Display Options:
Total: 10647
Small molecule
Approved
Unknown
Unknown
Astrocytoma; Central Nervous System Neoplasms; Colorectal Neoplasms; Glioblastoma; Gliosarcoma; Head and Neck Neoplasms; Lymphoma; Breast Neoplasms; Leukemia, Myelogenous, Chronic, BCR-ABL Positive; Liver Neoplasms; Ovarian Neoplasms; Urethral Neoplasms; Urinary Bladder Neoplasms; Carcinoma, Non-Small-Cell Lung; Hepatitis D; Leukemia, Myelomonocytic, Chronic; Myelodysplastic Syndromes; Neoplasm Metastasis; Laminopathies; Progeria
Protein farnesyltransferase inhibitor
Small molecule
Approved
Unknown
Unknown
Constipation
Osmotic agent
Small molecule
Approved
Unknown
Unknown
Migraine Disorders
Serotonin 1f (5-HT1f) receptor agonist
Small molecule
Approved
Unknown
Unknown
Carcinoma, Non-Small-Cell Lung
Hepatocyte growth factor receptor inhibitor
Unknown
Approved
Unknown
Unknown
Unknown
Unknown
Small molecule
Approved
Unknown
Unknown
Anesthesia; Pain; Conscious Sedation
GABA-A receptor; anion channel positive allosteric modulator
Small molecule
Approved
Unknown
Unknown
Kidney Diseases; Liver Diseases; Sleep Apnea, Obstructive; Alzheimer Disease; Sleep Disorders, Circadian Rhythm; Alcoholism; Epilepsy; Sleep Wake Disorders; Sleep Initiation and Maintenance Disorders
Orexin receptor 1 antagonist
Small molecule
Approved
Unknown
Unknown
Astrocytoma; Colonic Neoplasms; Glioma; Heart Failure; Leukemia, Myelogenous, Chronic, BCR-ABL Positive; Optic Nerve Glioma; Precursor Cell Lymphoblastic Leukemia-Lymphoma; Rectal Neoplasms; Sarcoma, Kaposi; Urinary Bladder Neoplasms; Adenocarcinoma; Adenocarcinoma, Follicular; Bile Duct Neoplasms; Biliary Tract Neoplasms; Breast Neoplasms; Carcinoma, Squamous Cell; Cholangiocarcinoma; Colorectal Neoplasms; Gallbladder Neoplasms; Liver Neoplasms; Lung Neoplasms; Lymphoma, Large B-Cell, Diffuse; Melanoma; Multiple Myeloma; Neurilemmoma; Neurofibroma, Plexiform; Neurofibromatosis 1; Pancreatic Neoplasms; Sarcoma; Stomach Neoplasms; Triple Negative Breast Neoplasms; Uterine Neoplasms; Carcinoma, Non-Small-Cell Lung; Thyroid Neoplasms; Uveal Melanoma; Neoplasms
Unknown
Small molecule
Approved
Unknown
Unknown
Leukemia, Myeloid, Acute; Lymphoma; Neoplasms; Carcinoma, Basal Cell; Prostatic Neoplasms, Castration-Resistant; Keratosis, Actinic
Tyrosine-protein kinase SRC inhibitor
Antibody
Approved
Unknown
Unknown
Anemia, Hemolytic, Autoimmune; Colorectal Neoplasms; Hematologic Neoplasms; Immune System Diseases; Lymphoma, Large B-Cell, Diffuse; Amyloidosis, Familial; Leukemia, Myeloid, Acute; Leukemia, T-Cell; Lymphoma; Paraproteinemias; Precursor Cell Lymphoblastic Leukemia-Lymphoma; Precursor T-Cell Lymphoblastic Leukemia-Lymphoma; Red-Cell Aplasia, Pure; Smoldering Multiple Myeloma; Multiple Myeloma; Neoplasms
Lymphocyte differentiation antigen CD38 inhibitor
Small molecule
Approved
Unknown
Unknown
Diabetes Mellitus, Type 2; Lipid Metabolism Disorders; Hyperlipidemias; Atherosclerosis; Cardiovascular Diseases; Coronary Artery Disease; Dyslipidemias; Hypercholesterolemia; Hyperlipoproteinemia Type II
ATP-citrate synthase inhibitor
Small molecule
Approved
Unknown
Unknown
Unknown
GABA-B receptor agonist
Small molecule
Approved
Unknown
Unknown
Irritable Bowel Syndrome; Pain; Psoriasis; Trigeminal Neuralgia; Migraine Disorders; Sinusitis; Temporomandibular Joint Disorders
Calcitonin gene-related peptide type 1 receptor antagonist
Small molecule
Approved
Unknown
Unknown
Cushing Syndrome; Pituitary ACTH Hypersecretion
Cytochrome P450 11B1 inhibitor
Unknown
Approved
Unknown
Unknown
Unknown
Unknown
Combination
Approved
Unknown
Unknown
Unknown
Unknown
Small molecule
Approved
Unknown
Unknown
Colitis, Ulcerative; Multiple Sclerosis; Multiple Sclerosis, Relapsing-Remitting
Sphingosine 1-phosphate receptor Edg-1 modulator
Small molecule
Approved
Unknown
Unknown
Amyotrophic Lateral Sclerosis; Glycogen Storage Disease Type I; Metabolic Diseases; Migraine Disorders; Pyruvate Dehydrogenase Complex Deficiency Disease; Ataxia Telangiectasia; Glycogen Storage Disease Type V; Glycogen Storage Disease Type VII; Hemiplegia; Huntington Disease; Hypoadrenocorticism, Familial; Rett Syndrome
Supplement
Oligosaccharide
Approved
Unknown
Unknown
Renal Insufficiency, Chronic; Anemia; Anemia, Iron-Deficiency
Supplement
Small molecule
Approved
Unknown
Unknown
Unknown
Unknown
Small molecule
Approved
Unknown
Unknown
Glioma; Leukemia, Mast-Cell; Leukemia, Myeloid, Acute; Mastocytosis, Systemic; Gastrointestinal Stromal Tumors; Neoplasms
Platelet-derived growth factor receptor alpha inhibitor
Small molecule
Approved
Unknown
Unknown
Alzheimer Disease
Unknown
Small molecule
Approved
Unknown
Unknown
Leukemia, Myeloid, Acute; Breast Neoplasms; Carcinoma, Non-Small-Cell Lung; Colorectal Neoplasms; Endometrial Neoplasms; Liposarcoma; Myeloproliferative Disorders; Pancreatic Neoplasms; Stomach Neoplasms; Urinary Bladder Neoplasms; Urogenital Neoplasms; Cholangiocarcinoma; Neoplasms
Fibroblast growth factor receptor 1 inhibitor
Small molecule
Approved
Unknown
Unknown
Breast Neoplasms; Carcinoma, Hepatocellular; Friedreich Ataxia; Idiopathic Pulmonary Fibrosis; Neoplasms; Colorectal Neoplasms; Conjunctivitis, Allergic; Crohn Disease; Intestinal Neoplasms; Cytomegalovirus Infections; Fever; Malaria, Falciparum; Malaria, Vivax; Schistosomiasis; Schistosomiasis haematobia; Severe Acute Respiratory Syndrome; Malaria
Unknown
Small molecule
Approved
Unknown
Unknown
Breast Neoplasms; Glioblastoma; Liver Diseases; Carcinoma, Hepatocellular; Kidney Neoplasms; Lung Neoplasms; Melanoma; Carcinoma, Non-Small-Cell Lung; Sarcoma; Neoplasms
Hepatocyte growth factor receptor inhibitor
Combination
Approved
Unknown
Unknown
Unknown
Unknown
Small molecule
Approved
Unknown
Unknown
Neurodegenerative Diseases; Alzheimer Disease; Chronic Traumatic Encephalopathy; Cognitive Dysfunction
Diagnostic agent
Small molecule
Approved
Unknown
Unknown
Dwarfism, Pituitary
Growth hormone receptor agonist
Combination
Approved
Unknown
Unknown
Unknown
Unknown
Small molecule
Approved
Unknown
Unknown
Pneumonia, Viral; Hemorrhagic Fever, Ebola; Respiratory Distress Syndrome; Influenza, Human; Pneumonia; Coronavirus Infections; COVID-19; Severe Acute Respiratory Syndrome; Virus Diseases
Replicase polyprotein 1ab inhibitor
Unknown
Approved
Unknown
Unknown
Unknown
Unknown
Small molecule
Approved
Unknown
ORAL
Multiple Sclerosis, Relapsing-Remitting; Multiple Sclerosis
Kelch-like ECH-associated protein 1 inhibitor
Small molecule
Approved
Unknown
Unknown
Kidney Diseases; Liver Diseases; Cushing Syndrome; Essential Hypertension; Hyperaldosteronism; Hypertension; Pituitary ACTH Hypersecretion; Adrenal Gland Diseases
Unknown
Small molecule
Approved
Unknown
Unknown
Carcinoid Tumor; Colorectal Neoplasms; Endometrial Neoplasms; Leukemia; Sarcoma, Ewing; Stomach Neoplasms; Breast Neoplasms; Carcinoma, Non-Small-Cell Lung; Leiomyosarcoma; Mesothelioma; Sarcoma; Ovarian Neoplasms; Neoplasms; Small Cell Lung Carcinoma
DNA negative modulator
Oligonucleotide
Approved
Unknown
Unknown
Kidney Calculi; Hyperoxaluria, Primary
Unknown