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Total: 10647
Small molecule
Approved
Unknown
Unknown
Liver Diseases; Pulmonary Disease, Chronic Obstructive; Renal Insufficiency; Sleep Apnea, Obstructive; Stress Disorders, Post-Traumatic; Sleep Initiation and Maintenance Disorders
Orexin receptor antagonist
Small molecule
Approved
Unknown
Unknown
HIV Infections; Virus Diseases
Structural capsid protein inhibitor
Small molecule
Approved
Unknown
Unknown
Epilepsies, Partial; Epilepsy, Complex Partial; Fragile X Syndrome; Smoking Cessation; Stress Disorders, Post-Traumatic; Status Epilepticus; Tuberous Sclerosis; Epilepsy; Epileptic Syndromes; Seizures; Spasms, Infantile
GABA-A receptor; anion channel positive allosteric modulator
Protein
Approved
Unknown
Unknown
Breast Neoplasms; Lymphoma; Neutropenia; Febrile Neutropenia; Neoplasms
Granulocyte colony stimulating factor receptor agonist
Small molecule
Approved
Unknown
Unknown
Heart Failure; Cardiomyopathy, Hypertrophic; Cardiovascular Diseases
Cardiac myosin inhibitor
Oligonucleotide
Approved
Unknown
Unknown
Amyloidosis; Amyloid Neuropathies, Familial; Polyneuropathies
Transthyretin mRNA rnai inhibitor
Antibody
Approved
Unknown
Unknown
Esophageal Neoplasms; Liver Neoplasms; Lymphoma; Lymphoma, Large B-Cell, Diffuse; Multiple Myeloma; Myelodysplastic Syndromes; Peritoneal Neoplasms; Adenocarcinoma, Follicular; Bile Duct Neoplasms; Biliary Tract Neoplasms; Breast Neoplasms; Carcinoma, Pancreatic Ductal; Cholangiocarcinoma; Colorectal Neoplasms; Dysgerminoma; Fallopian Tube Neoplasms; Genital Neoplasms, Female; Glioblastoma; Head and Neck Neoplasms; HIV Infections; Lung Neoplasms; Mesothelioma; Neoplasms, Germ Cell and Embryonal; Neuroendocrine Tumors; Ovarian Neoplasms; Pancreatic Neoplasms; Prostatic Neoplasms; Prostatic Neoplasms, Castration-Resistant; Sarcoma; Seminoma; Squamous Cell Carcinoma of Head and Neck; Stomach Neoplasms; Thyroid Neoplasms; Uveal Melanoma; Carcinoma, Renal Cell; Carcinoma, Squamous Cell; Melanoma; Small Cell Lung Carcinoma; Urinary Bladder Neoplasms; Carcinoma, Hepatocellular; Carcinoma, Non-Small-Cell Lung; Neoplasms
Cytotoxic T-lymphocyte protein 4 inhibitor
Combination
Approved
Unknown
Unknown
Unknown
Unknown
Small molecule
Approved
Unknown
Unknown
Dermatitis, Atopic; Psoriasis
Aryl hydrocarbon receptor agonist
Small molecule
Small molecule
Unknown
Unknown
Myelodysplastic Syndromes; Leukemia, Myeloid, Acute
Isocitrate dehydrogenase [NADP] cytoplasmic inhibitor
Protein
Approved
Unknown
Unknown
Liver Failure; Shock, Septic; Hemoptysis; Hemorrhage; Liver Cirrhosis; Hepatorenal Syndrome; Renal Insufficiency
Vasopressin V1 receptor binding agent
Small molecule
Approved
Unknown
Unknown
Immune System Diseases; Inflammation; Kidney Diseases; Liver Diseases; Pyoderma; Alopecia Areata; Colitis, Ulcerative; Hidradenitis Suppurativa; Lichen Planus; Lupus Erythematosus, Cutaneous; Lupus Erythematosus, Systemic; Lupus Nephritis; Pityriasis Rubra Pilaris; Arthritis, Psoriatic; Sjogren's Syndrome; Vitiligo; Psoriasis
Tyrosine-protein kinase TYK2 negative allosteric modulator
Protein
Approved
Unknown
Unknown
Non-alcoholic Fatty Liver Disease; Obesity, Morbid; Renal Insufficiency, Chronic; Wolfram Syndrome; Diabetes Mellitus; Diabetes Mellitus, Type 2; Obesity; Overweight
Gastric inhibitory polypeptide receptor agonist
Small molecule
Approved
Unknown
Unknown
Breast Neoplasms; Carcinoma, Non-Small-Cell Lung; Graft vs Host Disease; Leukemia, Lymphocytic, Chronic, B-Cell; Leukemia, Myelomonocytic, Chronic; Liver Diseases; Myelodysplastic Syndromes; Colorectal Neoplasms; Hodgkin Disease; Leukemia; Leukemia, Myeloid, Acute; Lymphoma; Lymphoma, Mantle-Cell; Myeloproliferative Disorders; Primary Myelofibrosis; Prostatic Neoplasms, Castration-Resistant; Severe Acute Respiratory Syndrome; Neoplasms
Tyrosine-protein kinase JAK2 inhibitor
Unknown
Approved
Unknown
Unknown
Unknown
Unknown
Small molecule
Approved
Unknown
Unknown
Food Hypersensitivity; Kidney Diseases; Liver Diseases; Stevens-Johnson Syndrome; Diabetes Mellitus, Type 1; Granuloma Annulare; Psoriasis; Sarcoidosis; Dermatitis, Atopic; Eczema
Tyrosine-protein kinase JAK1 inhibitor
Small molecule
Investigational
Unknown
Unknown
Carcinoma, Non-Small-Cell Lung; Carcinoma, Hepatocellular; Urinary Bladder Neoplasms; Biliary Tract Neoplasms; Sarcoma; Cholangiocarcinoma; Neoplasms
Fibroblast growth factor receptor inhibitor
Small molecule
Approved
Unknown
Unknown
Liver Diseases; Anemia, Sickle Cell; Thalassemia; alpha-Thalassemia; beta-Thalassemia
Pyruvate kinase isozymes R/L activator
Enzyme
Approved
Unknown
Unknown
Niemann-Pick Diseases; Niemann-Pick Disease, Type A; Niemann-Pick Disease, Type B
Sphingomyelin hydrolytic enzyme
Oligonucleotide
Approved
Unknown
Unknown
Amyotrophic Lateral Sclerosis
SOD1 mRNA antisense inhibitor
Small molecule
Approved
Unknown
Unknown
Essential Hypertension; Diabetes Mellitus; Diabetes Mellitus, Type 2
Sodium/glucose cotransporter 2 inhibitor
Protein
Approved
Unknown
Unknown
Wounds and Injuries; Brain Concussion; Brain Injuries; Fragile X Syndrome; Rett Syndrome
Unknown
Antibody
Approved
Unknown
Unknown
Arthritis, Rheumatoid; Arthritis, Psoriatic; Hidradenitis Suppurativa; Spondylitis, Ankylosing; Immune System Diseases; Parapsoriasis; Psoriasis
Interleukin 17A inhibitor
Small molecule
Approved
Unknown
Unknown
Breast Neoplasms; Fibroma; Multiple Myeloma; Pancreatic Neoplasms; Desmoid Tumors; Neoplasms
Gamma-secretase inhibitor
Small molecule
Approved
Unknown
Unknown
Mycoses; Sepsis
Unknown
Small molecule
Approved
Unknown
Unknown
Kidney Diseases; Liver Diseases; Hot Flashes
Neurokinin 3 receptor antagonist
Small molecule
Approved
Unknown
Unknown
Mood Disorders; Essential Tremor; Parkinson Disease; Depressive Disorder, Major; Depression, Postpartum; Depressive Disorder
GABA-A receptor; anion channel positive allosteric modulator
Small molecule
Approved
Unknown
Unknown
Cocaine-Related Disorders; Depressive Disorder
Serotonin 1a (5-HT1a) receptor agonist
Small molecule
Approved
Unknown
Unknown
Renal Insufficiency; Leukemia; Lymphoma, B-Cell, Marginal Zone; Multiple Sclerosis; Waldenstrom Macroglobulinemia; Leukemia, Lymphocytic, Chronic, B-Cell; Lymphoma, Mantle-Cell; Neoplasms
Tyrosine-protein kinase BTK inhibitor
Small molecule
Approved
Unknown
Unknown
Wounds and Injuries; Peripheral Vascular Diseases; Anemia; Renal Insufficiency, Chronic
Hypoxia-inducible factor prolyl hydroxylase inhibitor
Small molecule
Approved
Unknown
Unknown
Liver Diseases; Melanoma; Breast Neoplasms; Friedreich Ataxia
Nuclear factor erythroid 2-related factor 2 activator
Small molecule
Approved
Unknown
Unknown
Neoplasms
PI3-kinase p110-delta subunit inhibitor
Small molecule
Approved
Unknown
Unknown
Rosacea; Blepharitis; Eye Infections; Eye Infections, Parasitic
Ectoparasiticide
Protein
Approved
Unknown
Unknown
Hemoglobinuria, Paroxysmal; Amyotrophic Lateral Sclerosis; Hemoglobinuria; Myasthenia Gravis; Severe Acute Respiratory Syndrome
Complement C5 inhibitor
Small molecule
Approved
Unknown
Unknown
Hemoglobinuria, Paroxysmal; Kidney Diseases; Liver Diseases; Glomerulonephritis; Glomerulonephritis, Membranous; Lupus Nephritis; Macular Degeneration; Atypical Hemolytic Uremic Syndrome; Glomerulonephritis, IGA; Glomerulonephritis, Membranoproliferative; Hemoglobinuria
Complement factor B inhibitor