhibitor
Small molecule
Approved
Unknown
ORAL
Infections; Elephantiasis, Filarial; Strongyloidiasis; Helminthiasis; Onchocerciasis
Unknown
Small molecule
Approved
Unknown
ORAL
Kidney Diseases; HIV Infections; Virus Diseases
Human immunodeficiency virus type 1 reverse transcriptase negative allosteric modulator
Small molecule
Approved
Unknown
Unknown
Neuroblastoma; Paraganglioma; Pheochromocytoma
Norepinephrine transporter substrate
Small molecule
Approved
Unknown
TOPICAL
Lymphoma; Ichthyosis, Lamellar; Acne Vulgaris
Retinoic acid receptor gamma agonist
Small molecule
Approved
Unknown
Unknown
Migraine Disorders
Calcitonin gene-related peptide type 1 receptor antagonist
Small molecule
Approved
Unknown
ORAL
Amyloidosis; Amyloidosis, Familial; Carcinoma, Hepatocellular; Carcinoma, Non-Small-Cell Lung; Colorectal Neoplasms; Diabetic Foot; Fallopian Tube Neoplasms; Gliosarcoma; Hematologic Neoplasms; Leukemia; Leukemia, Biphenotypic, Acute; Leukemia, Myelogenous, Chronic, BCR-ABL Positive; Precursor Cell Lymphoblastic Leukemia-Lymphoma; Rectal Neoplasms; Sarcoma; Triple Negative Breast Neoplasms; Urinary Bladder Neoplasms; Breast Neoplasms; Carcinoma, Squamous Cell; Glioblastoma; Liposarcoma; Lymphoma; Lymphoma, Follicular; Lymphoma, T-Cell, Peripheral; Melanoma; Myelodysplastic Syndromes; Ovarian Neoplasms; Paraganglioma; Prostatic Neoplasms, Castration-Resistant; Severe Acute Respiratory Syndrome; Small Cell Lung Carcinoma; Thymoma; Thymus Neoplasms; Endometrial Neoplasms; Leukemia, Myeloid, Acute; Primary Myelofibrosis; Lymphoma, Large B-Cell, Diffuse; Multiple Myeloma; Neoplasms
Exportin-1 inhibitor
Small molecule
Approved
Unknown
Unknown
Kidney Diseases; Liver Diseases; Leukemia, Neutrophilic, Chronic; Myelodysplastic Syndromes; Myeloproliferative Disorders; Primary Myelofibrosis; Neoplasms
Tyrosine-protein kinase JAK2 inhibitor
Small molecule
Approved
Unknown
INTRAVENOUS
Severe Acute Respiratory Syndrome
Supplement
Small molecule
Approved
Unknown
Unknown
Delirium; Kidney Diseases; Liver Diseases; Rhinitis, Allergic, Seasonal; Substance-Related Disorders; Cancer Pain; Depressive Disorder, Treatment-Resistant; Pain; Shock, Septic; Depressive Disorder
Glutamate [NMDA] receptor negative allosteric modulator
Small molecule
Approved
Unknown
ORAL
Anemia; Anemia, Iron-Deficiency
Supplement