Display Options:
Total: 6532
Small molecule
Approved
Unknown
Unknown
Mycoses; Sepsis
Unknown
Small molecule
Approved
Unknown
Unknown
Neoplasms
PI3-kinase p110-delta subunit inhibitor
Small molecule
Approved
Unknown
Unknown
Cardiomyopathies; Kidney Diseases; Liver Diseases; Cardiomyopathy, Hypertrophic; Diabetes Mellitus; Diabetes Mellitus, Type 1; Diabetes Mellitus, Type 2; Heart Disease Risk Factors; Heart Failure; Renal Insufficiency, Chronic
Sodium/glucose cotransporter 1 inhibitor
Small molecule
Approved
Unknown
Unknown
Hemoglobinuria, Paroxysmal; Kidney Diseases; Liver Diseases; Glomerulonephritis; Glomerulonephritis, Membranous; Lupus Nephritis; Macular Degeneration; Atypical Hemolytic Uremic Syndrome; Glomerulonephritis, IGA; Glomerulonephritis, Membranoproliferative; Hemoglobinuria
Complement factor B inhibitor
Small molecule
Approved
Unknown
Unknown
Mood Disorders; Essential Tremor; Parkinson Disease; Depressive Disorder, Major; Depression, Postpartum; Depressive Disorder
GABA-A receptor; anion channel positive allosteric modulator
Small molecule
Approved
Unknown
Unknown
Hematologic Neoplasms; Hereditary Breast and Ovarian Cancer Syndrome; Uterine Cervical Neoplasms; Uterine Neoplasms; Adenocarcinoma; Carcinoma, Non-Small-Cell Lung; Carcinoma, Squamous Cell; Lymphoma, Follicular; Meningioma; Multiple Myeloma; Prostatic Neoplasms; Stomach Neoplasms; Triple Negative Breast Neoplasms; Prostatic Neoplasms, Castration-Resistant; Breast Neoplasms; Neoplasms
Serine/threonine-protein kinase AKT inhibitor
Small molecule
Approved
Unknown
Unknown
Kidney Diseases; Liver Diseases; Hot Flashes
Neurokinin 3 receptor antagonist
Small molecule
Approved
Unknown
Unknown
Cocaine-Related Disorders; Depressive Disorder
Serotonin 1a (5-HT1a) receptor agonist
Small molecule
Approved
Unknown
Unknown
Liver Diseases; Melanoma; Breast Neoplasms; Friedreich Ataxia
Nuclear factor erythroid 2-related factor 2 activator
Small molecule
Approved
Unknown
Unknown
Rosacea; Blepharitis; Eye Infections; Eye Infections, Parasitic
Ectoparasiticide
Small molecule
Approved
Unknown
Unknown
Hypertension; Glomerulosclerosis, Focal Segmental; Glomerulonephritis, IGA
Endothelin receptor ET-A antagonist
Small molecule
Approved
Unknown
Unknown
Essential Hypertension; Diabetes Mellitus; Diabetes Mellitus, Type 2
Sodium/glucose cotransporter 2 inhibitor
Small molecule
Approved
Unknown
Unknown
Renal Insufficiency; Leukemia; Lymphoma, B-Cell, Marginal Zone; Multiple Sclerosis; Waldenstrom Macroglobulinemia; Leukemia, Lymphocytic, Chronic, B-Cell; Lymphoma, Mantle-Cell; Neoplasms
Tyrosine-protein kinase BTK inhibitor
Small molecule
Approved
Unknown
Unknown
Wounds and Injuries; Peripheral Vascular Diseases; Anemia; Renal Insufficiency, Chronic
Hypoxia-inducible factor prolyl hydroxylase inhibitor
Small molecule
Approved
Unknown
Unknown
Dry Eye Syndromes; Ossification, Heterotopic; Myositis Ossificans
Retinoic acid receptor gamma agonist
Small molecule
Approved
Unknown
Unknown
Alopecia Areata; Dermatitis, Atopic; Eosinophilic Esophagitis; Inflammatory Bowel Diseases; Liver Cirrhosis, Biliary; Pyoderma; Colitis, Ulcerative; Crohn Disease
Sphingosine 1-phosphate receptor Edg-1 agonist
Small molecule
Approved
Unknown
Unknown
Colitis, Ulcerative; Muscular Dystrophy, Duchenne
Glucocorticoid receptor agonist
Small molecule
Approved
Unknown
Unknown
Asthma; Severe Acute Respiratory Syndrome; Migraine Disorders
Calcitonin-gene-related peptide receptor, CALCRL/RAMP1 antagonist
Small molecule
Approved
Unknown
Unknown
Carcinoma, Non-Small-Cell Lung; Leukemia, Myeloid; Polycythemia Vera; Thrombocythemia, Essential; Carcinoma, Pancreatic Ductal; Neoplasms; Primary Myelofibrosis
Tyrosine-protein kinase JAK1 inhibitor
Small molecule
Approved
Unknown
Unknown
Diagnostic Imaging
Diagnostic
Small molecule
Approved
Unknown
Unknown
Endometrial Neoplasms; Neoplasms; Breast Neoplasms
PI3-kinase p110-alpha subunit inhibitor
Small molecule
Approved
Unknown
Unknown
Gaucher Disease; Niemann-Pick Disease, Type C; Amyotrophic Lateral Sclerosis; Myositis, Inclusion Body
Unknown
Small molecule
Approved
Unknown
Unknown
Crohn Disease; Hodgkin Disease; Polycythemia Vera; Arthritis, Juvenile; Leukemia, Lymphocytic, Chronic, B-Cell; Multiple Myeloma; Myeloproliferative Disorders; Muscular Dystrophy, Duchenne
Unknown
Small molecule
Approved
Unknown
Unknown
Kidney Diseases; Liver Diseases; Geographic Atrophy; Glomerulonephritis, Membranoproliferative; Severe Acute Respiratory Syndrome; Hemoglobinuria; Hemoglobinuria, Paroxysmal; Hemolysis
Complement factor D inhibitor
Small molecule
Approved
Unknown
Unknown
Lung Neoplasms; Melanoma; Carcinoma, Non-Small-Cell Lung
ALK tyrosine kinase receptor inhibitor
Small molecule
Approved
Unknown
Unknown
Asthma; Cystic Fibrosis; Severe Acute Respiratory Syndrome; Pulmonary Disease, Chronic Obstructive
Phosphodiesterase 3 inhibitor
Small molecule
Approved
Unknown
Unknown
Liver Diseases; Carcinoma, Non-Small-Cell Lung; Neoplasms
CD74-ROS1 inhibitor
Small molecule
Approved
Unknown
Unknown
Liver Diseases; Cholangitis, Sclerosing; Hyperlipidemias; Hyperlipoproteinemia Type II; Non-alcoholic Fatty Liver Disease; Liver Cirrhosis, Biliary
Peroxisome proliferator-activated receptor delta agonist
Small molecule
Approved
Unknown
Unknown
Dyslipidemias; Hypercholesterolemia; Hyperlipoproteinemia Type II; Non-alcoholic Fatty Liver Disease
Thyroid hormone receptor beta-1 agonist
Small molecule
Approved
Unknown
Unknown
Liver Diseases; Anemia; Renal Insufficiency, Chronic
Egl nine homolog 1 inhibitor
Small molecule
Approved
Unknown
Unknown
Glioma; Liver Diseases; Neoplasms; Paraganglioma; Astrocytoma; Oligodendroglioma
IDH1/IDH2 inhibitor
Small molecule
Approved
Unknown
Unknown
Atrial Flutter; Heart Arrest; Tachycardia, Supraventricular; Arrhythmias, Cardiac; Atrial Fibrillation; Cardiovascular Diseases; Shock, Septic
Beta-1 adrenergic receptor antagonist
Small molecule
Approved
Unknown
Unknown
Kidney Diseases; Liver Diseases; Essential Hypertension; Hypertension
Endothelin receptor, ET-A/ET-B antagonist
Small molecule
Approved
Unknown
Unknown
Liver Diseases; Cholangitis, Sclerosing; Diabetes Mellitus, Type 2; Non-alcoholic Fatty Liver Disease; Liver Cirrhosis, Biliary; Cholangitis
Peroxisome proliferator-activated receptor alpha agonist
Small molecule
Approved
Unknown
Unknown
Unknown
Unknown