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Total: 10647
Small molecule
Approved
Unknown
Unknown
Diabetes Mellitus, Type 1; Cardiovascular Diseases
Unknown
Small molecule
Approved
Unknown
Unknown
Diabetic Nephropathies; Heart Diseases; Hypertension; Cardiovascular Diseases
Unknown
Enzyme
Approved
OTHER
INJECTION
Unknown
Glucocerebroside hydrolytic enzyme
Small molecule
Approved
Unknown
Unknown
Glioblastoma; Hepatitis C; Leukemia, Myeloid, Acute; Myelodysplastic Syndromes; Obesity; Alcoholism; Brain Injuries; Child Development Disorders, Pervasive; Cocaine-Related Disorders; Coccidioidomycosis; Depression, Postpartum; Fragile X Syndrome; Mood Disorders; Panic Disorder; Pruritus; Substance-Related Disorders; Anxiety; Anxiety Disorders; Autistic Disorder; Bipolar Disorder; Dementia; Meningitis, Cryptococcal; Obsessive-Compulsive Disorder; Phobia, Social; Schizophrenia; Sleep Initiation and Maintenance Disorders; Stress Disorders, Post-Traumatic; Depressive Disorder; Depressive Disorder, Major
Unknown
Small molecule
Approved
OTHER
ORAL
Atherosclerosis; Coronary Disease; Diabetes Mellitus, Type 2; Hypercholesterolemia; Cardiovascular Diseases; Diabetes Mellitus; Hypertension
Mineralocorticoid receptor antagonist
Small molecule
Approved
IMMUNE SYSTEM; OTHER; RESPIRATORY
ORAL
Anovulation; Depressive Disorder, Major; HIV Infections; Neoplasm Metastasis; Neoplasms; Osteomyelitis; Parkinson Disease; Prostatic Neoplasms, Castration-Resistant; Venous Thromboembolism; Buruli Ulcer; Carcinoma, Non-Small-Cell Lung; Carcinoma, Squamous Cell; Cystic Fibrosis; Disorders of Excessive Somnolence; Idiopathic Hypersomnia; Leukemia, Lymphocytic, Chronic, B-Cell; Lung Diseases; Lymphoma; Lymphoma, B-Cell, Marginal Zone; Narcolepsy; Periodontitis; Pseudomyxoma Peritonei; Toxoplasmosis, Cerebral; Asthma; Bronchiolitis Obliterans; Bronchopulmonary Dysplasia; Crohn Disease; Gastritis; Heart Diseases; Helicobacter Infections; Hemorrhage; Lymphoma, Non-Hodgkin; Multiple Myeloma; Mycobacterium avium-intracellulare Infection; Pneumonia, Bacterial; Sepsis; Shock, Septic; Stomach Neoplasms; Stomach Ulcer; Tuberculosis; Bacterial Infections; Bronchitis, Chronic; Duodenal Ulcer; Infections; Maxillary Sinusitis; Otitis Media; Pharyngitis; Pneumonia; Sinusitis; Tonsillitis
Bacterial 70S ribosome inhibitor
Small molecule
Approved
IMMUNE SYSTEM; OTHER
ORAL
AIDS Dementia Complex; Lymphoma; Acquired Immunodeficiency Syndrome; AIDS-Related Complex; Tuberculosis; HIV Infections; Virus Diseases
Human immunodeficiency virus type 1 reverse transcriptase inhibitor
Unknown
Approved
Unknown
Unknown
Bursitis; Dry Eye Syndromes; Dysphonia; Gingival Overgrowth; Keloid; Osteoarthritis, Knee; Pruritus; Psoriasis; Restless Legs Syndrome; Rhinitis, Atrophic; Skin Diseases; Tachycardia, Ventricular; Urinary Incontinence, Stress; Vocal Cord Paralysis; Wounds and Injuries; Acne Vulgaris; Alopecia; Arrhythmias, Cardiac; Atrial Fibrillation; Atrial Flutter; Brain Injuries; Burning Mouth Syndrome; Carpal Tunnel Syndrome; Chronic Pain; Compartment Syndromes; Cystitis, Interstitial; Dementia; Depressive Disorder; Depressive Disorder, Major; Epidermolysis Bullosa Simplex; Erectile Dysfunction; Esophageal Neoplasms; Essential Tremor; Facial Pain; Fasciitis, Plantar; Fissure in Ano; Granuloma; Graves Ophthalmopathy; Headache Disorders; Hernia, Ventral; Joint Diseases; Lacrimal Apparatus Diseases; Leiomyoma; Muscular Diseases; Nasal Polyps; Neuralgia, Postherpetic; Neuroma; Obesity; Obesity, Morbid; Osteoarthritis; Pancreatic Neoplasms; Parkinson Disease; Penile Induration; Premature Ejaculation; Prostatic Hyperplasia; Pulmonary Disease, Chronic Obstructive; Rectal Neoplasms; Rhinitis; Rotator Cuff Injuries; Scoliosis; Sialorrhea; Sleep Apnea Syndromes; Spinal Cord Injuries; Stomach Neoplasms; Temporomandibular Joint Disorders; Tendinopathy; Thoracic Outlet Syndrome; Ulcer; Urinary Retention; Aging; Blepharospasm; Bruxism; Cerebral Palsy; Cicatrix; Contracture; Esotropia; Fecal Incontinence; Gastroparesis; Headache; Hemiplegia; Hyperhidrosis; Low Back Pain; Migraine Disorders; Multiple Sclerosis; Muscle Cramp; Muscle Spasticity; Myofascial Pain Syndromes; Nervous System Diseases; Neuralgia; Pain; Patellofemoral Pain Syndrome; Prostatitis; Raynaud Disease; Reflex, Abnormal; Scleroderma, Localized; Shoulder Pain; Skin Aging; Sprains and Strains; Strabismus; Stroke; Tennis Elbow; Tension-Type Headache; Torticollis; Tremor; Trigeminal Neuralgia; Urinary Bladder, Neurogenic; Urinary Bladder, Overactive; Urinary Incontinence; Urinary Incontinence, Urge
Synaptosomal nerve-associated protein 25 (SNAP-25) inhibitor
Small molecule
Approved
OTHER
ORAL
Hepatolenticular Degeneration; Leukemia, Myelogenous, Chronic, BCR-ABL Positive; Leukemia, Myeloid, Acute; Myelodysplastic Syndromes; Asperger Syndrome; Autistic Disorder
Lead chelating agent
Unknown
Approved
Unknown
Unknown
Respiratory Distress Syndrome; Respiratory Distress Syndrome, Newborn
Surfactant agent
Small molecule
Approved
Unknown
Unknown
Atrial Fibrillation; Heart Failure; Arrhythmias, Cardiac
Beta-1 adrenergic receptor antagonist
Small molecule
Approved
Unknown
Unknown
Bacterial Infections
Unknown
Small molecule
Approved
Unknown
Unknown
Sleep Apnea, Central; Amenorrhea; Hemorrhage; Infertility; Polycystic Ovary Syndrome
Progesterone receptor agonist
Small molecule
Approved
OTHER
INHALATION
Postoperative Complications; Renal Insufficiency
GABA-A receptor; anion channel positive allosteric modulator
Small molecule
Approved
Unknown
Unknown
Dystonic Disorders; Low Back Pain; Marijuana Abuse; Obesity; Prostatic Neoplasms; Autistic Disorder; Parkinson Disease; Substance-Related Disorders; Anxiety; Attention Deficit Disorder with Hyperactivity; Dementia; Depressive Disorder; Schizophrenia; Sleep Initiation and Maintenance Disorders; Sleep Wake Disorders
Unknown
Small molecule
Approved
Unknown
Unknown
Melanosis; Skin Neoplasms; Sunburn
Unknown
Small molecule
Approved
Unknown
Unknown
Unknown
Diagnostic agent
Small molecule
Approved
Unknown
Unknown
Obesity; Pain; Migraine with Aura; Migraine without Aura; Migraine Disorders
Serotonin 1b (5-HT1b) receptor agonist
Small molecule
Approved
Unknown
Unknown
Unknown
Unknown
Unknown
Approved
Unknown
Unknown
Unknown
Unknown
Small molecule
Approved
Unknown
Unknown
Unknown
Unknown
Small molecule
Approved
Unknown
Unknown
Unknown
Unknown
Small molecule
Approved
Unknown
Unknown
Acute Coronary Syndrome; Oligodendroglioma; Renal Insufficiency, Chronic; Rhabdomyosarcoma; Calcinosis; Dermatomyositis; Glioma; Head and Neck Neoplasms; Hearing Loss; Mesothelioma; Myositis; Severe Acute Respiratory Syndrome; Hepatoblastoma; Medulloblastoma; Ototoxicity
Unknown
Protein
Approved
CANCER
UNKNOWN
Abortion, Habitual; Acquired Immunodeficiency Syndrome; Adenocarcinoma of Lung; Alopecia Areata; Anemia, Hemolytic, Autoimmune; Blast Crisis; Brain Neoplasms; Carcinoma, Hepatocellular; Carcinoma, Merkel Cell; Carcinoma, Non-Small-Cell Lung; Carcinoma, Squamous Cell; Colorectal Neoplasms; Cryoglobulinemia; Cytomegalovirus Infections; Encephalitis; Glioblastoma; Glioma; Gliosarcoma; Hematologic Neoplasms; Leukemia, Biphenotypic, Acute; Lymphoma, T-Cell, Cutaneous; Macrophage Activation Syndrome; Mesothelioma; Mycosis Fungoides; Myelodysplastic-Myeloproliferative Diseases; Myocardial Ischemia; Neoplasm Metastasis; Pancreatic Neoplasms; Papillomavirus Infections; Precursor Cell Lymphoblastic Leukemia-Lymphoma; Sarcoma; Sarcoma, Synovial; Sezary Syndrome; Squamous Intraepithelial Lesions; Thyroid Neoplasms; Uterine Cervical Neoplasms; Wiskott-Aldrich Syndrome; Alzheimer Disease; Amyotrophic Lateral Sclerosis; Behcet Syndrome; Breast Neoplasms, Male; Bronchiolitis Obliterans Syndrome; Carcinoma; Central Nervous System Neoplasms; Conjunctivitis, Allergic; Crohn Disease; Diabetes Mellitus, Type 1; Fallopian Tube Neoplasms; Graft vs Host Disease; Hodgkin Disease; Inflammatory Breast Neoplasms; Leukemia, Lymphocytic, Chronic, B-Cell; Leukemia, Myelogenous, Chronic, BCR-ABL Positive; Liver Neoplasms; Lung Neoplasms; Lymphoma, Non-Hodgkin; Multiple Myeloma; Myeloproliferative Disorders; Myositis; Nephrotic Syndrome; Ovarian Neoplasms; Peritoneal Neoplasms; Polychondritis, Relapsing; Polymyalgia Rheumatica; Prostatic Neoplasms, Castration-Resistant; Urinary Bladder Neoplasms; Uveal Melanoma; Anemia, Refractory; Anemia, Refractory, with Excess of Blasts; Breast Neoplasms; Burkitt Lymphoma; Carcinoma, Renal Cell; Dermatomyositis; Head and Neck Neoplasms; HIV Infections; Kidney Neoplasms; Leukemia; Leukemia, Basophilic, Acute; Leukemia, Erythroblastic, Acute; Leukemia, Megakaryoblastic, Acute; Leukemia, Monocytic, Acute; Leukemia, Myeloid, Acute; Leukemia, Myelomonocytic, Acute; Leukemia, Myelomonocytic, Chronic; Lupus Erythematosus, Systemic; Lymphoma; Lymphoma, Follicular; Lymphoma, Large B-Cell, Diffuse; Myelodysplastic Syndromes; Neuroblastoma; Severe Acute Respiratory Syndrome; Skin Neoplasms; Melanoma; Neoplasms
Interleukin-2 receptor agonist
Small molecule
Approved
CANCER; OTHER; RESPIRATORY
INJECTION; IV (INFUSION)
Anus Neoplasms; Brain Neoplasms; Carcinoid Tumor; Carcinoma, Intraductal, Noninfiltrating; Carcinoma, Renal Cell; Carcinoma, Small Cell; Carcinoma, Verrucous; Coronary Restenosis; Glioblastoma; Gliosarcoma; Hodgkin Disease; Leukemia, Lymphocytic, Chronic, B-Cell; Liver Neoplasms; Mesothelioma; Neoplasms, Cystic, Mucinous, and Serous; Rectal Neoplasms; Thyroid Carcinoma, Anaplastic; Vaginal Neoplasms; Adenocarcinoma, Bronchiolo-Alveolar; Adrenal Cortex Neoplasms; Arthritis, Rheumatoid; Bone Neoplasms; Breast Carcinoma In Situ; Carcinoma, Ductal; Carcinoma, Endometrioid; Carcinoma, Hepatocellular; Carcinoma, Merkel Cell; Carcinoma, Neuroendocrine; Carcinoma, Ovarian Epithelial; Central Nervous System Neoplasms; Cholangiocarcinoma; Colorectal Neoplasms; Constriction, Pathologic; Cystadenoma, Serous; Digestive System Diseases; Gallbladder Neoplasms; Gastrointestinal Stromal Tumors; Glioma; Hemangiosarcoma; Hereditary Breast and Ovarian Cancer Syndrome; Hypopharyngeal Neoplasms; Keratosis, Actinic; Kidney Neoplasms; Leukemia; Lymphoma; Mouth Neoplasms; Multiple Myeloma; Neoplasms, Complex and Mixed; Neoplasms, Germ Cell and Embryonal; Oropharyngeal Neoplasms; Penile Neoplasms; Peripheral Vascular Diseases; Prostatic Hyperplasia; Prostatic Neoplasms; Psoriasis; Salivary Gland Neoplasms; Small Cell Lung Carcinoma; Thymoma; Uterine Cervical Dysplasia; Uveal Melanoma; Vulvar Neoplasms; Adenocarcinoma; Adenocarcinoma of Lung; Anemia; Biliary Tract Neoplasms; Breast Neoplasms, Male; Carcinoma, Large Cell; Carcinoma, Pancreatic Ductal; Carcinoma, Squamous Cell; Endometrial Neoplasms; Esophageal Neoplasms; Fallopian Tube Neoplasms; Genital Neoplasms, Female; Gestational Trophoblastic Disease; Head and Neck Neoplasms; HIV Infections; Hypersensitivity; Inflammatory Breast Neoplasms; Ischemia; Lung Neoplasms; Lymphoma, Non-Hodgkin; Melanoma; Nasopharyngeal Carcinoma; Nasopharyngeal Neoplasms; Neoplasm Metastasis; Pain; Paraganglioma; Peripheral Arterial Disease; Peripheral Nervous System Diseases; Peritoneal Neoplasms; Prostatic Neoplasms, Castration-Resistant; Retroviridae Infections; Sarcoma; Sex Cord-Gonadal Stromal Tumors; Squamous Cell Carcinoma of Head and Neck; Stomach Neoplasms; Teratoma; Testicular Neoplasms; Thyroid Neoplasms; Triple Negative Breast Neoplasms; Urethral Neoplasms; Urinary Bladder Neoplasms; Urogenital Neoplasms; Uterine Cervical Neoplasms; Uterine Neoplasms; Breast Neoplasms; Carcinoma; Carcinoma, Non-Small-Cell Lung; Neoplasms; Ovarian Neoplasms; Pancreatic Neoplasms; Sarcoma, Kaposi
Tubulin inhibitor
Small molecule
Approved
OTHER
INJECTION
Leukemia; Lymphoma; Precursor Cell Lymphoblastic Leukemia-Lymphoma; Neoplasms
DNA topoisomerase II inhibitor
Small molecule
Approved
OTHER
ORAL
Carcinoma, Non-Small-Cell Lung; Gastroesophageal Reflux; Leukemia, Myeloid, Acute; Infections; Severe Acute Respiratory Syndrome; Toxoplasmosis, Cerebral; Malaria, Falciparum; Amebiasis; Malaria; Pneumocystis Infections; Pneumonia, Pneumocystis
Cytochrome b inhibitor
Small molecule
Approved
OTHER
INJECTION
Astrocytoma; Glioblastoma; Glioma; Multiple Sclerosis, Chronic Progressive; Paraganglioma; Central Nervous System Diseases
Diagnostic agent
Small molecule
Approved
Unknown
Unknown
Unknown
Bacterial DNA gyrase inhibitor
Small molecule
Approved
OTHER
TOPICAL
Prostatic Neoplasms, Castration-Resistant; Neoplasms
Insulin-like growth factor I receptor inhibitor
Small molecule
Approved
OTHER
ORAL
Osteomyelitis; Otitis Media
Bacterial penicillin-binding protein inhibitor
Small molecule
Approved
Unknown
Unknown
Melanosis; Skin Neoplasms; Sunburn
Unknown
Small molecule
Approved
Unknown
Unknown
Breast Neoplasms; Erectile Dysfunction; HIV Infections; Hyperlipidemias; Kidney Diseases; Neoplasms; Pancreatitis; Aortic Aneurysm, Abdominal; Aortic Valve Insufficiency; beta-Thalassemia; Cardiomyopathy, Hypertrophic; Dystonic Disorders; Heart Diseases; Hyperaldosteronism; Liver Diseases; Raynaud Disease; Thalassemia; Vascular Diseases; Atherosclerosis; Coronary Disease; Depressive Disorder; Diabetes Mellitus; Diabetes Mellitus, Type 2; Essential Hypertension; Heart Failure; Hypercholesterolemia; Hypertension; Myocardial Infarction; Myocardial Ischemia; Cardiovascular Diseases
Unknown
Small molecule
Approved
Unknown
Unknown
Lecithin Cholesterol Acyltransferase Deficiency; Essential Hypertension; Proteinuria; Angina Pectoris; Angina Pectoris, Variant; Angina, Stable; Coronary Artery Disease; Diabetes Mellitus; Heart Failure; Hypercholesterolemia; Hyperlipidemias; Hyperlipoproteinemia Type II; Hypertension; Myocardial Infarction; Osteoarthritis; Stroke
Voltage-gated L-type calcium channel blocker
Small molecule
Approved
IMMUNE SYSTEM; OTHER
TOPICAL
Hepatitis B, Chronic; Mycoses; Colitis, Ulcerative; Crohn Disease; Tinea Pedis; Onychomycosis; Tinea
Squalene monooxygenase inhibitor