Display Options:
Total: 10647
Protein
Approved
Unknown
Unknown
Amyotrophic Lateral Sclerosis; Hemoglobinuria, Paroxysmal; Myasthenia Gravis; Severe Acute Respiratory Syndrome
Complement C5 inhibitor
Small molecule
Approved
Unknown
Unknown
Endometrial Neoplasms; Fallopian Tube Neoplasms; Hematologic Neoplasms; Hereditary Breast and Ovarian Cancer Syndrome; Ovarian Neoplasms; Uterine Cervical Neoplasms; Adenocarcinoma; Carcinoma, Non-Small-Cell Lung; Carcinoma, Squamous Cell; Multiple Myeloma; Neoplasms; Prostatic Neoplasms; Stomach Neoplasms; Breast Neoplasms; Prostatic Neoplasms, Castration-Resistant
Serine/threonine-protein kinase AKT inhibitor
Small molecule
Approved
Unknown
Unknown
Glomerulonephritis; Glomerulonephritis, Membranous; Atypical Hemolytic Uremic Syndrome; Glomerulonephritis, IGA; Hemoglobinuria, Paroxysmal
Complement factor B inhibitor
Small molecule
Approved
Unknown
Unknown
Dry Eye Syndromes; Myositis Ossificans
Retinoic acid receptor gamma agonist
Small molecule
Approved
Unknown
Unknown
Alopecia Areata; Crohn Disease; Dermatitis, Atopic; Eosinophilic Esophagitis; Inflammatory Bowel Diseases; Liver Cirrhosis, Biliary; Pyoderma; Colitis, Ulcerative
Sphingosine 1-phosphate receptor Edg-1 agonist
Small molecule
Approved
Unknown
Unknown
Colitis, Ulcerative; Muscular Dystrophy, Duchenne
Unknown
Small molecule
Unknown
Unknown
Unknown
Severe Acute Respiratory Syndrome; Migraine Disorders
Unknown
Small molecule
Approved
Unknown
Unknown
Carcinoma, Non-Small-Cell Lung; Polycythemia Vera; Thrombocythemia, Essential; Carcinoma, Pancreatic Ductal; Primary Myelofibrosis
Tyrosine-protein kinase JAK1 inhibitor
Oligonucleotide
Approved
Unknown
Unknown
Unknown
Unknown
Small molecule
Approved
Unknown
Unknown
Hypertension; Glomerulonephritis, IGA; Glomerulosclerosis, Focal Segmental
Endothelin receptor ET-A antagonist
Small molecule
Approved
Unknown
Unknown
Amyloidosis; Amyloid Neuropathies, Familial
Transthyretin stabiliser
Small molecule
Approved
Unknown
Unknown
Breast Neoplasms; Neoplasms
PI3-kinase p110-alpha subunit inhibitor
Small molecule
Approved
Unknown
Unknown
Carcinoma, Renal Cell; HIV Infections; Melanoma; Neutropenia; Waldenstrom Macroglobulinemia
C-X-C chemokine receptor type 4 antagonist
Small molecule
Approved
Unknown
Unknown
Carcinoma, Non-Small-Cell Lung
Unknown
Small molecule
Approved
Unknown
Unknown
Unknown
Unknown
Small molecule
Approved
Unknown
Unknown
Kidney Diseases; Liver Diseases; Glomerulonephritis, Membranoproliferative; Hemoglobinuria, Paroxysmal
Complement factor D inhibitor
Small molecule
Approved
Unknown
Unknown
Liver Diseases; Cholangitis, Sclerosing; Hyperlipidemias; Hyperlipoproteinemia Type II; Non-alcoholic Fatty Liver Disease; Liver Cirrhosis, Biliary
Peroxisome proliferator-activated receptor delta agonist
Small molecule
Approved
Unknown
Unknown
Asthma; Cystic Fibrosis; Severe Acute Respiratory Syndrome; Pulmonary Disease, Chronic Obstructive
Unknown
Small molecule
Approved
Unknown
Unknown
Kidney Diseases; Liver Diseases; Essential Hypertension; Hypertension
Endothelin receptor, ET-A/ET-B antagonist
Small molecule
Approved
Unknown
Unknown
Carcinoma, Non-Small-Cell Lung; Neoplasms
Unknown
Oligonucleotide
Approved
Unknown
Unknown
Breast Neoplasms; Lymphoma; Neuroblastoma; Carcinoma, Non-Small-Cell Lung; Multiple Myeloma; Myelodysplastic Syndromes; Polycythemia Vera; Thrombocythemia, Essential; Primary Myelofibrosis
Telomerase reverse transcriptase inhibitor
Small molecule
Approved
Unknown
Unknown
Hyperlipoproteinemia Type II; Non-alcoholic Fatty Liver Disease
Thyroid hormone receptor beta-1 agonist
Small molecule
Approved
Unknown
Unknown
Liver Diseases; Renal Insufficiency, Chronic; Anemia
Egl nine homolog 1 inhibitor
Small molecule
Approved
Unknown
Unknown
Gaucher Disease; Niemann-Pick Disease, Type C; Amyotrophic Lateral Sclerosis; Myositis, Inclusion Body
Unknown
Small molecule
Approved
Unknown
Unknown
Unknown
Unknown
Small molecule
Approved
Unknown
Unknown
Glioma
IDH1/IDH2 inhibitor
Small molecule
Approved
Unknown
Unknown
Crohn Disease; Hodgkin Disease; Polycythemia Vera; Arthritis, Juvenile; Leukemia, Lymphocytic, Chronic, B-Cell; Multiple Myeloma; Myeloproliferative Disorders; Muscular Dystrophy, Duchenne
Unknown
Small molecule
Approved
Unknown
Unknown
Arrhythmias, Cardiac; Atrial Fibrillation; Cardiovascular Diseases; Shock, Septic
Beta-1 adrenergic receptor antagonist
Small molecule
Approved
Unknown
Unknown
Liver Diseases; Diabetes Mellitus, Type 2; Non-alcoholic Fatty Liver Disease; Liver Cirrhosis, Biliary
Peroxisome proliferator-activated receptor alpha agonist
Small molecule
Approved
Unknown
Unknown
Lung Neoplasms; Melanoma; Carcinoma, Non-Small-Cell Lung
ALK tyrosine kinase receptor inhibitor
Small molecule
Investigational
Unknown
Unknown
Multiple Myeloma; Carcinoma, Non-Small-Cell Lung; Carcinoma, Squamous Cell; Graft vs Host Disease; Hematologic Neoplasms; Hodgkin Disease; Lymphoma, Non-Hodgkin; Leukemia, Myeloid, Acute; Melanoma; Myelodysplastic Syndromes; Ovarian Neoplasms; Precursor Cell Lymphoblastic Leukemia-Lymphoma; Sarcoma, Ewing; Neoplasms
Unknown
Small molecule
Approved
Unknown
Unknown
Colorectal Neoplasms; Neoplasms; Carcinoma, Non-Small-Cell Lung; Neurofibromatosis 1
Dual specificity mitogen-activated protein kinase kinase 1 inhibitor
Small molecule
Investigational
Unknown
Unknown
Carcinoma, Hepatocellular; Multiple Myeloma; Neoplasms; Waldenstrom Macroglobulinemia
26S proteosome inhibitor
Unknown
Investigational
Unknown
Unknown
Unknown
Unknown
Unknown
Investigational
Unknown
Unknown
Neoplasms
Unknown