Display Options:
Total: 6532
Small molecule
Approved
Unknown
ORAL
Carcinoma, Renal Cell; Colorectal Neoplasms; Cystadenocarcinoma, Serous; Diffuse Intrinsic Pontine Glioma; Glioma; Lymphoma; Lymphoma, Non-Hodgkin; Multiple Myeloma; Neoplasm Metastasis; Neuroblastoma; Neurofibromatosis 1; Osteosarcoma; Ovarian Neoplasms; Prostatic Neoplasms; Rhabdoid Tumor; Rhabdomyosarcoma; Sarcoma, Ewing; Sarcoma, Kaposi; Urinary Bladder Neoplasms; Biliary Tract Neoplasms; Brain Neoplasms; Breast Neoplasms, Male; Carcinoma, Hepatocellular; Carcinoma, Pancreatic Ductal; Carcinoma, Squamous Cell; Endometrial Neoplasms; Genital Neoplasms, Female; Glioblastoma; Head and Neck Neoplasms; Hemangiosarcoma; Lung Neoplasms; Lymphoma, Mantle-Cell; Melanoma; Meningioma; Mesothelioma; Neuroendocrine Tumors; Oligodendroglioma; Paraganglioma; Prostatic Neoplasms, Castration-Resistant; Thyroid Neoplasms; Carcinoma, Non-Small-Cell Lung; Liposarcoma; Breast Neoplasms; Neoplasms
Cyclin-dependent kinase 4 inhibitor
Small molecule
Approved
Unknown
Unknown
Unknown
Unknown
Small molecule
Approved
Unknown
ORAL
Kidney Diseases; Liver Diseases; Atrial Fibrillation; Atrial Flutter; Hemorrhage; Thromboembolism; Thrombosis; Venous Thromboembolism
Coagulation factor X inhibitor
Small molecule
Approved
Unknown
Unknown
Hematologic Neoplasms; Liver Diseases; Multiple Myeloma; Neoplasms; Leukemia, Myeloid; Leukemia, Myeloid, Acute; Myelodysplastic Syndromes; Leukemia
Unknown
Small molecule
Approved
Unknown
ORAL
Liver Diseases; Precursor Cell Lymphoblastic Leukemia-Lymphoma; Rectal Neoplasms; Myelodysplastic Syndromes; Leukemia; Leukemia, Mast-Cell; Leukemia, Myeloid, Acute; Mastocytosis; Mastocytosis, Systemic; Neoplasms
Platelet-derived growth factor receptor inhibitor
Small molecule
Approved
Unknown
Unknown
Carcinoma, Non-Small-Cell Lung; Carcinoma, Squamous Cell; Colonic Neoplasms; Lymphoma; Precursor Cell Lymphoblastic Leukemia-Lymphoma; Prostatic Neoplasms, Castration-Resistant; Renal Insufficiency; Urinary Bladder Neoplasms; Breast Neoplasms; Cholangiocarcinoma; Endometrial Neoplasms; Gallbladder Neoplasms; Leukemia, Lymphocytic, Chronic, B-Cell; Lymphoma, B-Cell, Marginal Zone; Lymphoma, Follicular; Lymphoma, Large B-Cell, Diffuse; Lymphoma, Mantle-Cell; Lymphoma, Non-Hodgkin; Neoplasms
PI3-kinase p110-alpha subunit inhibitor
Small molecule
Approved
Unknown
Unknown
Carcinoma; Carcinoma, Hepatocellular; Colorectal Neoplasms; Leukemia, Myelogenous, Chronic, BCR-ABL Positive; Ovarian Neoplasms; Stomach Neoplasms; Carcinoma, Non-Small-Cell Lung; Glioblastoma; Hemangiosarcoma; Prostatic Neoplasms; Biliary Tract Neoplasms; Breast Neoplasms; Neoplasms
Epidermal growth factor receptor erbB1 inhibitor
Small molecule
Approved
Unknown
Unknown
Cachexia; Dwarfism, Pituitary
Ghrelin receptor agonist
Small molecule
Approved
Unknown
Unknown
Hypersensitivity; Substance Withdrawal Syndrome; Cocaine-Related Disorders; Opioid-Related Disorders
Unknown
Small molecule
Approved
Unknown
TOPICAL
Wounds and Injuries; Impetigo
DNA gyrase inhibitor
Small molecule
Approved
Unknown
ORAL
Kidney Diseases; Liver Diseases; Aspergillosis, Allergic Bronchopulmonary; Muscular Dystrophies, Limb-Girdle; Muscular Dystrophies; Muscular Dystrophy, Duchenne
Glucocorticoid receptor agonist
Small molecule
Approved
Unknown
Unknown
Liver Diseases; Pneumonia; Gonorrhea; Infections; Pneumonia, Bacterial; Bacterial Infections
Unknown
Small molecule
Approved
Unknown
ORAL
Neoplasms; Ovarian Neoplasms; Breast Neoplasms
Epidermal growth factor receptor erbB1 inhibitor
Small molecule
Approved
Unknown
ORAL
Vaginal Discharge; Amebiasis; Trichomonas Infections; Vaginosis, Bacterial
DNA inhibitor
Small molecule
Approved
Unknown
Unknown
Kidney Diseases; Liver Diseases; Multiple System Atrophy; Parkinson Disease
Monoamine oxidase B inhibitor
Small molecule
Approved
Unknown
ORAL
Heart Failure; Diabetes Mellitus; Diabetes Mellitus, Type 2; Mitral Valve Insufficiency
Sodium/glucose cotransporter 2 inhibitor
Small molecule
Approved
Unknown
OPHTHALMIC
Glaucoma; Glaucoma, Open-Angle; Ocular Hypertension
Prostanoid FP receptor agonist
Small molecule
Approved
Unknown
Unknown
Bronchiolitis Obliterans Syndrome; Glioblastoma; Myelodysplastic Syndromes; Leukemia, Myeloid, Acute; Sarcoma; Neoplasms
Smoothened homolog antagonist
Small molecule
Approved
Unknown
ORAL
Dysentery; Irritable Bowel Syndrome; Diarrhea; Eye Infections; Tuberculosis
Unknown
Small molecule
Approved
Unknown
Unknown
Renal Insufficiency; Renal Insufficiency, Chronic; Urinary Tract Infections; Bacterial Infections
Unknown
Small molecule
Approved
Unknown
Unknown
Smallpox; Virus Diseases
Envelope phospholipase OPG057 inhibitor
Small molecule
Approved
Unknown
Unknown
Unknown
Progesterone receptor agonist
Small molecule
Approved
Unknown
Unknown
Fabry Disease
Alpha-galactosidase A stabiliser
Small molecule
Approved
Unknown
ORAL
Renal Insufficiency, Chronic; Hyperoxaluria, Primary; Epilepsies, Myoclonic; Epilepsy; Myoclonic Epilepsy, Juvenile; Seizures
Unknown
Small molecule
Approved
Unknown
Unknown
Anemia, Aplastic; Blood Platelet Disorders; Liver Diseases; Purpura, Thrombocytopenic, Idiopathic; Thrombocytopenia; Hemorrhage
Thrombopoietin receptor agonist
Small molecule
Approved
Unknown
Unknown
Unknown
Unknown
Small molecule
Approved
Unknown
ORAL
Leukemia, Myeloid, Acute
Smoothened homolog antagonist
Small molecule
Approved
Unknown
Unknown
Cocaine-Related Disorders; Heroin Dependence; Liver Failure; Marijuana Abuse; Opioid-Related Disorders; Substance-Related Disorders
Unknown
Small molecule
Approved
Unknown
Unknown
Ischemic Stroke; Acne Vulgaris; Bacterial Infections
Unknown
Small molecule
Approved
Unknown
ORAL
Liver Diseases; Lymphoma, Large B-Cell, Diffuse; Melanoma; Mycosis Fungoides; Precursor Cell Lymphoblastic Leukemia-Lymphoma; Sezary Syndrome; Arthritis, Rheumatoid; Asthma; Carcinoma, Squamous Cell; Hematologic Neoplasms; Leukemia; Leukemia, Lymphoid; Lymphoma; Lymphoma, Non-Hodgkin; Lymphoma, T-Cell, Peripheral; Severe Acute Respiratory Syndrome; Leukemia, Lymphocytic, Chronic, B-Cell; Lymphoma, Follicular; Neoplasms
Unknown
Small molecule
Approved
Unknown
Unknown
Cystitis, Hemorrhagic; Infections; Urinary Tract Infections; Pneumonia; Pneumonia, Bacterial; Bacterial Infections
Unknown
Small molecule
Approved
Unknown
Unknown
Acute Pain
Opioid receptors; mu/kappa/delta agonist
Small molecule
Approved
Unknown
Unknown
HIV Infections
Human immunodeficiency virus type 1 integrase inhibitor
Small molecule
Approved
Unknown
ORAL
Liver Diseases; Thrombocytopenia
Thrombopoietin receptor agonist
Small molecule
Approved
Unknown
Unknown
Unknown
Unknown