Display Options:
Total: 10647
Small molecule
Approved
Unknown
ORAL
Lupus Erythematosus, Systemic; Alopecia Areata; Arthritis, Juvenile; Arthritis, Psoriatic; Arthritis, Rheumatoid; Colitis, Ulcerative; Crohn Disease; Dermatitis, Atopic; Giant Cell Arteritis; Hidradenitis Suppurativa; Spondylitis, Ankylosing; Takayasu Arteritis; Vitiligo
Unknown
Small molecule
Approved
Unknown
Unknown
Alzheimer Disease; Bipolar Disorder; Depressive Disorder, Major; Schizophrenia; Psychotic Disorders
Dopamine D2 receptor antagonist
Small molecule
Approved
Unknown
Unknown
Kidney Diseases; Substance-Related Disorders; Alcoholism; Child Development Disorders, Pervasive; Prader-Willi Syndrome; Schizophrenia; Idiopathic Hypersomnia; Narcolepsy; Parkinson Disease
Histamine H3 receptor inverse agonist
Small molecule
Approved
Unknown
Unknown
Unknown
Unknown
Small molecule
Approved
Unknown
Unknown
Unknown
Unknown
Antibody
Approved
Unknown
Unknown
Choroidal Neovascularization; Macular Degeneration; Macular Edema; Retinal Vein Occlusion; Retinal Neovascularization; Wet Macular Degeneration
Vascular endothelial growth factor A inhibitor
Small molecule
Approved
Unknown
ORAL
Tuberculosis; Tuberculosis, Multidrug-Resistant; Tuberculosis, Pulmonary
Unknown
Small molecule
Approved
Unknown
Unknown
Kidney Diseases; Liver Diseases; Leukemia, Neutrophilic, Chronic; Myelodysplastic Syndromes; Myeloproliferative Disorders; Primary Myelofibrosis; Neoplasms
Tyrosine-protein kinase JAK2 inhibitor
Protein
Approved
Unknown
SUBCUTANEOUS
Acne Vulgaris; Ischemic Stroke; Porphyria, Variegate; Urticaria; Vitiligo; Xeroderma Pigmentosum; Protoporphyria, Erythropoietic
Melanocortin receptor 1 agonist
Combination
Approved
Unknown
Unknown
Unknown
Unknown
Small molecule
Approved
Unknown
ORAL
Amyloid Neuropathies, Familial; Polyneuropathies; Amyloidosis; Amyloidosis, Familial; Cardiomyopathies
Transthyretin stabiliser
Small molecule
Approved
Unknown
Unknown
Arthritis, Rheumatoid; Gastrointestinal Stromal Tumors; Leukemia, Myeloid, Acute; Liver Diseases; Neurilemmoma; Prostatic Neoplasms; Breast Neoplasms; Glioblastoma; Hemangiosarcoma; Hodgkin Disease; Melanoma; Prostatic Neoplasms, Castration-Resistant; Synovitis, Pigmented Villonodular; Neoplasms
Macrophage colony stimulating factor receptor inhibitor
Small molecule
Approved
Unknown
Unknown
Leukemia; Anemia, Hemolytic, Autoimmune; Castleman Disease; Immunoglobulin G4-Related Disease; Kidney Diseases; Leukemia, Lymphoid; Lupus Nephritis; Lymphoma; Lymphoma, B-Cell, Marginal Zone; Neuromyelitis Optica; Paraproteinemias; Purpura, Thrombocytopenic, Idiopathic; Severe Acute Respiratory Syndrome; Leukemia, Lymphocytic, Chronic, B-Cell; Lymphohistiocytosis, Hemophagocytic; Lymphoma, Follicular; Lymphoma, Large B-Cell, Diffuse; Lymphoma, Non-Hodgkin; Lymphoma, Mantle-Cell; Neoplasms; Waldenstrom Macroglobulinemia
Tyrosine-protein kinase BTK inhibitor
Small molecule
Approved
Unknown
ORAL
Amyloidosis; Amyloidosis, Familial; Carcinoma, Hepatocellular; Carcinoma, Non-Small-Cell Lung; Colorectal Neoplasms; Diabetic Foot; Fallopian Tube Neoplasms; Gliosarcoma; Hematologic Neoplasms; Leukemia; Leukemia, Biphenotypic, Acute; Leukemia, Myelogenous, Chronic, BCR-ABL Positive; Precursor Cell Lymphoblastic Leukemia-Lymphoma; Rectal Neoplasms; Sarcoma; Triple Negative Breast Neoplasms; Urinary Bladder Neoplasms; Breast Neoplasms; Carcinoma, Squamous Cell; Glioblastoma; Liposarcoma; Lymphoma; Lymphoma, Follicular; Lymphoma, T-Cell, Peripheral; Melanoma; Myelodysplastic Syndromes; Ovarian Neoplasms; Paraganglioma; Prostatic Neoplasms, Castration-Resistant; Severe Acute Respiratory Syndrome; Small Cell Lung Carcinoma; Thymoma; Thymus Neoplasms; Endometrial Neoplasms; Leukemia, Myeloid, Acute; Primary Myelofibrosis; Lymphoma, Large B-Cell, Diffuse; Multiple Myeloma; Neoplasms
Exportin-1 inhibitor
Unknown
Approved
Unknown
Unknown
Migraine Disorders; Torticollis; Skin Aging
Synaptosomal nerve-associated protein 25 (SNAP-25) proteolytic enzyme
Oligonucleotide
Approved
Unknown
Unknown
Muscular Dystrophies; Muscular Dystrophy, Duchenne
Dystrophin pre-mRNA positive modulator
Small molecule
Approved
Unknown
Unknown
Delirium; Kidney Diseases; Liver Diseases; Rhinitis, Allergic, Seasonal; Substance-Related Disorders; Cancer Pain; Depressive Disorder, Treatment-Resistant; Pain; Shock, Septic; Depressive Disorder
Glutamate [NMDA] receptor negative allosteric modulator
Small molecule
Approved
Unknown
ORAL
Anemia; Anemia, Iron-Deficiency
Supplement
Small molecule
Approved
Unknown
Unknown
Unknown
Membrane staining aid in ophthalmic surgery
Small molecule
Approved
Unknown
Unknown
Kidney Diseases; Liver Diseases; Dermatomyositis; Multiple Sclerosis, Relapsing-Remitting; Polymyositis; Multiple Sclerosis, Chronic Progressive; Multiple Sclerosis
Sphingosine 1-phosphate receptor Edg-1 agonist
Small molecule
Approved
Unknown
Unknown
Kidney Diseases; Liver Diseases; Acute Lung Injury; Idiopathic Pulmonary Fibrosis; Anemia; Anemia, Hemolytic; Anemia, Sickle Cell
Hemoglobin HbA positive modulator
Small molecule
Approved
Unknown
ORAL
Amyotrophic Lateral Sclerosis; Liver Diseases; Substance-Related Disorders; Parkinson Disease
Adenosine A2a receptor antagonist
Small molecule
Approved
Unknown
Unknown
Migraine Disorders
Calcitonin gene-related peptide type 1 receptor antagonist
Small molecule
Approved
Unknown
Unknown
Unknown
GABA-B receptor agonist
Small molecule
Approved
Unknown
Unknown
Migraine Disorders
Calcitonin gene-related peptide type 1 receptor antagonist
Small molecule
Approved
Unknown
Unknown
Breast Neoplasms; Carcinoma, Lobular; Uterine Neoplasms
Unknown
Antibody
Approved
Unknown
Unknown
Diabetic Neuropathies; Pain; Migraine Disorders
Calcitonin gene-related peptide inhibitor
Small molecule
Approved
Unknown
Unknown
Autoimmune Diseases; HIV Infections
Envelope polyprotein GP160 inhibitor
Small molecule
Approved
Unknown
Unknown
Migraine Disorders
Serotonin 1f (5-HT1f) receptor agonist
Antibody
Approved
Unknown
Unknown
Neoplasms; Scleroderma, Diffuse; Breast Neoplasms; Carcinoma, Non-Small-Cell Lung; Sarcoma; Graves Ophthalmopathy
Insulin-like growth factor I receptor antagonist
Combination
Approved
Unknown
Unknown
Unknown
Unknown
Antibody
Approved
Unknown
Unknown
Hematologic Neoplasms; Leukemia, Lymphocytic, Chronic, B-Cell; Leukemia, Prolymphocytic; Lymphoma, B-Cell, Marginal Zone; Lymphoma, Mantle-Cell; Lymphoma, Non-Hodgkin; Precursor Cell Lymphoblastic Leukemia-Lymphoma; Lymphoma, Follicular; Lymphoma; Lymphoma, Large B-Cell, Diffuse; Neoplasms
B-lymphocyte antigen CD19 binding agent
Small molecule
Approved
Unknown
Unknown
Astrocytoma; Central Nervous System Neoplasms; Colorectal Neoplasms; Glioblastoma; Gliosarcoma; Head and Neck Neoplasms; Lymphoma; Breast Neoplasms; Leukemia, Myelogenous, Chronic, BCR-ABL Positive; Liver Neoplasms; Ovarian Neoplasms; Urethral Neoplasms; Urinary Bladder Neoplasms; Carcinoma, Non-Small-Cell Lung; Hepatitis D; Leukemia, Myelomonocytic, Chronic; Myelodysplastic Syndromes; Neoplasm Metastasis; Laminopathies; Progeria
Protein farnesyltransferase inhibitor
Small molecule
Approved
Unknown
Unknown
Constipation
Osmotic agent
Small molecule
Approved
Unknown
Unknown
Carcinoma, Non-Small-Cell Lung
Hepatocyte growth factor receptor inhibitor