Display Options:
Total: 10647
Small molecule
Approved
NEUROLOGY DRUGS & NERVOUS SYSTEM; OTHER
INTRAVENOUS; ORAL
Aphasia; Canavan Disease; Essential Tremor; Lymphoma, Follicular; Stroke; Alzheimer Disease; Anemia, Sickle Cell; Bipolar Disorder; Brain Neoplasms; Cocaine-Related Disorders; Cognitive Dysfunction; Dyskinesia, Drug-Induced; Epilepsy, Absence; Epilepsy, Reflex; Glioblastoma; Leukemia, Myeloid, Acute; Neuralgia, Postherpetic; Neuroblastoma; Obsessive-Compulsive Disorder; Opioid-Related Disorders; Paraganglioma; Parkinson Disease; Polyneuropathies; Psychotic Disorders; Restless Legs Syndrome; Stress Disorders, Post-Traumatic; Torticollis; Alcoholism; Anxiety; Dementia; Depressive Disorder; Epilepsies, Partial; Movement Disorders; Panic Disorder; Schizophrenia; Status Epilepticus; Subarachnoid Hemorrhage; Substance Withdrawal Syndrome; Epilepsy; Epilepsy, Tonic-Clonic; Seizures
Synaptic vesicle glycoprotein 2A modulator
Small molecule
Approved
HEMATOLOGY
ORAL
Cerebellar Ataxia; Cognitive Dysfunction; HIV Infections; Myocardial Infarction; Amyotrophic Lateral Sclerosis; Friedreich Ataxia; Parkinson Disease; Stroke; Acute Kidney Injury; Hemochromatosis; Pantothenate Kinase-Associated Neurodegeneration; Anemia, Sickle Cell; beta-Thalassemia; Iron Overload; Thalassemia
Unknown
Small molecule
Approved
IMMUNE SYSTEM
TOPICAL
Breast Neoplasms; Lichen Planus; Lupus Erythematosus, Cutaneous; Psoriasis; Hand Dermatoses; Eczema; Neoplasms; Sarcoma, Kaposi
Retinoid receptor agonist
Small molecule
Approved
Unknown
Unknown
Obesity; Renal Insufficiency, Chronic; Infections; Influenza in Birds; Thrombocytopenia; Influenza, Human; Pneumonia; Purpura, Thrombocytopenic, Idiopathic; Severe Acute Respiratory Syndrome; Virus Diseases
Unknown
Small molecule
Approved
OTHER
ORAL
Metabolic Syndrome; Hyperlipoproteinemia Type I; Polycystic Ovary Syndrome; Infertility; Obesity
Gastric lipase inhibitor
Small molecule
Approved
Unknown
Unknown
Acquired Immunodeficiency Syndrome; Acute Coronary Syndrome; Alzheimer Disease; Amyotrophic Lateral Sclerosis; Anemia; Arthritis, Rheumatoid; Asthma; Carcinoma, Renal Cell; Cardiotoxicity; Constipation; Coronary Disease; Cystic Fibrosis; Diabetes Mellitus; Diabetes Mellitus, Type 2; Dyspepsia; Epilepsy; Erectile Dysfunction; Fibromyalgia; Heart Failure; Hepatitis C; HIV Infections; Hypertension; Hypoglycemia; Hypotension, Orthostatic; Immune System Diseases; Lice Infestations; Lipid Metabolism Disorders; Lupus Erythematosus, Systemic; Lymphoma; Malaria, Vivax; Myocardial Ischemia; Nausea; Non-alcoholic Fatty Liver Disease; Obesity; Osteomyelitis; Pain; Phenylketonurias; Postpartum Hemorrhage; Premature Birth; Psychotic Disorders; Respiratory Tract Infections; Restless Legs Syndrome; Schizophrenia; Smoking Cessation; Cholangitis; Corneal Ulcer; Lung Diseases; Muscle Spasticity; Neoplasms; Parkinson Disease; Tuberculosis, Meningeal; Tuberculosis, Multidrug-Resistant; Abscess; Acanthamoeba Keratitis; Breast Neoplasms; Bronchitis, Chronic; Cataract; Cellulitis; Cholecystitis, Acute; Conjunctivitis, Bacterial; Endophthalmitis; Helicobacter Infections; Infections; Inflammation; Influenza, Human; Keratitis; Meningitis; Otitis Media; Pelvic Inflammatory Disease; Pneumonia; Pneumonia, Bacterial; Pulmonary Disease, Chronic Obstructive; Severe Acute Respiratory Syndrome; Sinusitis; Skin Diseases; Tuberculosis; Tuberculosis, Pulmonary; Bacterial Infections; Eye Infections
Unknown
Small molecule
Approved
Unknown
Unknown
Osteomyelitis
Bacterial 70S ribosome inhibitor
Protein
Approved
OTHER
SINGLE-USE
Carcinoma, Ovarian Epithelial; Cystic Fibrosis; Gliosarcoma; Leukemia; Lymphoma, Non-Hodgkin; Neuroblastoma; Osteosarcoma; Prostatic Neoplasms, Castration-Resistant; Psoriasis; Retinal Degeneration; Rhabdomyosarcoma; Sarcoma, Ewing; Uveitis; Uveitis, Anterior; Xerostomia; Arthritis, Reactive; Aspergillosis; Bronchiolitis Obliterans; Fallopian Tube Neoplasms; Friedreich Ataxia; Hepatitis C, Chronic; HIV Infections; Leukocyte-Adhesion Deficiency Syndrome; Liver Cirrhosis; Lung Diseases; Meningitis, Cryptococcal; Mesothelioma; Multiple Myeloma; Mycobacterium avium-intracellulare Infection; Mycobacterium Infections; Mycosis Fungoides; Ovarian Neoplasms; Peritoneal Neoplasms; Sezary Syndrome; Breast Neoplasms; Candidemia; Condylomata Acuminata; Idiopathic Pulmonary Fibrosis; Lymphoma; Melanoma; Pneumonia, Ventilator-Associated; Pulmonary Fibrosis; Granulomatous Disease, Chronic; Neoplasms; Osteopetrosis
Interferon gamma receptor agonist
Small molecule
Approved
Unknown
Unknown
Adenocarcinoma; Carcinoma, Non-Small-Cell Lung; Esophageal Neoplasms; Hodgkin Disease; Lymphoma, Follicular; Lymphoma, Non-Hodgkin; Neoplasms, Germ Cell and Embryonal; Ovarian Neoplasms; Pancreatic Neoplasms; Prostatic Neoplasms, Castration-Resistant; Sepsis; Small Cell Lung Carcinoma; Testicular Neoplasms; Thymoma; Breast Neoplasms; Carcinoma, Hepatocellular; Inflammatory Breast Neoplasms; Lymphoma, Large B-Cell, Diffuse; Lymphoma, T-Cell, Peripheral; Nasopharyngeal Carcinoma; Sarcoma; Stomach Neoplasms; Thrombosis; Triple Negative Breast Neoplasms; Urinary Bladder Neoplasms; Neoplasms
Unknown
Small molecule
Approved
OTHER
INJECTION
Magnetic Resonance Imaging
Diagnostic agent
Small molecule
Approved
Unknown
Unknown
Unknown
Unknown
Unknown
Approved
Unknown
Unknown
Anemia, Iron-Deficiency; Anemia
Supplement
Small molecule
Approved
Unknown
Unknown
Alzheimer Disease; Atrial Fibrillation; Brain Ischemia; Chronic Pain; Cocaine-Related Disorders; Cognitive Dysfunction; Cough; Epilepsy; Heart Diseases; Hernia, Inguinal; Hypotension; Nasal Polyps; Neuralgia; Neural Tube Defects; Postoperative Complications; Radius Fractures; Renal Insufficiency; Scoliosis; Tobacco Use Disorder; Vascular Diseases; Acute Kidney Injury; Amyotrophic Lateral Sclerosis; Brain Neoplasms; Burns; Child Development Disorders, Pervasive; Coronary Disease; Dental Anxiety; Dysautonomia, Familial; Hernias, Diaphragmatic, Congenital; Hypertension, Pulmonary; Hypertrophy; Mental Disorders; Pheochromocytoma; Pre-Eclampsia; Pregnancy; Shoulder Pain; Temporomandibular Joint Disorders; Anxiety; Brain Diseases; Brain Injuries; Breast Neoplasms; Cleft Palate; Colorectal Neoplasms; Delirium; Fractures, Bone; Headache; Heart Septal Defects, Atrial; Hypertension; Inflammation; Lung Diseases; Neoplasms; Obesity; Obesity, Morbid; Opioid-Related Disorders; Pain; Pharyngitis; Postoperative Nausea and Vomiting; Psychomotor Agitation; Rectal Diseases; Respiratory Insufficiency; Retinopathy of Prematurity; Rib Fractures; Shock, Septic; Sleep Apnea, Obstructive; Sleep Initiation and Maintenance Disorders; Stomach Neoplasms; Subarachnoid Hemorrhage; Tremor; Wounds and Injuries
Unknown
Protein
Approved
Unknown
Unknown
Unknown
Diagnostic agent
Small molecule
Approved
Unknown
Unknown
Pain; Pregnancy
Sodium channel protein type IV alpha subunit blocker
Unknown
Approved
Unknown
Unknown
Hypoplastic Left Heart Syndrome; Severe Acute Respiratory Syndrome; Respiratory Distress Syndrome; Respiratory Distress Syndrome, Newborn
Surfactant agent
Small molecule
Approved
Unknown
Unknown
Acne Vulgaris; Astrocytoma; Colonic Neoplasms; Colorectal Neoplasms; Crohn Disease; Dermatitis, Seborrheic; Glioma; Gliosarcoma; Oligodendroglioma; Sarcoma; Basal Cell Nevus Syndrome; Brain Neoplasms; Carcinoma, Basal Cell; Desmoid Tumors; Glioblastoma; Neurofibromatosis 1; Infections; Keratosis, Actinic; Paraganglioma; Neoplasms
Unknown
Small molecule
Approved
IMMUNE SYSTEM
INHALATION
Dengue; Diabetes Mellitus, Type 2; Infections; Influenza, Human; Virus Diseases
Neuraminidase inhibitor
Small molecule
Approved
OTHER; PHARMACOLOGY
INJECTION
Unknown
Muscle-type nicotinic acetylcholine receptor antagonist
Small molecule
Approved
Unknown
Unknown
Unknown
Tyrosinase inhibitor
Small molecule
Approved
Unknown
Unknown
Abdominal Pain; Cleft Palate; Postoperative Complications; Back Pain; Neoplasms; Pain; Pregnancy
Unknown
Small molecule
Approved
NEUROLOGY DRUGS & NERVOUS SYSTEM; OTHER
ORAL
Sleep Wake Disorders; Anxiety; Dementia; Depressive Disorder; Schizophrenia; Sleep Initiation and Maintenance Disorders
GABA A receptor alpha-1/beta-1/gamma-2 positive allosteric modulator
Small molecule
Approved
Unknown
Unknown
Anemia; Astrocytoma; Brain Neoplasms; Crohn Disease; Cystic Fibrosis; Diabetes Mellitus, Type 1; Gastroparesis; Glioblastoma; Granulomatous Disease, Chronic; Inflammation; Lupus Erythematosus, Systemic; Melanoma; Meningioma; Multiple Myeloma; Multiple Sclerosis; Multiple Sclerosis, Relapsing-Remitting; Neoplasms; Peripheral Arterial Disease; Prostatic Neoplasms; Pulmonary Alveolar Proteinosis; Adrenoleukodystrophy; Alcoholism; Alzheimer Disease; Amyotrophic Lateral Sclerosis; Asthma; Carcinoma, Non-Small-Cell Lung; Carcinoma, Squamous Cell; Cardiovascular Diseases; Cerebral Hemorrhage; Child Development Disorders, Pervasive; Cognitive Dysfunction; Depressive Disorder, Major; Glucose Intolerance; Hepatitis; Hepatitis C; Hepatitis C, Chronic; Hypertension, Pulmonary; Infections; Leukemia, Myelogenous, Chronic, BCR-ABL Positive; Leukemia, Myeloid, Acute; Leukoplakia, Oral; Liposarcoma; Liposarcoma, Myxoid; Lung Neoplasms; Obesity; Opioid-Related Disorders; Pancreatic Neoplasms; Parkinson Disease; Polycystic Kidney Diseases; Polycystic Ovary Syndrome; Prostatic Neoplasms, Castration-Resistant; Psoriasis; Renal Insufficiency, Chronic; Stroke; Thyroid Neoplasms; Arthritis, Rheumatoid; Atherosclerosis; Coronary Disease; Diabetes Mellitus, Type 2; Fatty Liver; Friedreich Ataxia; HIV-Associated Lipodystrophy Syndrome; HIV Infections; Hypercholesterolemia; Hypertension; Insulin Resistance; Liver Diseases; Metabolic Syndrome; Non-alcoholic Fatty Liver Disease; Diabetes Mellitus
Unknown
Small molecule
Approved
OTHER
ORAL
CADASIL; Fatty Liver; Osteoarthritis; Pain; Cerebral Small Vessel Diseases; Cognitive Dysfunction; Heart Failure; Intermittent Claudication; Stroke; Urticaria; Wounds and Injuries; Arthritis, Rheumatoid; Atherosclerosis; Cardiovascular Diseases; Cerebral Infarction; Cerebrovascular Disorders; Coronary Disease; Ischemic Stroke; Peripheral Arterial Disease; Peripheral Vascular Diseases; Thrombosis
Phosphodiesterase 3A inhibitor
Small molecule
Approved
CANCER; OTHER
INTRAVENOUS; ORAL
Cytomegalovirus Infections; Desmoplastic Small Round Cell Tumor; Ependymoma; Fallopian Tube Neoplasms; Meningitis, Aseptic; Prostatic Neoplasms; Prostatic Neoplasms, Castration-Resistant; Wilms Tumor; Biliary Tract Neoplasms; Brain Diseases; Brain Stem Neoplasms; Breast Neoplasms; Carcinoid Tumor; Carcinoma, Hepatocellular; Carcinoma, Islet Cell; Carcinoma, Neuroendocrine; Colorectal Neoplasms; Gastrointestinal Stromal Tumors; Hereditary Breast and Ovarian Cancer Syndrome; Leiomyosarcoma; Leukemia; Leukemia, Myeloid, Acute; Lung Neoplasms; Lymphoma; Lymphoma, Non-Hodgkin; Medulloblastoma; Myelodysplastic Syndromes; Neuroectodermal Tumors, Primitive, Peripheral; Neuroendocrine Tumors; Neurofibromatosis 1; Ovarian Neoplasms; Pancreatic Neoplasms; Pheochromocytoma; Pinealoma; Pituitary Neoplasms; Rectal Neoplasms; Retinoblastoma; Rhabdomyosarcoma; Rhabdomyosarcoma, Alveolar; Rhabdomyosarcoma, Embryonal; Sarcoma; Skin Neoplasms; Small Cell Lung Carcinoma; Spinal Cord Neoplasms; Uveal Melanoma; Astrocytoma; Brain Neoplasms; Carcinoma, Non-Small-Cell Lung; Central Nervous System Neoplasms; Choroid Plexus Neoplasms; Diffuse Intrinsic Pontine Glioma; Ganglioneuroblastoma; Gliosarcoma; Melanoma; Neoplasm Metastasis; Neuroblastoma; Oligodendroglioma; Optic Nerve Glioma; Paraganglioma; Sarcoma, Ewing; Glioblastoma; Glioma; Neoplasms
DNA inhibitor
Small molecule
Approved
Unknown
Unknown
Contracture; Peanut Hypersensitivity; Conjunctivitis, Allergic; Dyspepsia; Fibromyalgia; Peripheral Nervous System Diseases; Rhinitis, Allergic, Perennial; Severe Acute Respiratory Syndrome; Eye Manifestations; Hypersensitivity
Unknown
Small molecule
Approved
IMMUNE SYSTEM; OTHER; UROLOGY AND KIDNEY
ORAL
Acute Lung Injury; Adenocarcinoma of Lung; Alcoholism; Alzheimer Disease; Carcinoma, Non-Small-Cell Lung; Carcinoma, Squamous Cell; Central Nervous System Neoplasms; Desmoid Tumors; Diabetic Retinopathy; Eosinophilic Esophagitis; Fallopian Tube Neoplasms; Frontotemporal Dementia; Gangliosidoses; Gaucher Disease; Glioma; Glycogen Storage Disease Type II; Granulomatous Disease, Chronic; Heart Failure; Hematologic Neoplasms; HIV Infections; Hypercholesterolemia; Hyperinsulinism; Hypertension, Pulmonary; Kidney Diseases; Leiomyosarcoma; Leukemia, Lymphoid; Leukemia, Myelogenous, Chronic, BCR-ABL Positive; Leukemia, Plasma Cell; Lung Neoplasms; Multiple Sclerosis, Relapsing-Remitting; Neoplasms, Plasma Cell; Neurilemmoma; Panuveitis; Parkinson Disease; Pemphigus; Port-Wine Stain; Primary Immunodeficiency Diseases; Prostatic Neoplasms; Rectal Neoplasms; Respiratory Distress Syndrome; Respiratory Insufficiency; Sarcopenia; Scleritis; Sjogren's Syndrome; Small Cell Lung Carcinoma; Thalassemia; Uveitis, Anterior; Adenomatous Polyposis Coli; Aging; Amyotrophic Lateral Sclerosis; Anemia; Anemia, Aplastic; Anemia, Hemolytic, Autoimmune; Anemia, Sickle Cell; beta-Thalassemia; Blood Platelet Disorders; Bronchiolitis Obliterans Syndrome; Bronchitis; Carcinoma, Renal Cell; Castleman Disease; Choroidal Neovascularization; Depressive Disorder; Dry Eye Syndromes; Fanconi Anemia; Geographic Atrophy; Glioblastoma; Gliosarcoma; Glomerulonephritis, IGA; Glomerulosclerosis, Focal Segmental; Graves Ophthalmopathy; Hemangioendothelioma; Hematologic Diseases; Hemorrhage; Hypertension; Immunologic Deficiency Syndromes; Intracranial Aneurysm; Intracranial Arteriovenous Malformations; Leukemia; Leukemia, Lymphocytic, Chronic, B-Cell; Leukemia, Myeloid, Acute; Liver Diseases; Liver Neoplasms; Lupus Erythematosus, Systemic; Lupus Nephritis; Lymphoma; Lymphoma, Large B-Cell, Diffuse; Lymphoma, Mantle-Cell; Lymphoma, T-Cell, Cutaneous; Macular Degeneration; Multiple Myeloma; Multiple System Atrophy; Myelodysplastic Syndromes; Neoplasm Metastasis; Neoplasms, Germ Cell and Embryonal; Neuroblastoma; Neurofibromatosis 1; Osteosarcoma; Ovarian Neoplasms; Pancreatic Neoplasms; Paraganglioma; Perivascular Epithelioid Cell Neoplasms; Pinealoma; Polycystic Kidney Diseases; Precursor Cell Lymphoblastic Leukemia-Lymphoma; Prostatic Neoplasms, Castration-Resistant; Renal Insufficiency; Retroperitoneal Fibrosis; Sarcoidosis; Sarcoma; Scleroderma, Systemic; Severe Acute Respiratory Syndrome; Severe Combined Immunodeficiency; Sturge-Weber Syndrome; Thyroid Neoplasms; Uveitis, Intermediate; Uveitis, Posterior; Vascular Malformations; Vitiligo; Birt-Hogg-Dube Syndrome; Breast Neoplasms; Carcinoma, Hepatocellular; Cardiovascular Abnormalities; Diabetes Mellitus, Type 1; Diabetic Nephropathies; Fibroma; Graft vs Host Disease; Hodgkin Disease; Influenza, Human; Kidney Failure, Chronic; Lichen Planus, Oral; Lymphangioleiomyomatosis; Lymphedema; Lymphoma, Non-Hodgkin; Myositis, Inclusion Body; Neurofibromatoses; Pachyonychia Congenita; Polycystic Kidney, Autosomal Dominant; Renal Insufficiency, Chronic; Skin Neoplasms; Urinary Bladder Neoplasms; Angiofibroma; Delayed Graft Function; Eye Diseases; Kidney Transplantation; Neoplasms; Tuberous Sclerosis
FK506-binding protein 1A inhibitor
Small molecule
Approved
Unknown
Unknown
Asthma; Pulmonary Disease, Chronic Obstructive
Unknown
Small molecule
Approved
EYE; OTHER
OPHTHALMIC
Chronic Pain; Conjunctivitis, Allergic; Dermatitis; Fractures, Bone; Rhinitis, Allergic, Perennial
Histamine H1 receptor antagonist
Small molecule
Approved
Unknown
Unknown
Unknown
Unknown
Small molecule
Approved
Unknown
Unknown
Adrenoleukodystrophy; Anemia, Sickle Cell; Barrett Esophagus; Burns; Carcinoma in Situ; Carcinoma, Intraductal, Noninfiltrating; Gingivitis; Glioblastoma; Hyperlipidemias; Irritable Bowel Syndrome; Nasal Obstruction; Pneumonia; Primary Immunodeficiency Diseases; Skin Diseases; Skin Neoplasms; Tibial Fractures; Acquired Immunodeficiency Syndrome; Aging; Autistic Disorder; Bronchiolitis; Colonic Neoplasms; Common Cold; Conjunctivitis, Allergic; Depressive Disorder; Dermatitis, Atopic; Diabetes Mellitus; Glucose Intolerance; Hematologic Neoplasms; Hereditary Breast and Ovarian Cancer Syndrome; Hypersensitivity; Infertility, Male; Keratosis, Actinic; Leukemia, Myeloid, Acute; Malnutrition; Metabolic Syndrome; Multiple Sclerosis; Neoplasms; Neurofibromatosis 1; Optic Neuritis; Ovarian Neoplasms; Parkinson Disease; Prediabetic State; Psoriasis; Psychotic Disorders; Pulmonary Disease, Chronic Obstructive; Rectal Neoplasms; Respiratory Insufficiency; Staphylococcal Infections; Urinary Tract Infections; Adenoma; Arthritis, Juvenile; Asthma; Bone Diseases, Metabolic; Breast Neoplasms; Cardiovascular Diseases; Cognitive Dysfunction; Colitis, Ulcerative; Colorectal Neoplasms; Crohn Disease; Diabetes, Gestational; Diabetes Mellitus, Type 1; Diabetes Mellitus, Type 2; Epilepsy; Fractures, Bone; Heart Failure; Helicobacter Infections; Hepatitis C; Hip Fractures; HIV Infections; Hyperparathyroidism; Hypogonadism; Infections; Inflammatory Bowel Diseases; Influenza, Human; Leukemia, Lymphocytic, Chronic, B-Cell; Lipid Metabolism Disorders; Lupus Erythematosus, Systemic; Lymphoma, Large B-Cell, Diffuse; Melanoma; Multiple Sclerosis, Relapsing-Remitting; Non-alcoholic Fatty Liver Disease; Obesity; Osteoporosis, Postmenopausal; Polycystic Ovary Syndrome; Pregnancy; Prostatic Neoplasms; Prostatic Neoplasms, Castration-Resistant; Renal Insufficiency, Chronic; Schizophrenia; Severe Acute Respiratory Syndrome; Tuberculosis; Tuberculosis, Pulmonary; Urticaria; Vitamin D Deficiency; Anemia; Anemia, Iron-Deficiency; Osteoporosis
Vitamin D receptor agonist
Small molecule
Approved
Unknown
Unknown
Aortic Aneurysm, Abdominal; Asthma; Muscular Dystrophy, Duchenne
Unknown
Small molecule
Approved
OTHER; RESPIRATORY
ORAL
Romano-Ward Syndrome; Heart Failure; Arrhythmias, Cardiac; Atrial Fibrillation; Atrial Flutter
HERG blocker
Small molecule
Approved
Unknown
Unknown
Amyotrophic Lateral Sclerosis; Cholangiocarcinoma; Communicable Diseases; Hematologic Neoplasms; Lymphoma; Neoplasms; Dyspepsia; Duodenal Ulcer; Gastrointestinal Hemorrhage; Helicobacter Infections; Gastroesophageal Reflux; Peptic Ulcer
Unknown
Small molecule
Approved
DIABETES DRUGS & ENDOCRINOLOGY; OTHER
ORAL
HIV Infections; Central Nervous System Neoplasms; Head and Neck Neoplasms; Heart Failure; Leukoplakia, Oral; Non-alcoholic Fatty Liver Disease; Pituitary ACTH Hypersecretion; Sarcoma; Atherosclerosis; Insulin Resistance; Diabetes Mellitus; Diabetes Mellitus, Type 2
Peroxisome proliferator-activated receptor gamma agonist