Display Options:
Total: 10647
Combination
Approved
Unknown
Unknown
Unknown
Unknown
Small molecule
Approved
Unknown
Unknown
Liver Diseases; Renal Insufficiency; Adenocarcinoma, Follicular; Carcinoma, Medullary; Carcinoma, Non-Small-Cell Lung; Neoplasms; Thyroid Neoplasms
Coiled-coil domain-containing protein 6/Tyrosine-protein kinase receptor RET inhibitor
Small molecule
Approved
Unknown
Unknown
Neuroblastoma; Trypanosomiasis, African; Chagas Disease; Leishmaniasis; Trypanosomiasis
DNA inhibitor
Small molecule
Approved
Unknown
Unknown
Angioedema; Angioedemas, Hereditary
Unknown
Small molecule
approved
Unknown
Unknown
Cytomegalovirus Infections; Virus Diseases
Phosphotransferase pUL97 inhibitor
Small molecule
Approved
Unknown
Unknown
Invasive Fungal Infections; Mycoses; Aspergillosis; Aspergillosis, Allergic Bronchopulmonary; Blastomycosis; Candidemia; Candidiasis, Invasive; Candidiasis, Vulvovaginal; Coccidioidomycosis; Histoplasmosis; Vulvovaginitis
1,3-beta-glucan synthase inhibitor
Combination
Approved
Unknown
Unknown
Unknown
Unknown
Combination
Approved
Unknown
Unknown
Unknown
Unknown
Small molecule
Approved
Unknown
Unknown
Attention Deficit Disorder with Hyperactivity
Norepinephrine transporter inhibitor
Small molecule
Approved
Unknown
Unknown
Metal Metabolism, Inborn Errors
Unknown
Combination
Approved
Unknown
Unknown
Unknown
Unknown
Small molecule
Approved
Unknown
Unknown
Coronary Disease; Cardiovascular Diseases; Heart Failure
Soluble guanylate cyclase activator
Small molecule
Approved
Unknown
Unknown
Bronchiolitis Obliterans Syndrome; Psoriasis; Multiple Sclerosis; Multiple Sclerosis, Relapsing-Remitting
Sphingosine 1-phosphate receptor Edg-1 agonist
Small molecule
Approved
Unknown
Unknown
Autoimmune Diseases; Graft vs Host Disease
Rho-associated protein kinase inhibitor
Small molecule
Approved
Unknown
Unknown
Kidney Diseases; Liver Diseases; Lung Neoplasms; Carcinoma, Non-Small-Cell Lung; Neoplasms
Epidermal growth factor receptor erbB1 inhibitor
Small molecule
Approved
Unknown
Unknown
Cholestasis; Liver Cirrhosis, Biliary; Non-alcoholic Fatty Liver Disease; Alagille Syndrome; Biliary Atresia; Cholestasis, Intrahepatic
Ileal bile acid transporter inhibitor
Small molecule
Approved
Unknown
Unknown
Migraine Disorders
Calcitonin gene-related peptide type 1 receptor antagonist
Combination
Approved
Unknown
Unknown
Unknown
Unknown
Combination
Approved
Unknown
Unknown
Unknown
Unknown
Small molecule
Approved
Unknown
Unknown
Liver Diseases; Renal Insufficiency, Chronic; Carcinoma, Renal Cell; Hemangioblastoma; Neoplasms; Neuroendocrine Tumors; von Hippel-Lindau Disease
Endothelial PAS domain-containing protein 1 inhibitor
Combination
Approved
Unknown
Unknown
Unknown
Unknown
Combination
Approved
Unknown
Unknown
Unknown
Unknown
Unknown
Approved
Unknown
Unknown
Diabetes Mellitus; Diabetes Mellitus, Type 1; Hypoglycemia
Glucagon receptor agonist
Small molecule
Approved
Unknown
Unknown
Neoplasms; Cholangiocarcinoma
Fibroblast growth factor receptor inhibitor
Protein
Investigational
Unknown
Unknown
Mucopolysaccharidosis IV; Dwarfism; Achondroplasia; Bone Diseases
Atrial natriuretic peptide receptor B binding agent
Protein
Approved
Unknown
Unknown
Macular Degeneration; Amyotrophic Lateral Sclerosis; Glomerulonephritis, Membranoproliferative; Thrombotic Microangiopathies; Anemia, Hemolytic, Autoimmune; Geographic Atrophy; Hemoglobinuria; Eye Diseases; Hemoglobinuria, Paroxysmal
Complement C3 inhibitor
Small molecule
Approved
Unknown
Unknown
Hodgkin Disease; Leukemia, Lymphocytic, Chronic, B-Cell; Lymphoma, Follicular; Lymphoma, Large B-Cell, Diffuse; Lymphoma, Mantle-Cell; Lymphoma, Non-Hodgkin; Waldenstrom Macroglobulinemia; Neoplasms
Unknown
Combination
Approved
Unknown
Unknown
Unknown
Unknown
Small molecule
Approved
Unknown
Unknown
Depressive Disorder
Unknown
Small molecule
Approved
Unknown
Unknown
Neoplasms; Breast Neoplasms; Carcinoma, Hepatocellular; Diagnostic Imaging; Genital Neoplasms, Female; Positron-Emission Tomography; Prostatic Neoplasms
Diagnostic agent
Unknown
Approved
Unknown
Unknown
Atherosclerosis; Dyslipidemias; Hypercholesterolemia; Hyperlipoproteinemia Type II
PCSK9 mRNA rnai inhibitor
Oligonucleotide
Approved
Unknown
Unknown
Muscular Dystrophies; Muscular Dystrophy, Duchenne
Dystrophin pre-mRNA positive modulator
Unknown
Approved
Unknown
Unknown
Leukemia, Myelogenous, Chronic, BCR-ABL Positive
Bcr/Abl fusion protein inhibitor
Small molecule
Approved
Unknown
Unknown
Idiopathic Hypersomnia
Dopamine transporter inhibitor
Small molecule
Approved
Unknown
Unknown
Metal Metabolism, Inborn Errors
Unknown