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Total: 6532
Small molecule
Approved
Unknown
Unknown
Neurodegenerative Diseases; Alzheimer Disease; Chronic Traumatic Encephalopathy; Cognitive Dysfunction
Diagnostic agent
Small molecule
Approved
Unknown
Unknown
Carcinoma, Squamous Cell; Leukemia; Leukemia, Myeloid; Leukemia, Myelomonocytic, Chronic; Lymphoma, T-Cell, Peripheral; Mastocytosis, Systemic; Neoplasms; Prostatic Neoplasms; Triple Negative Breast Neoplasms; Leukemia, Myeloid, Acute; Myelodysplastic Syndromes
Cytidine deaminase inhibitor
Small molecule
Approved
Unknown
Unknown
Carcinoma, Hepatocellular; Carcinoma, Non-Small-Cell Lung; Leukemia, Myelogenous, Chronic, BCR-ABL Positive; Liver Diseases; Lung Neoplasms; Colonic Neoplasms; Hemangiosarcoma; Stomach Neoplasms; Breast Neoplasms; Colorectal Neoplasms; Neoplasm Metastasis; Neoplasms
Receptor protein-tyrosine kinase erbB-2 inhibitor
Small molecule
Approved
Unknown
Unknown
Angioedema; Angioedemas, Hereditary
Unknown
Small molecule
Approved
Unknown
Unknown
Ectoparasitic Infestations; Lice Infestations
Copper sequestering agent
Small molecule
Approved
Unknown
Unknown
Kidney Diseases; Liver Diseases; Cushing Syndrome; Essential Hypertension; Hyperaldosteronism; Hypertension; Pituitary ACTH Hypersecretion; Adrenal Gland Diseases
Unknown
Small molecule
Approved
Unknown
Unknown
Liver Diseases; Severe Acute Respiratory Syndrome; Colitis, Ulcerative; Crohn Disease; Multiple Sclerosis; Multiple Sclerosis, Relapsing-Remitting
Sphingosine 1-phosphate receptor 5 modulator
Small molecule
Approved
Unknown
Unknown
Thyroid Neoplasms; Carcinoma, Medullary; Carcinoma, Non-Small-Cell Lung; Neoplasms
Coiled-coil domain-containing protein 6/Tyrosine-protein kinase receptor RET inhibitor
Small molecule
Approved
Unknown
Unknown
Alzheimer Disease
Unknown
Small molecule
Approved
Unknown
Unknown
Constipation
Osmotic agent
Small molecule
Approved
Unknown
Unknown
Irritable Bowel Syndrome; Pain; Psoriasis; Trigeminal Neuralgia; Migraine Disorders; Sinusitis; Temporomandibular Joint Disorders
Calcitonin gene-related peptide type 1 receptor antagonist
Small molecule
Approved
Unknown
Unknown
Astrocytoma; Central Nervous System Neoplasms; Colorectal Neoplasms; Glioblastoma; Gliosarcoma; Head and Neck Neoplasms; Lymphoma; Breast Neoplasms; Leukemia, Myelogenous, Chronic, BCR-ABL Positive; Liver Neoplasms; Ovarian Neoplasms; Urethral Neoplasms; Urinary Bladder Neoplasms; Carcinoma, Non-Small-Cell Lung; Hepatitis D; Leukemia, Myelomonocytic, Chronic; Myelodysplastic Syndromes; Neoplasm Metastasis; Laminopathies; Progeria
Protein farnesyltransferase inhibitor
Small molecule
Approved
Unknown
Unknown
HIV Infections; Virus Diseases
Envelope polyprotein GP160 inhibitor
Small molecule
Approved
Unknown
Unknown
Pneumonia, Viral; Hemorrhagic Fever, Ebola; Respiratory Distress Syndrome; Influenza, Human; Pneumonia; Coronavirus Infections; COVID-19; Severe Acute Respiratory Syndrome; Virus Diseases
Replicase polyprotein 1ab inhibitor
Small molecule
Approved
Unknown
Unknown
Anesthesia; Pain; Conscious Sedation
GABA-A receptor; anion channel positive allosteric modulator
Small molecule
Approved
Unknown
ORAL
Multiple Sclerosis, Relapsing-Remitting; Multiple Sclerosis
Kelch-like ECH-associated protein 1 inhibitor
Small molecule
Approved
Unknown
Unknown
Alopecia; Acne Vulgaris
Androgen Receptor antagonist
Small molecule
Approved
Unknown
Unknown
Carcinoid Tumor; Colorectal Neoplasms; Endometrial Neoplasms; Leukemia; Sarcoma, Ewing; Stomach Neoplasms; Breast Neoplasms; Carcinoma, Non-Small-Cell Lung; Leiomyosarcoma; Mesothelioma; Sarcoma; Ovarian Neoplasms; Neoplasms; Small Cell Lung Carcinoma
DNA negative modulator
Small molecule
Approved
Unknown
Unknown
Leukemia, Myeloid, Acute; Lymphoma; Neoplasms; Carcinoma, Basal Cell; Prostatic Neoplasms, Castration-Resistant; Keratosis, Actinic
Tyrosine-protein kinase SRC inhibitor
Small molecule
Approved
Unknown
Unknown
Neoplasms; Prostatic Neoplasms, Castration-Resistant; Small Cell Lung Carcinoma; Lymphoma, Follicular; Sarcoma
Histone-lysine N-methyltransferase EZH2 inhibitor
Small molecule
Approved
Unknown
Unknown
Cocaine-Related Disorders; Spasms, Infantile; Lennox Gastaut Syndrome; Epilepsy; Obesity
Unknown
Small molecule
Approved
Unknown
Unknown
Attention Deficit Disorder with Hyperactivity
Dopamine transporter inhibitor
Small molecule
Approved
Unknown
Unknown
Breast Neoplasms; Gastrointestinal Stromal Tumors; Uterine Cervical Neoplasms; Achondroplasia; Carcinoma, Squamous Cell; Glioblastoma; Melanoma; Osteomalacia; Papillomavirus Infections; Paraganglioma; Squamous Cell Carcinoma of Head and Neck; Cholangiocarcinoma; Urinary Bladder Neoplasms; Neoplasms
Fibroblast growth factor receptor inhibitor
Small molecule
Approved
Unknown
Unknown
Neoplasms; Cholangiocarcinoma
Fibroblast growth factor receptor inhibitor
Small molecule
Approved
Unknown
Unknown
Small Cell Lung Carcinoma
Cyclin-dependent kinase 4 inhibitor
Small molecule
Approved
Unknown
Unknown
Bipolar Disorder; Schizophrenia
Delta opioid receptor partial agonist
Small molecule
Approved
Unknown
Unknown
Liver Diseases; Pancreatic Neoplasms; Lung Neoplasms; Ovarian Neoplasms; Colorectal Neoplasms; Carcinoma, Non-Small-Cell Lung; Neoplasms
GTPase KRas inhibitor
Small molecule
Approved
Unknown
Unknown
Biliary Atresia; Liver Diseases; Alagille Syndrome
Ileal bile acid transporter inhibitor
Small molecule
Approved
Unknown
Unknown
Coronary Disease; Cardiovascular Diseases; Heart Failure
Soluble guanylate cyclase activator
Small molecule
Approved
Unknown
Unknown
Carcinoma, Non-Small-Cell Lung
Epidermal growth factor receptor erbB1 inhibitor
Small molecule
Approved
Unknown
Unknown
Bronchiolitis Obliterans Syndrome; Psoriasis; Multiple Sclerosis; Multiple Sclerosis, Relapsing-Remitting
Sphingosine 1-phosphate receptor Edg-1 agonist
Small molecule
Approved
Unknown
Unknown
Kidney Diseases; Liver Diseases; Lung Neoplasms; Carcinoma, Non-Small-Cell Lung; Neoplasms
Epidermal growth factor receptor erbB1 inhibitor
Small molecule
Approved
Unknown
Unknown
Autoimmune Diseases; Graft vs Host Disease
Rho-associated protein kinase inhibitor
Small molecule
Approved
Unknown
Unknown
Invasive Fungal Infections; Candidiasis, Vulvovaginal
1,3-beta-glucan synthase inhibitor
Small molecule
Approved
Unknown
Unknown
Cholestasis; Liver Cirrhosis, Biliary; Non-alcoholic Fatty Liver Disease; Alagille Syndrome; Biliary Atresia; Cholestasis, Intrahepatic
Ileal bile acid transporter inhibitor