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Total: 10647
Small molecule
Approved
Unknown
Unknown
Amyotrophic Lateral Sclerosis; Cystic Fibrosis; Lymphoma; Muscular Atrophy, Spinal; Myelodysplastic-Myeloproliferative Diseases; Myelodysplastic Syndromes; Argininosuccinic Aciduria; HIV Infections; Huntington Disease; Leukemia; Machado-Joseph Disease; Pyruvate Dehydrogenase Complex Deficiency Disease; Tuberculosis, Pulmonary; Carbamoyl-Phosphate Synthase I Deficiency Disease; Citrullinemia; Hyperammonemia; Ornithine Carbamoyltransferase Deficiency Disease; Urea Cycle Disorders, Inborn
Glutamine sequestering agent
Enzyme
Approved
Unknown
Unknown
Diabetes Mellitus, Type 1; Hypoglycemia; Pancreatic Neoplasms; Pancreatitis; Cystic Fibrosis; Exocrine Pancreatic Insufficiency; Pancreatitis, Chronic
Fatty acids hydrolytic enzyme
Small molecule
Approved
DIABETES DRUGS & ENDOCRINOLOGY; OTHER
ORAL
Postoperative Nausea and Vomiting; Sleep Apnea, Obstructive; Stomach Diseases; Alcoholism; Amphetamine-Related Disorders; Anorexia; Anorexia Nervosa; Cachexia; Cocaine-Related Disorders; Fibromyalgia; Paraganglioma; Substance-Related Disorders; Weight Loss; Anxiety; Child Development Disorders, Pervasive; Dementia; Heroin Dependence; Nausea; Schizophrenia; Depressive Disorder; Depressive Disorder, Major; Sleep Initiation and Maintenance Disorders
Adrenergic receptor alpha-2 antagonist
Small molecule
Approved
Unknown
Unknown
Hepatopulmonary Syndrome; Hypotension, Orthostatic; Ischemic Stroke; Ascites; Hypotension; Shock, Septic; Spinal Cord Injuries; Cardiovascular Diseases
Unknown
Small molecule
Approved
OTHER
INTRAMUSCULAR; ORAL
Dyskinesia, Drug-Induced; Lecithin Cholesterol Acyltransferase Deficiency; Mood Disorders; Weight Loss; Amyotrophic Lateral Sclerosis; Anorexia Nervosa; Autistic Disorder; Delirium; Opioid-Related Disorders; Vomiting; Alcoholism; Anorexia; Anxiety; Borderline Personality Disorder; Dementia; Depressive Disorder; Depressive Disorder, Treatment-Resistant; Developmental Disabilities; Feeding and Eating Disorders; Gambling; Genital Neoplasms, Female; Huntington Disease; Intellectual Disability; Nausea; Neoplasms; Postoperative Nausea and Vomiting; Testicular Neoplasms; Weight Gain; Bipolar Disorder; Depressive Disorder, Major; Mental Disorders; Psychomotor Agitation; Psychotic Disorders; Schizophrenia
D2-like dopamine receptor antagonist
Small molecule
Approved
Unknown
TOPICAL
Herpes Labialis; Virus Diseases
Human herpesvirus 1 DNA polymerase inhibitor
Small molecule
Approved
CANCER; OTHER; PREGNANCY AND GYNECOLOGY
INJECTION; INTRAVENOUS
Breast Neoplasms, Male; Carcinoma, Endometrioid; Carcinoma, Renal Cell; Colonic Neoplasms; Cystadenoma, Serous; Digestive System Diseases; Lymphoma; Multiple Myeloma; Myelodysplastic Syndromes; Myeloproliferative Disorders; Nausea; Neoplasms, Plasma Cell; Sarcoma, Synovial; Vaginal Neoplasms; Vulvar Neoplasms; Biliary Tract Neoplasms; Carcinoma, Hepatocellular; Carcinoma, Intraductal, Noninfiltrating; Carcinoma, Large Cell; Carcinoma, Neuroendocrine; Carcinoma, Ovarian Epithelial; Carcinoma, Transitional Cell; Colorectal Neoplasms; Gastrointestinal Stromal Tumors; Hereditary Breast and Ovarian Cancer Syndrome; Leiomyosarcoma; Leukemia; Liver Neoplasms; Mediastinal Neoplasms; Melanoma; Osteosarcoma; Pancreatic Neoplasms; Penile Neoplasms; Retroviridae Infections; Salivary Gland Neoplasms; Sarcoma, Ewing; Small Cell Lung Carcinoma; Testicular Neoplasms; Thyroid Carcinoma, Anaplastic; Tonsillar Neoplasms; Triple Negative Breast Neoplasms; Urethral Neoplasms; Uterine Neoplasms; Adenocarcinoma of Lung; Anorexia; Cachexia; Carcinoma; Carcinoma, Squamous Cell; Endometrial Neoplasms; Esophageal Neoplasms; Fallopian Tube Neoplasms; Fatigue; Genital Neoplasms, Male; Hypersensitivity; Hypopharyngeal Neoplasms; Inflammatory Breast Neoplasms; Kidney Neoplasms; Laryngeal Neoplasms; Lung Neoplasms; Mouth Neoplasms; Nasopharyngeal Carcinoma; Nasopharyngeal Neoplasms; Neoplasm Metastasis; Neutropenia; Oropharyngeal Neoplasms; Ovarian Neoplasms; Paranasal Sinus Neoplasms; Peritoneal Neoplasms; Pharyngeal Neoplasms; Prostatic Neoplasms, Castration-Resistant; Sarcoma; Squamous Cell Carcinoma of Head and Neck; Urinary Bladder Neoplasms; Urogenital Neoplasms; Uterine Cervical Neoplasms; Adenocarcinoma; Breast Neoplasms; Carcinoma, Non-Small-Cell Lung; Head and Neck Neoplasms; Neoplasms; Prostatic Neoplasms; Stomach Neoplasms
Tubulin inhibitor
Protein
Approved
Unknown
INTRAVENOUS; SUBCUTANEOUS
Diabetes Mellitus, Type 1; Diabetes Mellitus, Type 2; Hyperglycemia; Diabetes Mellitus
Insulin receptor agonist
Unknown
Approved
OTHER
TOPICAL
Unknown
Unknown
Small molecule
Approved
Unknown
ORAL
Hepatitis C, Chronic; Infertility, Male; Hepatitis C; Hyperoxaluria, Primary; Non-alcoholic Fatty Liver Disease; Obesity; Syringomyelia; Xerostomia; Depressive Disorder; Homocystinuria
Betaine-homocysteine S-methyltransferase substrate
Small molecule
Approved
Unknown
Unknown
Conjunctivitis, Allergic; Rhinitis, Allergic, Perennial; Rhinitis, Allergic, Seasonal; Eye Manifestations; Nasal Obstruction
Unknown
Enzyme
Approved
Unknown
Unknown
Borderline Personality Disorder; Diarrhea; Malnutrition
Starch hydrolytic enzyme
Small molecule
Approved
EYE; IMMUNE SYSTEM; OTHER
INJECTION
Condylomata Acuminata; Herpes Simplex; HIV Infections; Kidney Diseases; Uterine Cervical Neoplasms; Infections; Papilloma; Sarcoma; Uterine Cervical Dysplasia; Anus Neoplasms; Cytomegalovirus Infections; Cytomegalovirus Retinitis; Primary Immunodeficiency Diseases; Virus Diseases
Human herpesvirus 1 DNA polymerase inhibitor
Enzyme
Approved
OTHER
SINGLE-USE; UNKNOWN
Hematologic Neoplasms; Retinal Vein Occlusion; Thrombophlebitis; Abdominal Abscess; Arterial Occlusive Diseases; Bronchitis; Infections; Macular Degeneration; Neoplasms; Nervous System Diseases; Respiratory Insufficiency; Retinal Hemorrhage; Severe Acute Respiratory Syndrome; Urinary Retention; Venous Thrombosis; Abscess; Angina, Stable; Brain Ischemia; Cardiovascular Diseases; Cerebral Hemorrhage; Cerebral Infarction; Coronary Disease; Empyema; Empyema, Pleural; Hemorrhage; Ischemic Stroke; Myocardial Ischemia; Respiratory Distress Syndrome; Retinal Artery Occlusion; Subarachnoid Hemorrhage; Eye Diseases; Heart Failure; Myocardial Infarction; Pulmonary Embolism; Stroke; Thrombosis
Tissue-type plasminogen activator exogenous protein
Enzyme
Approved
CARDIOVASCULAR
UNKNOWN
Ischemic Stroke; Stroke; Heart Failure; Myocardial Infarction; ST Elevation Myocardial Infarction; Thrombosis
Tissue-type plasminogen activator exogenous protein
Small molecule
Approved
OTHER
INJECTION
Brain Neoplasms; Diffuse Intrinsic Pontine Glioma; Leukemia; Leukemia, Myeloid, Acute; Lymphoma, T-Cell, Cutaneous; Sarcoma, Synovial; Stomach Neoplasms; Adenocarcinoma; Adenocarcinoma of Lung; Anxiety; Bile Duct Neoplasms; Biliary Tract Diseases; Bone Neoplasms; Carcinoma, Large Cell; Carcinoma, Ovarian Epithelial; Carcinoma, Renal Cell; Colonic Neoplasms; Colorectal Neoplasms; Digestive System Diseases; Endometrial Neoplasms; Esophageal Neoplasms; Esthesioneuroblastoma, Olfactory; Gastrointestinal Stromal Tumors; Glioma; Head and Neck Neoplasms; Kidney Neoplasms; Leiomyosarcoma; Leukemia-Lymphoma, Adult T-Cell; Liver Neoplasms; Lymphoma, Large-Cell, Anaplastic; Lymphoma, Mantle-Cell; Lymphoma, T-Cell; Medulloblastoma; Melanoma; Multiple Myeloma; Neoplasms, Germ Cell and Embryonal; Osteosarcoma; Precursor Cell Lymphoblastic Leukemia-Lymphoma; Prostatic Neoplasms, Castration-Resistant; Rectal Neoplasms; Sarcoma, Ewing; Small Cell Lung Carcinoma; Testicular Neoplasms; Thyroid Neoplasms; Urethral Neoplasms; Biliary Tract Neoplasms; Breast Neoplasms; Carcinoma; Carcinoma, Hepatocellular; Carcinoma, Non-Small-Cell Lung; Carcinoma, Pancreatic Ductal; Carcinoma, Squamous Cell; Cholangiocarcinoma; Fallopian Tube Neoplasms; Gallbladder Neoplasms; Genital Neoplasms, Female; Granuloma, Lethal Midline; Hepatoblastoma; Hernia; Hernia, Ventral; Hodgkin Disease; Immunoblastic Lymphadenopathy; Lung Neoplasms; Lymphoma; Lymphoma, Follicular; Lymphoma, Large B-Cell, Diffuse; Lymphoma, Non-Hodgkin; Lymphoma, T-Cell, Peripheral; Mesothelioma; Nasopharyngeal Carcinoma; Nasopharyngeal Neoplasms; Neoplasm Metastasis; Ovarian Neoplasms; Pancreatic Neoplasms; Peritoneal Neoplasms; Sarcoma; Triple Negative Breast Neoplasms; Urinary Bladder Neoplasms; Urogenital Neoplasms; Uterine Cervical Neoplasms; Neoplasms
Unknown
Small molecule
Approved
DERMATOLOGY; OTHER
TOPICAL
Skin Diseases; Molluscum Contagiosum; Acne Vulgaris
Retinoic acid receptor agonist
Small molecule
Approved
IMMUNE SYSTEM
ORAL
Intestinal Diseases; Hookworm Infections; Onchocerciasis, Ocular; Severe Acute Respiratory Syndrome; Trichuriasis; Ectoparasitic Infestations; Elephantiasis, Filarial; Filariasis; HIV Infections; Malaria; Malnutrition; Onchocerciasis; Strongyloidiasis; Toxocariasis; Helminthiasis; Infections; Neurocysticercosis
Tubulin inhibitor
Unknown
Approved
CANCER
ORAL
Unknown
Unknown
Unknown
Approved
DERMATOLOGY; IMMUNE SYSTEM; OTHER; PEDIATRICS
ORAL; TOPICAL
Alcoholism; Infections; Leishmaniasis; Triple Negative Breast Neoplasms; Acne Vulgaris; Anosmia; Dengue; Dermatitis, Atopic; Onchocerciasis, Ocular; Severe Dengue; Trichuriasis; Blepharitis; Elephantiasis, Filarial; Influenza, Human; Malaria; Pneumonia; Severe Acute Respiratory Syndrome; Helminthiasis; Lice Infestations; Onchocerciasis; Rosacea; Strongyloidiasis
Glutamate-gated chloride channel modulator
Protein
Approved
NEUROLOGY DRUGS & NERVOUS SYSTEM; OTHER
UNKNOWN
Stroke; Alzheimer Disease; Asthma; Colitis, Ulcerative; Crohn Disease; Multiple Organ Failure; Polyradiculoneuropathy, Chronic Inflammatory Demyelinating; Pulmonary Disease, Chronic Obstructive; Hepatitis C; Influenza, Human; Multiple Sclerosis, Relapsing-Remitting; Pneumonia; Respiratory Distress Syndrome; Severe Acute Respiratory Syndrome; Multiple Sclerosis; Neoplasms
Interferon alpha/beta receptor agonist
Small molecule
Approved
Unknown
Unknown
Kidney Diseases; Osteomyelitis; Communicable Diseases; Hematologic Neoplasms; Enterobacteriaceae Infections; Pneumonia, Ventilator-Associated; Pyelonephritis; Shock, Septic; Urinary Tract Infections; Bacterial Infections
Unknown
Small molecule
Approved
Unknown
Unknown
Attention Deficit Disorder with Hyperactivity; Narcolepsy
Dopamine transporter releasing agent
Unknown
Approved
OTHER
INJECTION
Unknown
Unknown
Small molecule
Approved
Unknown
Unknown
Astrocytoma; Carcinoma, Renal Cell; Carcinoma, Small Cell; Desmoplastic Small Round Cell Tumor; Fibroma; Fibrosarcoma; Genital Neoplasms, Female; Glioma; Histiocytoma; Liposarcoma, Myxoid; Lymphoma; Melanoma; Meningeal Neoplasms; Meningitis, Aseptic; Myoepithelioma; Neoplasms, Plasma Cell; Oligodendroglioma; Paraganglioma; Rectal Neoplasms; Sarcoma, Clear Cell; Severe Acute Respiratory Syndrome; Triple Negative Breast Neoplasms; Brain Neoplasms; Breast Neoplasms; Carcinoma, Ovarian Epithelial; Central Nervous System Neoplasms; Colonic Neoplasms; Endometrial Neoplasms; Fallopian Tube Neoplasms; Glioblastoma; Gliosarcoma; Leukemia; Leukemia, Myeloid, Acute; Lymphoma, Non-Hodgkin; Mediastinal Neoplasms; Medulloblastoma; Multiple Myeloma; Peritoneal Neoplasms; Rhabdomyosarcoma; Sarcoma; Sarcoma, Ewing; Uterine Neoplasms; Wilms Tumor; Carcinoma, Non-Small-Cell Lung; Ganglioneuroblastoma; Lung Neoplasms; Neoplasms; Neuroblastoma; Ovarian Neoplasms; Precursor Cell Lymphoblastic Leukemia-Lymphoma; Retinoblastoma; Small Cell Lung Carcinoma; Uterine Cervical Neoplasms
Unknown
Small molecule
Approved
Unknown
Unknown
Attention Deficit Disorder with Hyperactivity
Dopamine transporter releasing agent
Small molecule
Approved
Unknown
Unknown
Status Epilepticus; Epilepsy
Unknown
Protein
Approved
Unknown
Unknown
Adenoma
Diagnostic agent
Antibody
Approved
OTHER
UNKNOWN
Unknown
Diagnostic (monoclonal antibody that is labelled with Indium (111In) for imaging)
Small molecule
Approved
Unknown
Unknown
Colorectal Neoplasms; Colorectal Neoplasms, Hereditary Nonpolyposis; Constriction, Pathologic; Endometrial Neoplasms; Epilepsy; Essential Hypertension; Hemorrhagic Fever, Ebola; Leukemia, Myeloid, Acute; Mucocutaneous Lymph Node Syndrome; Multiple Myeloma; Myelodysplastic Syndromes; Obesity; Sleep Wake Disorders; Venous Thromboembolism; Acute Kidney Injury; Anemia, Sickle Cell; Arthritis, Rheumatoid; Asthma; Carcinoma, Renal Cell; Cardiomyopathies; Carotid Artery Diseases; Chagas Disease; Crohn Disease; Depressive Disorder; Diabetes Insipidus; Diabetes Mellitus, Type 1; Glioblastoma; Glomerulosclerosis, Focal Segmental; Heart Failure; Hepatitis C; Hypertension, Pulmonary; Inflammatory Bowel Diseases; Inflammatory Breast Neoplasms; Influenza, Human; Intracranial Aneurysm; Kidney Neoplasms; Leukemia; Liver Cirrhosis; Lymphoma; Lymphoma, Non-Hodgkin; Macular Degeneration; Melanoma; Migraine Disorders; Multiple Sclerosis; Multiple Sclerosis, Relapsing-Remitting; Myocardial Infarction; Nasopharyngeal Carcinoma; Neoplasms; Nephrotic Syndrome; Non-alcoholic Fatty Liver Disease; Osteoarthritis, Knee; Osteonecrosis; Paraplegia; Periodontitis; Purpura, Thrombocytopenic, Idiopathic; Sarcoidosis; Scleroderma, Localized; Sepsis; Sleep Apnea, Obstructive; Stroke; Tuberculosis; Vascular Diseases; Vitiligo; Acute Chest Syndrome; Acute Coronary Syndrome; Alzheimer Disease; Atherosclerosis; Atrial Fibrillation; Bicuspid Aortic Valve Disease; Breast Neoplasms; Cardiomyopathy, Hypertrophic; Cognitive Dysfunction; Coronary Artery Disease; Coronary Disease; Diabetes Mellitus; Diabetes Mellitus, Type 2; Edema, Cardiac; Graves Ophthalmopathy; Hematoma, Subdural, Intracranial; HIV Infections; Hypercholesterolemia; Hyperlipidemia, Familial Combined; Hyperlipidemias; Hyperlipoproteinemia Type II; Hyperlipoproteinemia Type III; Hyperlipoproteinemia Type IV; Hypertension; Hypertriglyceridemia; Ischemic Stroke; Kidney Diseases; Lipid Metabolism Disorders; Lupus Erythematosus, Systemic; Metabolic Syndrome; Necrosis; Pre-Eclampsia; Prostatic Neoplasms; Prostatic Neoplasms, Castration-Resistant; Psoriasis; Renal Insufficiency; Renal Insufficiency, Chronic; Severe Acute Respiratory Syndrome; ST Elevation Myocardial Infarction; Cardiovascular Diseases
Unknown
Small molecule
Approved
Unknown
Unknown
Abdominal Pain; Otitis Media; Colorectal Neoplasms; Diarrhea; Dyspepsia; Infertility
Antifoaming agent
Small molecule
Approved
OTHER
OPHTHALMIC
Alopecia Areata; Meniere Disease; Vitiligo; Glaucoma; Glaucoma, Open-Angle; Hypertension; Ocular Hypertension
Prostanoid FP receptor agonist
Small molecule
Approved
Unknown
Unknown
Unknown
Unknown
Small molecule
Approved
DIABETES DRUGS & ENDOCRINOLOGY; OTHER
ORAL
Diabetes Mellitus, Type 1; Diabetes Mellitus; Diabetes Mellitus, Type 2
Lysosomal alpha-glucosidase inhibitor
Small molecule
Approved
Unknown
Unknown
Rhinitis, Allergic, Perennial; Rhinitis, Allergic, Seasonal; Eye Manifestations; Hypersensitivity; Nasal Obstruction
Unknown