Display Options:
Total: 10647
Small molecule
Approved
Unknown
Unknown
Astrocytoma; Central Nervous System Neoplasms; Colorectal Neoplasms; Gliosarcoma; Head and Neck Neoplasms; Lymphoma; Breast Neoplasms; Leukemia, Myelogenous, Chronic, BCR-ABL Positive; Liver Neoplasms; Ovarian Neoplasms; Urethral Neoplasms; Urinary Bladder Neoplasms; Carcinoma, Non-Small-Cell Lung; Hepatitis D; Leukemia, Myelomonocytic, Chronic; Myelodysplastic Syndromes; Neoplasm Metastasis; Progeria
Protein farnesyltransferase inhibitor
Small molecule
Approved
Unknown
Unknown
Constipation
Osmotic agent
Small molecule
Approved
Unknown
Unknown
Migraine Disorders
Serotonin 1f (5-HT1f) receptor agonist
Small molecule
Approved
Unknown
Unknown
Carcinoma, Non-Small-Cell Lung
Hepatocyte growth factor receptor inhibitor
Unknown
Approved
Unknown
Unknown
Unknown
Unknown
Small molecule
Approved
Unknown
Unknown
Pain
GABA-A receptor; anion channel positive allosteric modulator
Small molecule
Approved
Unknown
Unknown
Kidney Diseases; Liver Diseases; Sleep Apnea, Obstructive; Sleep Disorders, Circadian Rhythm; Sleep Initiation and Maintenance Disorders
Orexin receptor 1 antagonist
Small molecule
Approved
Unknown
Unknown
Astrocytoma; Biliary Tract Neoplasms; Cholangiocarcinoma; Colonic Neoplasms; Kidney Neoplasms; Leukemia, Myelogenous, Chronic, BCR-ABL Positive; Optic Nerve Glioma; Precursor Cell Lymphoblastic Leukemia-Lymphoma; Rectal Neoplasms; Sarcoma, Kaposi; Triple Negative Breast Neoplasms; Urinary Bladder Neoplasms; Adenocarcinoma; Adenocarcinoma, Follicular; Breast Neoplasms; Carcinoma, Hepatocellular; Carcinoma, Squamous Cell; Colorectal Neoplasms; Gallbladder Neoplasms; Liver Neoplasms; Lung Neoplasms; Lymphoma, Large B-Cell, Diffuse; Melanoma; Multiple Myeloma; Neurofibroma, Plexiform; Neurofibromatosis 1; Pancreatic Neoplasms; Sarcoma; Stomach Neoplasms; Carcinoma, Non-Small-Cell Lung; Thyroid Neoplasms; Neoplasms
Dual specificity mitogen-activated protein kinase kinase 1 inhibitor
Small molecule
Approved
Unknown
Unknown
Leukemia, Myeloid, Acute; Lymphoma; Prostatic Neoplasms, Castration-Resistant; Keratosis, Actinic
Tyrosine-protein kinase SRC inhibitor
Antibody
Approved
Unknown
Unknown
Anemia, Hemolytic, Autoimmune; Colorectal Neoplasms; Hematologic Neoplasms; Immune System Diseases; Amyloidosis, Familial; Leukemia, Myeloid, Acute; Leukemia, T-Cell; Lymphoma; Paraproteinemias; Precursor Cell Lymphoblastic Leukemia-Lymphoma; Precursor T-Cell Lymphoblastic Leukemia-Lymphoma; Smoldering Multiple Myeloma; Multiple Myeloma; Neoplasms
Lymphocyte differentiation antigen CD38 inhibitor
Small molecule
Approved
Unknown
Unknown
Diabetes Mellitus, Type 2; Hypercholesterolemia; Lipid Metabolism Disorders; Hyperlipidemias; Atherosclerosis; Cardiovascular Diseases; Coronary Artery Disease; Hyperlipoproteinemia Type II
ATP-citrate synthase inhibitor
Small molecule
Approved
Unknown
Unknown
Unknown
GABA-B receptor agonist
Small molecule
Approved
Unknown
Unknown
Psoriasis; Trigeminal Neuralgia; Migraine Disorders
Calcitonin gene-related peptide type 1 receptor antagonist
Small molecule
Approved
Unknown
Unknown
Pituitary ACTH Hypersecretion
Cytochrome P450 11B1 inhibitor
Unknown
Approved
Unknown
Unknown
Unknown
Unknown
Combination
Approved
Unknown
Unknown
Unknown
Unknown
Small molecule
Approved
Unknown
Unknown
Multiple Sclerosis
Sphingosine 1-phosphate receptor Edg-1 modulator
Small molecule
Approved
Unknown
Unknown
Glycogen Storage Disease Type I; Migraine Disorders; Amyotrophic Lateral Sclerosis; Ataxia Telangiectasia; Glycogen Storage Disease; Glycogen Storage Disease Type VII; Hemiplegia; Huntington Disease; Rett Syndrome
Supplement
Oligosaccharide
Approved
Unknown
Unknown
Renal Insufficiency, Chronic; Anemia; Anemia, Iron-Deficiency
Supplement
Small molecule
Approved
Unknown
Unknown
Unknown
Unknown
Small molecule
Approved
Unknown
Unknown
Glioma; Leukemia, Mast-Cell; Mastocytosis, Systemic; Gastrointestinal Stromal Tumors; Neoplasms
Platelet-derived growth factor receptor alpha inhibitor
Small molecule
Approved
Unknown
Unknown
Alzheimer Disease
Unknown
Small molecule
Approved
Unknown
Unknown
Leukemia, Myeloid, Acute; Endometrial Neoplasms; Myeloproliferative Disorders; Urinary Bladder Neoplasms; Urogenital Neoplasms; Cholangiocarcinoma; Neoplasms
Fibroblast growth factor receptor 1 inhibitor
Small molecule
Approved
Unknown
Unknown
Breast Neoplasms; Carcinoma, Hepatocellular; Friedreich Ataxia; Neoplasms; Colorectal Neoplasms; Crohn Disease; Severe Acute Respiratory Syndrome; Cytomegalovirus Infections; Fever; Malaria, Falciparum; Malaria, Vivax; Schistosomiasis; Schistosomiasis haematobia; Malaria
Unknown
Small molecule
Approved
Unknown
Unknown
Breast Neoplasms; Glioblastoma; Liver Diseases; Carcinoma, Hepatocellular; Kidney Neoplasms; Lung Neoplasms; Melanoma; Carcinoma, Non-Small-Cell Lung; Sarcoma; Neoplasms
Hepatocyte growth factor receptor inhibitor
Combination
Approved
Unknown
Unknown
Unknown
Unknown
Small molecule
Approved
Unknown
Unknown
Alzheimer Disease; Chronic Traumatic Encephalopathy; Cognitive Dysfunction
Diagnostic agent
Small molecule
Approved
Unknown
Unknown
Dwarfism, Pituitary
Growth hormone receptor agonist
Combination
Approved
Unknown
Unknown
Unknown
Unknown
Small molecule
Approved
Unknown
Unknown
Pneumonia, Viral; Hemorrhagic Fever, Ebola; Respiratory Distress Syndrome; Severe Acute Respiratory Syndrome
Replicase polyprotein 1ab inhibitor
Unknown
Approved
Unknown
Unknown
Unknown
Unknown
Small molecule
Approved
Unknown
ORAL
Multiple Sclerosis, Relapsing-Remitting; Multiple Sclerosis
Kelch-like ECH-associated protein 1 inhibitor
Small molecule
Approved
Unknown
Unknown
Kidney Diseases; Liver Diseases; Cushing Syndrome; Essential Hypertension; Hyperaldosteronism; Hypertension; Pituitary ACTH Hypersecretion; Adrenal Gland Diseases
Unknown
Small molecule
Approved
Unknown
Unknown
Carcinoid Tumor; Endometrial Neoplasms; Glioblastoma; Leukemia; Stomach Neoplasms; Breast Neoplasms; Carcinoma, Non-Small-Cell Lung; Mesothelioma; Sarcoma; Ovarian Neoplasms; Neoplasms; Small Cell Lung Carcinoma
DNA negative modulator
Oligonucleotide
Approved
Unknown
Unknown
Hyperoxaluria, Primary
Hydroxyacid oxidase 1 mRNA RNAi inhibitor