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Total: 10647
Unknown
Approved
Unknown
Unknown
Unknown
Unknown
Enzyme
Approved
Unknown
Unknown
Leukemia, Lymphoid; Neoplasms; Leukemia, Biphenotypic, Acute; Myelodysplastic Syndromes; Leukemia; Leukemia, Myeloid, Acute; Precursor Cell Lymphoblastic Leukemia-Lymphoma
Asparagine hydrolytic enzyme
Small molecule
Approved
OTHER
ORAL
Adenocarcinoma; Carcinoma; Central Nervous System Neoplasms; Diffuse Intrinsic Pontine Glioma; Esophageal Neoplasms; Glioma; Neuroblastoma; Paraganglioma; Pheochromocytoma; Rectal Neoplasms; Adenocarcinoma, Follicular; Astrocytoma; Breast Neoplasms; Carcinoma, Hepatocellular; Carcinoma, Renal Cell; Carcinoma, Squamous Cell; Colorectal Neoplasms; Fallopian Tube Neoplasms; Gastrointestinal Stromal Tumors; Glioblastoma; Gliosarcoma; Head and Neck Neoplasms; Kidney Neoplasms; Leukemia, Myeloid, Acute; Mesothelioma; Multiple Myeloma; Neoplasm Metastasis; Oligodendroglioma; Ovarian Neoplasms; Pancreatic Neoplasms; Peritoneal Neoplasms; Prostatic Neoplasms; Prostatic Neoplasms, Castration-Resistant; Small Cell Lung Carcinoma; Stomach Neoplasms; Ureteral Neoplasms; Urethral Neoplasms; Urinary Bladder Neoplasms; Carcinoma, Non-Small-Cell Lung; Lung Neoplasms; Carcinoma, Medullary; Neoplasms; Thyroid Neoplasms
Ephrin receptor inhibitor
Unknown
Approved
Unknown
Unknown
Unknown
Unknown
Small molecule
Approved
Unknown
Unknown
Cardiovascular Diseases; Hyperlipoproteinemia Type II
Unknown
Antibody
Approved
OTHER
IV (INFUSION)
Anthrax
Protective antigen binding agent
Small molecule
Approved
CARDIOVASCULAR
ORAL
Breast Neoplasms; Lipid Metabolism Disorders; Adenoma; Alzheimer Disease; Colonic Neoplasms; Non-alcoholic Fatty Liver Disease; Cardiovascular Diseases; Severe Acute Respiratory Syndrome; Dyslipidemias; Hypertriglyceridemia; Pancreatitis
Unknown
Small molecule
Approved
EYE
OPHTHALMIC
Glaucoma; Glaucoma, Open-Angle; Ocular Hypertension
Prostanoid FP receptor agonist
Small molecule
Approved
GASTROINTESTINAL; OTHER; UROLOGY AND KIDNEY
ORAL
Bone Neoplasms; Leukemia, Myeloid, Acute; Myelodysplastic Syndromes; Rhabdomyosarcoma; Small Cell Lung Carcinoma; Bile Duct Neoplasms; Biliary Tract Neoplasms; Carcinoma, Adenoid Cystic; Carcinoma, Renal Cell; Cholangiocarcinoma; Digestive System Neoplasms; Fallopian Tube Neoplasms; Glioblastoma; Hemangiosarcoma; Liposarcoma; Macular Degeneration; Melanoma; Meningioma; Osteosarcoma; Ovarian Neoplasms; Pancreatic Neoplasms; Pulmonary Disease, Chronic Obstructive; Rectal Neoplasms; Sarcoma; Stomach Neoplasms; Thyroid Neoplasms; Carcinoma, Hepatocellular; Colonic Neoplasms; Esophageal Neoplasms; Gastrointestinal Stromal Tumors; Colorectal Neoplasms; Neoplasms
Discoidin domain-containing receptor 2 inhibitor
Small molecule
Approved
MUSCULOSKELETAL; OTHER
ORAL
Celiac Disease; Kidney Diseases; Paraparesis, Tropical Spastic; Purpura, Thrombocytopenic, Idiopathic; Multiple Sclerosis, Chronic Progressive; Multiple Sclerosis; Multiple Sclerosis, Relapsing-Remitting
Dihydroorotate dehydrogenase inhibitor
Unknown
Approved
Unknown
Unknown
Unknown
Unknown
Small molecule
Approved
NEUROLOGY DRUGS & NERVOUS SYSTEM; OTHER; PEDIATRICS
ORAL
Alcoholism; Bipolar Disorder; Depressive Disorder, Major; Torticollis; Amyotrophic Lateral Sclerosis; Diabetic Neuropathies; Essential Tremor; Migraine Disorders; Neuralgia; Small Fiber Neuropathy; Epilepsy, Tonic-Clonic; Lennox Gastaut Syndrome; Parkinson Disease; Epilepsies, Partial; Epilepsy; Seizures
Glutamate receptor ionotropic AMPA antagonist
Small molecule
Approved
Unknown
Unknown
Multiple Sclerosis; Glioblastoma; Alzheimer Disease; Cognitive Dysfunction; Radionuclide Imaging
Diagnostic agent
Protein
Approved
Unknown
Unknown
Carcinoma, Intraductal, Noninfiltrating; Carcinoma, Merkel Cell; Digestive System Neoplasms; Kidney Diseases; Prostatic Neoplasms; ACTH Syndrome, Ectopic; Adenoma; Adenoma, Islet Cell; Breast Neoplasms; Carcinoma, Hepatocellular; Carcinoma, Medullary; Cushing Syndrome; Dumping Syndrome; Hematologic Neoplasms; Hyperglycemia; Lung Neoplasms; Meningioma; Multiple Myeloma; Neoplasms; Neuroendocrine Tumors; Pain; Pituitary Neoplasms; Postoperative Complications; Prostatic Neoplasms, Castration-Resistant; Small Cell Lung Carcinoma; Thymoma; Thyroid Neoplasms; Uveal Melanoma; Acromegaly; Carcinoid Tumor; Pancreatic Neoplasms; Pituitary ACTH Hypersecretion
Unknown
Small molecule
Approved
Unknown
Unknown
Carcinoma, Squamous Cell; Gliosarcoma; Leukemia, Myeloid, Acute; Liver Diseases; Multiple Myeloma; Urogenital Neoplasms; Adenocarcinoma, Follicular; Adrenal Cortex Neoplasms; Astrocytoma; Bile Duct Neoplasms; Breast Neoplasms; Carcinoid Tumor; Carcinoma; Carcinoma, Neuroendocrine; Cholangiocarcinoma; Colorectal Neoplasms; Gastrointestinal Stromal Tumors; Glioblastoma; Kidney Neoplasms; Liver Neoplasms; Lung Neoplasms; Melanoma; Meningioma; Neuroendocrine Tumors; Osteosarcoma; Pancreatic Neoplasms; Prostatic Neoplasms; Prostatic Neoplasms, Castration-Resistant; Pulmonary Disease, Chronic Obstructive; Rectal Neoplasms; Retroviridae Infections; Salivary Gland Neoplasms; Sarcoma; Urinary Bladder Neoplasms; Uterine Cervical Neoplasms; Carcinoma, Hepatocellular; Carcinoma, Medullary; Carcinoma, Non-Small-Cell Lung; Carcinoma, Renal Cell; Thyroid Neoplasms; Neoplasms
Unknown
Small molecule
Approved
Unknown
ORAL
Dermatomyositis; Granuloma Annulare; Granulomatous Disease, Chronic; Kidney Diseases; Lupus Erythematosus, Cutaneous; Lupus Erythematosus, Systemic; Myasthenia Gravis; Renal Insufficiency, Chronic; Sarcoidosis; Stevens-Johnson Syndrome; Alopecia Areata; Colitis; Crohn Disease; Down Syndrome; Dry Eye Syndromes; Granuloma, Lethal Midline; Leishmaniasis, Cutaneous; Myocarditis; Myositis; Pneumonia; Pouchitis; Scleroderma, Systemic; Sjogren's Syndrome; Wounds and Injuries; Arthritis, Juvenile; Arthritis, Psoriatic; Arthritis, Rheumatoid; Colitis, Ulcerative; Glioblastoma; Polymyalgia Rheumatica; Psoriasis; Severe Acute Respiratory Syndrome; Spondylitis, Ankylosing; Takayasu Arteritis
Unknown
Small molecule
Approved
OTHER; UROLOGY AND KIDNEY
ORAL
Esophageal Achalasia; Kidney Diseases; Liver Diseases; Polycystic Ovary Syndrome; Cerebral Hemorrhage; Heart Failure; Hypertrophy, Left Ventricular; Pain; Prediabetic State; Urinary Bladder, Neurogenic; Cystitis, Interstitial; Kidney Calculi; Polyuria; Urinary Bladder, Overactive; Urinary Incontinence; Urinary Incontinence, Urge
Beta-3 adrenergic receptor agonist
Protein
Approved
GASTROINTESTINAL; OTHER
ORAL
Adenoma; Colorectal Neoplasms; Constipation; Irritable Bowel Syndrome
Heat-stable enterotoxin receptor agonist
Small molecule
Approved
GASTROINTESTINAL
ORAL
Breast Neoplasms; Irritable Bowel Syndrome; Diarrhea
Anoctamin-1 blocker
Small molecule
Approved
Unknown
Unknown
Myelodysplastic Syndromes; Adenocarcinoma of Lung; Blast Crisis; Carcinoma, Medullary; Carcinoma, Non-Small-Cell Lung; Gastrointestinal Stromal Tumors; Glioblastoma; Leukemia; Leukemia, Myeloid, Acute; Small Cell Lung Carcinoma; Thyroid Neoplasms; Leukemia, Myelogenous, Chronic, BCR-ABL Positive; Neoplasms; Precursor Cell Lymphoblastic Leukemia-Lymphoma
Unknown
Enzyme
Approved
Unknown
Unknown
Hematologic Neoplasms; Lymphoma; Neoplasms; Osteosarcoma; Precursor Cell Lymphoblastic Leukemia-Lymphoma; Metabolic Side Effects of Drugs and Substances
Methotrexate hydrolytic enzyme
Unknown
Approved
PEDIATRICS
INTRATRACHEAL
Cystic Fibrosis; Respiratory Distress Syndrome; Respiratory Distress Syndrome, Newborn; Respiratory Insufficiency; Meconium Aspiration Syndrome
Surfactant agent
Small molecule
Approved
RESPIRATORY
ORAL
Tuberculosis; Tuberculosis, Multidrug-Resistant
ATP synthase inhibitor
Unknown
Approved
Unknown
Unknown
Unknown
Unknown
Small molecule
Approved
Unknown
Unknown
Blood Coagulation Disorders; Ischemic Stroke; Nephrotic Syndrome; Thromboembolism; Foramen Ovale, Patent; Heart Failure; Hemorrhage; Liver Cirrhosis; Renal Insufficiency, Chronic; Acute Coronary Syndrome; Anemia, Sickle Cell; Aortic Valve Stenosis; Atrial Flutter; Hematoma; Ischemia; Neoplasms; Precursor Cell Lymphoblastic Leukemia-Lymphoma; Renal Insufficiency; Severe Acute Respiratory Syndrome; Arthroplasty; Atrial Fibrillation; Embolism; Pulmonary Embolism; Stroke; Thrombosis; Venous Thromboembolism; Venous Thrombosis
Coagulation factor X inhibitor
Small molecule
Approved
CANCER
ORAL
Carcinoma, Renal Cell; Kidney Diseases; Liver Diseases; Pancreatic Neoplasms; Adenocarcinoma; Carcinoma; Carcinoma, Hepatocellular; Endometrial Neoplasms; Lymphoma, Mantle-Cell; Ovarian Neoplasms; Severe Acute Respiratory Syndrome; Triple Negative Breast Neoplasms; Urinary Bladder Neoplasms; Uterine Neoplasms; Breast Neoplasms; Neoplasms; Prostatic Neoplasms
Androgen Receptor antagonist
Small molecule
Approved
Unknown
Unknown
Liver Diseases; Lung Diseases; Mycobacterium avium-intracellulare Infection; Leprosy; Tuberculosis, Multidrug-Resistant; Tuberculosis, Pulmonary; Tuberculosis
Unknown
Enzyme
Approved
HEMATOLOGY
INTRAVENOUS
Gaucher Disease
Glucocerebroside hydrolytic enzyme
Small molecule
Approved
Unknown
Unknown
Cardiovascular Diseases; Kidney Diseases; Liver Diseases; Marijuana Abuse; Substance-Related Disorders; Cocaine-Related Disorders; Opioid-Related Disorders; Peripheral Nervous System Diseases; Tobacco Use Disorder; Obesity
Unknown
Small molecule
Approved
RESPIRATORY
ORAL
Liver Diseases; Sinusitis; Bronchitis, Chronic; Ciliary Motility Disorders; Pulmonary Disease, Chronic Obstructive; Cystic Fibrosis; Respiratory Tract Diseases
Cystic fibrosis transmembrane conductance regulator positive modulator
Protein
Approved
Unknown
Unknown
Graft vs Host Disease; Kidney Diseases; Liver Diseases; Crohn Disease; HIV Infections; Hyperlipidemias; Malnutrition; Malabsorption Syndromes; Short Bowel Syndrome
Glucagon-like peptide 2 receptor agonist
Small molecule
Approved
OTHER
ORAL
Carcinoma, Non-Small-Cell Lung; Carcinoma, Pancreatic Ductal; Insulin Resistance; Leukemia, Biphenotypic, Acute; Malaria; Pancreatic Neoplasms; Precursor Cell Lymphoblastic Leukemia-Lymphoma; Leukemia, Myeloid, Acute; Neoplasms; Acquired Immunodeficiency Syndrome; Pneumonia, Pneumocystis; Severe Acute Respiratory Syndrome; HIV Infections; Infections
Cytochrome P450 3A inhibitor
Unknown
Approved
Unknown
Unknown
Unknown
Unknown
Small molecule
Approved
Unknown
Unknown
Unknown
Unknown
Small molecule
Approved
Unknown
Unknown
Unknown
Unknown