Display Options:
Total: 10647
Small molecule
Approved
OTHER
ORAL
Alcoholism; Brain Injuries; Chondrocalcinosis; Diabetes Mellitus; Diabetes Mellitus, Type 2; Influenza in Birds; Kidney Diseases; Neoplasms; Cellulitis; Heart Failure; Heart Failure, Systolic; Cystitis, Hemorrhagic; Infections; Infertility, Male; Obesity; Urinary Tract Infections; Gout
Solute carrier family 22 member 11 inhibitor
Small molecule
Approved
OTHER
ORAL
Unknown
Unknown
Small molecule
Approved
OTHER
INJECTION; ORAL
Lung Diseases, Obstructive
Phosphodiesterase 3A inhibitor
Small molecule
Approved
OTHER
ORAL
Amphetamine-Related Disorders; Fatigue; HIV Infections; Multiple Myeloma; Neoplasms; Obesity; Prostatic Neoplasms, Castration-Resistant; Retinal Dystrophies; Sarcoma; Alcohol-Related Disorders; Breast Neoplasms; Carcinoma, Non-Small-Cell Lung; Cocaine-Related Disorders; Glioblastoma; Melanoma; Neoplasms, Germ Cell and Embryonal; Opioid-Related Disorders; Pancreatic Neoplasms; Paraganglioma; Severe Acute Respiratory Syndrome; Alcoholism; Ectoparasitic Infestations
Aldehyde dehydrogenase inhibitor
Small molecule
Approved
Unknown
Unknown
Urinary Bladder, Neurogenic; Digestive System Diseases
Unknown
Small molecule
Approved
OTHER
TOPICAL
Dandruff; Dermatitis, Seborrheic; Pruritus; Tinea
Unknown
Small molecule
Approved
Unknown
Unknown
Hypotension, Orthostatic; Orthostatic Intolerance
Unknown
Small molecule
Approved
OTHER
ORAL
Epilepsy
Sodium channel alpha subunit blocker
Small molecule
Approved
OTHER
ORAL
Unknown
Histamine H2 receptor antagonist
Small molecule
Approved
Unknown
Unknown
Cardiovascular Diseases; Mydriasis; Prostatic Neoplasms, Castration-Resistant; Pheochromocytoma
Adrenergic receptor alpha antagonist
Small molecule
Approved
OTHER
TOPICAL
Unknown
Tyrosinase inhibitor
Small molecule
Approved
OTHER
FOR RX COMPOUNDING; INJECTION; ORAL; RECTAL; TOPICAL; VAGINAL
Diabetes Mellitus, Type 1; Fibromyalgia; HIV Infections; Infections; Insulin Resistance; Lymphoma, Large-Cell, Anaplastic; Obesity; Tobacco Use Disorder; Addison Disease; Adrenal Cortex Neoplasms; Aging; Atrial Fibrillation; Borderline Personality Disorder; Central Nervous System Neoplasms; Granuloma, Pyogenic; Heart Failure; Inflammatory Bowel Diseases; Leukemia, Mast-Cell; Lymphohistiocytosis, Hemophagocytic; Lymphoma, Large B-Cell, Diffuse; Melanoma; Memory Disorders; Multiple Myeloma; Myocardial Infarction; Neoplasms, Plasma Cell; Opioid-Related Disorders; Pancreatitis; Phobic Disorders; Wounds and Injuries; Alcoholism; Alopecia Areata; Anemia, Refractory; Anemia, Refractory, with Excess of Blasts; Bronchopulmonary Dysplasia; Eczema; Heart Arrest; Hypotension; Hypoxia; Influenza, Human; Leukemia, Biphenotypic, Acute; Leukemia, Erythroblastic, Acute; Leukemia, Lymphoid; Leukemia, Megakaryoblastic, Acute; Leukemia, Monocytic, Acute; Leukemia, Myeloid, Acute; Leukemia, Myelomonocytic, Acute; Leukemia, Myelomonocytic, Chronic; Liver Cirrhosis; Myelodysplastic Syndromes; Myeloproliferative Disorders; Oral Submucous Fibrosis; Pain; Pneumonia, Viral; Precursor Cell Lymphoblastic Leukemia-Lymphoma; Prostatic Neoplasms; Prostatic Neoplasms, Castration-Resistant; Sepsis; Severe Acute Respiratory Syndrome; Shock, Septic; Adrenal Hyperplasia, Congenital; Adrenal Insufficiency; Arthritis, Juvenile; Arthritis, Psoriatic; Arthritis, Rheumatoid; Asthma; Bursitis; Colitis, Ulcerative; Conjunctivitis, Allergic; Crohn Disease; Dermatitis; Dermatitis, Atopic; Dermatitis, Seborrheic; Endocrine System Diseases; Exanthema; Eye Diseases; Hemorrhoids; Herpes Labialis; Inflammation; Leukemia; Lymphoma; Nasal Obstruction; Neoplasms; Osteoarthritis; Otitis Externa; Pneumonia; Pruritus; Psoriasis; Serum Sickness; Skin Diseases; Spondylitis; Tenosynovitis
Glucocorticoid receptor agonist
Small molecule
Approved
Unknown
Unknown
Hypoglycemia; Obesity; Sleep Apnea, Obstructive; Mydriasis; Presbyopia; Cardiovascular Diseases
Unknown
Small molecule
Approved
OTHER
INJECTION; ORAL
Osteomyelitis; Psoriasis; Rheumatic Heart Disease; HIV Infections; Syphilis; Bacterial Infections; Infections
Bacterial penicillin-binding protein inhibitor
Small molecule
Approved
Unknown
Unknown
Hypertension; Hypotension, Orthostatic; Infections; Mucositis; Neoplasms; Obesity; Ocular Hypertension; Orthostatic Intolerance; Ovarian Cysts; Pain; Stomatitis; Vascular Diseases; Acute Lung Injury; Bronchiolitis; Cognitive Dysfunction; Mydriasis; Shock, Septic; Stress Disorders, Post-Traumatic; Common Cold; Eye Diseases; Fecal Incontinence; Hypotension; Influenza, Human; Ischemic Stroke; Respiratory Tract Infections; Rhinitis, Allergic, Seasonal; Stroke; Cardiovascular Diseases; Eye Manifestations; Hemorrhoids; Nasal Obstruction
Unknown
Small molecule
Approved
Unknown
Unknown
Arthritis, Rheumatoid; Glioblastoma; Neoplasm Metastasis; Adenocarcinoma; Asperger Syndrome; Autistic Disorder; Biliary Tract Diseases; Biliary Tract Neoplasms; Carcinoma, Neuroendocrine; Child Development Disorders, Pervasive; Colonic Neoplasms; Esophageal Neoplasms; Neoplasms; Osteosarcoma; Uterine Neoplasms; Carcinoma, Hepatocellular; Carcinoma, Pancreatic Ductal; Colorectal Neoplasms; Depressive Disorder; Down Syndrome; Liver Neoplasms; Nasopharyngeal Carcinoma; Pancreatic Neoplasms; Psychotic Disorders; Rectal Neoplasms; Schizophrenia; Stomach Neoplasms
Unknown
Small molecule
Approved
OTHER
INJECTION; ORAL
Melanoma; Osteomyelitis; Acquired Immunodeficiency Syndrome; Diabetic Foot; Tuberculosis, Multidrug-Resistant; Ulcer; Meningitis; HIV Infections; Silicosis; Tuberculosis; Tuberculosis, Pulmonary
Enoyl-[acyl-carrier-protein] reductase inhibitor
Small molecule
Approved
Unknown
Unknown
Glucosephosphate Dehydrogenase Deficiency; Obesity; Severe Acute Respiratory Syndrome; Malaria, Falciparum; Malaria, Vivax; Pneumonia, Pneumocystis; Malaria
Unknown
Small molecule
Approved
Unknown
Unknown
Bradycardia; Myalgia; Stroke
Unknown
Small molecule
Approved
Unknown
Unknown
Anemia, Sickle Cell; Constipation; Neck Pain; Osteoarthritis; Myopia; Toothache; Cough; Pain
Unknown
Small molecule
Approved
Unknown
Unknown
Lung Neoplasms; Polycystic Kidney Diseases; Rectal Neoplasms; Breast Neoplasms; Cardiovascular Diseases; Cerebral Hemorrhage; Heart Diseases; Heart Failure; Neoplasms; Pre-Eclampsia; Stroke; Vascular Diseases; Atherosclerosis; Coronary Disease; Diabetes Mellitus, Type 2; Hypercholesterolemia; Ovarian Neoplasms; Uterine Cervical Neoplasms; Hypertension
Unknown
Small molecule
Approved
Unknown
Unknown
Digestive System Diseases
Unknown
Small molecule
Approved
OTHER
ORAL
Burkitt Lymphoma; Astrocytoma; Blastic Plasmacytoid Dendritic Cell Neoplasm; Brain Neoplasms; Colitis; Glioblastoma; Glioma; Oligodendroglioma; Colitis, Ulcerative; Crohn Disease; Histiocytosis, Langerhans-Cell; Leukemia; Leukemia, Biphenotypic, Acute; Leukemia, Myeloid, Acute; Leukemia, Promyelocytic, Acute; Lymphoma; Precursor T-Cell Lymphoblastic Leukemia-Lymphoma; Leukemia, Lymphoid; Neoplasms; Precursor Cell Lymphoblastic Leukemia-Lymphoma
Amidophosphoribosyltransferase inhibitor
Small molecule
Approved
OTHER
SUBCUTANEOUS
Dermatitis; Fanconi Anemia; Gout; HIV Infections; Inflammation; Leukemia, Plasma Cell; Malaria; Melanoma; Scleroderma, Systemic; Severe Acute Respiratory Syndrome; Anemia, Diamond-Blackfan; Anemia, Sickle Cell; Blast Crisis; Blastic Plasmacytoid Dendritic Cell Neoplasm; Bone Marrow Failure Disorders; Burkitt Lymphoma; Carcinoma, Merkel Cell; Carcinoma, Non-Small-Cell Lung; Central Serous Chorioretinopathy; Colitis, Ulcerative; Colorectal Neoplasms; Constriction, Pathologic; Coronary Disease; Desmoid Tumors; Ependymoma; Hematologic Neoplasms; Hemoglobinuria; Histiocytosis, Langerhans-Cell; Immunoblastic Lymphadenopathy; Kidney Neoplasms; Leukemia, Large Granular Lymphocytic; Leukemia, Lymphocytic, Chronic, B-Cell; Leukemia-Lymphoma, Adult T-Cell; Leukemia, Myelomonocytic, Juvenile; Lymphohistiocytosis, Hemophagocytic; Lymphoma, AIDS-Related; Lymphoma, B-Cell, Marginal Zone; Lymphoma, Mantle-Cell; Lymphoma, T-Cell, Peripheral; Mesothelioma; Multiple Myeloma; Myasthenia Gravis; Myelodysplastic-Myeloproliferative Diseases; Myocardial Infarction; Neoplasm Metastasis; Neoplasms, Plasma Cell; Neuroblastoma; Neurofibromatosis 1; Osteopetrosis; Ovarian Neoplasms; Polycythemia Vera; Primary Myelofibrosis; Retinitis Pigmentosa; Schizophrenia; Severe Combined Immunodeficiency; Sezary Syndrome; Shwachman-Diamond Syndrome; Testicular Neoplasms; Urticaria; Waldenstrom Macroglobulinemia; Wiskott-Aldrich Syndrome; Alopecia Areata; Anemia, Aplastic; Anemia, Refractory; Anemia, Refractory, with Excess of Blasts; Asthma; Brain Neoplasms; Carcinoma, Squamous Cell; Cardiovascular Diseases; Central Nervous System Neoplasms; Choriocarcinoma; Choroid Plexus Neoplasms; Crohn Disease; Dermatitis, Atopic; Dermatomyositis; Gestational Trophoblastic Disease; Giant Cell Arteritis; Graft vs Host Disease; Granuloma, Lethal Midline; Granulomatosis with Polyangiitis; Head and Neck Neoplasms; Hearing Loss, Sensorineural; Hodgkin Disease; Hydatidiform Mole; Leukemia; Leukemia, Biphenotypic, Acute; Leukemia, Erythroblastic, Acute; Leukemia, Lymphoid; Leukemia, Megakaryoblastic, Acute; Leukemia, Monocytic, Acute; Leukemia, Myelogenous, Chronic, BCR-ABL Positive; Leukemia, Myeloid, Acute; Leukemia, Myelomonocytic, Acute; Leukemia, Myelomonocytic, Chronic; Leukemia, Promyelocytic, Acute; Liver Cirrhosis, Biliary; Lupus Erythematosus, Systemic; Lymphoma; Lymphoma, Follicular; Lymphoma, Large B-Cell, Diffuse; Lymphoma, Large-Cell, Anaplastic; Lymphoma, T-Cell, Cutaneous; Macular Edema; Medulloblastoma; Multiple Sclerosis; Myelodysplastic Syndromes; Myeloproliferative Disorders; Neuroectodermal Tumors, Primitive; Osteoarthritis; Osteosarcoma; Pemphigoid, Bullous; Precursor T-Cell Lymphoblastic Leukemia-Lymphoma; Pregnancy, Ectopic; Retroperitoneal Fibrosis; Sarcoma; Spondylitis, Ankylosing; Urethral Neoplasms; Urinary Bladder Neoplasms; Uterine Cervical Neoplasms; Uveitis; Uveitis, Intermediate; Vasculitis; Vitiligo; Vitreoretinopathy, Proliferative; Arthritis; Arthritis, Juvenile; Arthritis, Psoriatic; Arthritis, Rheumatoid; Breast Neoplasms; Immune System Diseases; Lymphoma, Non-Hodgkin; Meningeal Carcinomatosis; Mycosis Fungoides; Neoplasms; Precursor Cell Lymphoblastic Leukemia-Lymphoma; Psoriasis
Dihydrofolate reductase inhibitor
Small molecule
Approved
OTHER
ORAL
Unknown
Bacterial dihydropteroate synthase inhibitor
Small molecule
Approved
OTHER
ORAL
Osteomyelitis; Bacterial Infections; Eye Infections
Bacterial dihydropteroate synthase inhibitor
Small molecule
Approved
OTHER
INJECTION; SUBCUTANEOUS
Muscular Dystrophy, Facioscapulohumeral; HIV Wasting Syndrome; Prostatic Neoplasms; Prostatic Neoplasms, Castration-Resistant; Pulmonary Disease, Chronic Obstructive; Weight Loss; Hypogonadism; Neoplasms; Orchitis
Androgen Receptor agonist
Unknown
Approved
OTHER
INJECTION
Adenocarcinoma, Follicular; Thyroid Neoplasms; Head and Neck Neoplasms
Thyroid stimulating hormone receptor agonist
Small molecule
Approved
OTHER
ORAL
Osteomyelitis; Bacterial Infections; Cystitis; Urinary Tract Infections
DNA inhibitor
Small molecule
Approved
OTHER
ORAL
Andersen Syndrome; Diabetes Mellitus, Type 1; Hypotension, Orthostatic; Melanoma; Prostatic Neoplasms, Castration-Resistant; Psychotic Disorders; Schizophrenia; Small Cell Lung Carcinoma; Chronic Pain; Cysticercosis; Helicobacter Infections; Hypertension, Pulmonary; Kidney Diseases; Landau-Kleffner Syndrome; Macular Edema; Multiple Sclerosis; Retinoschisis; Sleep Apnea, Obstructive; Status Epilepticus; Stroke; Apnea; Carcinoma, Hepatocellular; Hydrocephalus, Normal Pressure; Pseudotumor Cerebri; Altitude Sickness; Edema; Epilepsy; Glaucoma; Glaucoma, Angle-Closure; Heart Failure; Seizures
Carbonic anhydrase II inhibitor
Small molecule
Approved
OTHER
ORAL
Amyotrophic Lateral Sclerosis; Gangliosidoses, GM2; Head and Neck Neoplasms; Leukemia, Lymphocytic, Chronic, B-Cell; Myelodysplastic Syndromes; Sandhoff Disease; Tay-Sachs Disease; Toxoplasmosis, Cerebral; Anemia; Chorioretinitis; Depressive Disorder; HIV Infections; Malaria, Falciparum; Malaria, Vivax; Pneumonia, Pneumocystis; Pregnancy; Premature Birth; Schistosomiasis; Schizophrenia; Toxoplasmosis, Congenital; Malaria; Toxoplasmosis
Dihydrofolate reductase inhibitor
Small molecule
Approved
Unknown
Unknown
Pain
Unknown
Small molecule
Approved
OTHER
INJECTION; ORAL
Urinary Bladder, Overactive; Peptic Ulcer
Muscarinic acetylcholine receptor M1 antagonist
Small molecule
Approved
Unknown
Unknown
Unknown
Unknown
Small molecule
Approved
Unknown
Unknown
Digestive System Diseases
Unknown