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Total: 10647
Small molecule
Approved
Unknown
Unknown
Anemia, Sickle Cell; Carcinoma, Hepatocellular; Carcinoma, Non-Small-Cell Lung; Colonic Neoplasms; HIV Infections; Leukemia, Myelomonocytic, Chronic; Liver Neoplasms; Lung Neoplasms; Lymphoma, Mantle-Cell; Melanoma; Nasopharyngeal Neoplasms; Neoplasms, Plasma Cell; Paraganglioma; Polycythemia Vera; Primary Myelofibrosis; Prostatic Neoplasms; Rectal Neoplasms; Skin Neoplasms; Breast Neoplasms; Bronchiolitis Obliterans Syndrome; Carcinoma, Renal Cell; Colorectal Neoplasms; Diffuse Intrinsic Pontine Glioma; Glioblastoma; Glioma; Graft vs Host Disease; Hematologic Neoplasms; Leukemia; Leukemia, Myelogenous, Chronic, BCR-ABL Positive; Leukemia, Myeloid, Acute; Leukemia, Plasma Cell; Lymphoma; Lymphoma, Large B-Cell, Diffuse; Lymphoma, Non-Hodgkin; Lymphoma, T-Cell, Cutaneous; Myelodysplastic Syndromes; Neuroendocrine Tumors; Pancreatic Neoplasms; Plasmacytoma; Precursor Cell Lymphoblastic Leukemia-Lymphoma; Prostatic Neoplasms, Castration-Resistant; Stomach Neoplasms; Thyroid Neoplasms; Waldenstrom Macroglobulinemia; Hodgkin Disease; Multiple Myeloma; Neoplasms
Unknown
Small molecule
Approved
Unknown
Unknown
Liver Diseases; Cystic Fibrosis
Cystic fibrosis transmembrane conductance regulator stabiliser
Small molecule
Approved
Unknown
Unknown
Carcinoma, Pancreatic Ductal; Central Nervous System Neoplasms; Glioblastoma; Kidney Diseases; Liver Diseases; Lymphoma; Rectal Neoplasms; Adenocarcinoma; Adenocarcinoma, Follicular; Adenocarcinoma of Lung; Adrenal Cortex Neoplasms; Biliary Tract Neoplasms; Breast Neoplasms; Carcinoma, Adenoid Cystic; Carcinoma, Merkel Cell; Carcinoma, Neuroendocrine; Kidney Neoplasms; Liver Neoplasms; Meningeal Carcinomatosis; Mesothelioma; Neuroendocrine Tumors; Osteosarcoma; Ovarian Neoplasms; Paraganglioma; Retroviridae Infections; Sarcoma; Sarcoma, Kaposi; Small Cell Lung Carcinoma; Stomach Neoplasms; Thymoma; Uterine Cervical Neoplasms; Vulvar Neoplasms; Carcinoma, Hepatocellular; Carcinoma, Non-Small-Cell Lung; Carcinoma, Renal Cell; Carcinoma, Squamous Cell; Cholangiocarcinoma; Colorectal Neoplasms; Endometrial Neoplasms; Esophageal Neoplasms; Melanoma; Thyroid Neoplasms; Urinary Bladder Neoplasms; Neoplasms
Unknown
Enzyme
Approved
Unknown
INJECTION
Hypophosphatasia
Pyrophosphate hydrolytic enzyme
Small molecule
Approved
Unknown
Unknown
Hepatitis C, Chronic
Nonstructural protein 5A inhibitor
Small molecule
Approved
Unknown
INTRAMUSCULAR
Psychotic Disorders; Schizophrenia
Dopamine D2 receptor partial agonist
Antibody
Approved
Unknown
INJECTION
Anemia, Aplastic; Anemia, Hemolytic; Carcinoma, Renal Cell; Glioblastoma; Graft vs Host Disease; Hodgkin Disease; Immune System Diseases; Lymphoma, Non-Hodgkin; Lymphoma, T-Cell, Cutaneous; Mycosis Fungoides; Prostatic Neoplasms; Alzheimer Disease; Anemia, Sickle Cell; Carcinoma, Non-Small-Cell Lung; Colorectal Neoplasms; Genital Neoplasms, Male; Glomerulonephritis; Glomerulonephritis, Membranoproliferative; Leukemia; Leukemia, Biphenotypic, Acute; Leukemia, Lymphocytic, Chronic, B-Cell; Leukemia, Lymphoid; Leukemia, Myeloid, Acute; Leukemia, Plasma Cell; Lupus Erythematosus, Systemic; Lupus Nephritis; Lymphoma; Lymphoma, Follicular; Lymphoma, Large B-Cell, Diffuse; Lymphoma, Mantle-Cell; Myelodysplastic Syndromes; Nephrotic Syndrome; Neuromyelitis Optica; Paraproteinemias; Plasmacytoma; POEMS Syndrome; Precursor Cell Lymphoblastic Leukemia-Lymphoma; Prostatic Neoplasms, Castration-Resistant; Purpura, Thrombocytopenic, Idiopathic; Waldenstrom Macroglobulinemia; Amyloidosis; Amyloidosis, Familial; Smoldering Multiple Myeloma; Multiple Myeloma; Neoplasms
Lymphocyte differentiation antigen CD38 inhibitor
Protein
Approved
DIABETES DRUGS & ENDOCRINOLOGY; OTHER
INJECTION
Hyperparathyroidism; Psoriasis; Osteoporosis; Hypocalcemia; Hypoparathyroidism; Osteoporosis, Postmenopausal
Parathyroid hormone receptor agonist
Protein
Approved
Unknown
SUBCUTANEOUS
Diabetes Mellitus, Type 1; Diabetes Mellitus, Type 2; Diabetes Mellitus
Insulin receptor agonist
Oligosaccharide
Approved
Unknown
Unknown
Hypersensitivity; Kidney Diseases; Obesity; Obesity, Morbid; Organophosphate Poisoning; Burns; Postoperative Complications; Postoperative Nausea and Vomiting; Prostatic Neoplasms, Castration-Resistant
Unknown
Antibody
Approved
Unknown
INJECTION
Infections; Clostridium Infections; Enterocolitis, Pseudomembranous
Toxin B inhibitor
Small molecule
Approved
Unknown
Unknown
Tourette Syndrome; Parkinson Disease; Depressive Disorder, Major; Neurodegenerative Diseases; Schizophrenia; Psychotic Disorders
Unknown
Small molecule
Approved
Unknown
VAGINAL
Diabetes Mellitus, Type 1; Sarcoma, Synovial; Crohn Disease; Depressive Disorder; Erectile Dysfunction; HIV Infections; Hot Flashes; Low Back Pain; Multiple Myeloma; Myotonic Dystrophy; Primary Ovarian Insufficiency; Stress Disorders, Post-Traumatic; Substance Withdrawal Syndrome; Addison Disease; Adrenal Insufficiency; Aging; Anorexia Nervosa; Breast Neoplasms; Genital Neoplasms, Female; Infertility; Lupus Erythematosus, Systemic; Malaria; Menopause; Sexual Dysfunction, Physiological; Skin Aging; Arthritis, Rheumatoid; Atrophic Vaginitis; Dysmenorrhea; Osteoarthritis; Pain
Unknown
Small molecule
Approved
Unknown
Unknown
Pain; Blood Coagulation Disorders; Cognitive Dysfunction; Hemorrhage; Hypotension; Pre-Eclampsia; Cardiovascular Diseases; Nasal Obstruction; Obesity
Unknown
Small molecule
Approved
Unknown
ORAL
Adenomatous Polyposis Coli; Cholestasis; Liver Diseases; Obesity; Pruritus; Barrett Esophagus; Cholangitis, Sclerosing; Hepatitis, Alcoholic; Lipodystrophy, Familial Partial; Non-alcoholic Fatty Liver Disease; Cholangitis; Liver Cirrhosis, Biliary
Bile acid receptor FXR agonist
Small molecule
Approved
Unknown
TOPICAL
Alopecia Areata; Dermatitis; Psoriasis; Scleroderma, Localized; Vitiligo; Dermatitis, Atopic; Eczema
Phosphodiesterase 4 inhibitor
Oligonucleotide
Approved
Unknown
INTRAVENOUS
Muscular Dystrophies; Muscular Dystrophy, Duchenne
Dystrophin pre-mRNA positive modulator
Small molecule
Approved
Unknown
Unknown
Carcinoma, Lobular; Glioma; Brain Neoplasms; Glioblastoma; Nasopharyngeal Carcinoma; Prostatic Neoplasms, Castration-Resistant; Paraganglioma; Prostatic Neoplasms; Radionuclide Imaging
Diagnostic agent
Antibody
Approved
Unknown
INJECTION
Adenocarcinoma; Glioma; Gliosarcoma; Idiopathic Pulmonary Fibrosis; Leukemia, Myelogenous, Chronic, BCR-ABL Positive; Leukemia, Myeloid, Acute; Multiple Myeloma; Myelodysplastic Syndromes; Paraganglioma; Rhabdomyosarcoma; Skin Neoplasms; Adrenal Cortex Neoplasms; Anus Neoplasms; Astrocytoma; Biliary Tract Neoplasms; Carcinoma; Carcinoma, Neuroendocrine; Carcinoma, Pancreatic Ductal; Cholangiocarcinoma; Colonic Neoplasms; Gallbladder Neoplasms; Gastrointestinal Stromal Tumors; Glioblastoma; Head and Neck Neoplasms; Hematologic Neoplasms; Hodgkin Disease; Kidney Neoplasms; Leukemia, Lymphocytic, Chronic, B-Cell; Liver Neoplasms; Lymphoma; Lymphoma, Follicular; Lymphoma, Large B-Cell, Diffuse; Lymphoma, Non-Hodgkin; Lymphoma, T-Cell, Cutaneous; Mycosis Fungoides; Neoplasm Metastasis; Oropharyngeal Neoplasms; Osteosarcoma; Pancreatic Neoplasms; Prostatic Neoplasms, Castration-Resistant; Rectal Neoplasms; Retroviridae Infections; Sarcoma; Sarcoma, Alveolar Soft Part; Sezary Syndrome; Stomach Neoplasms; Thyroid Neoplasms; Carcinoma, Hepatocellular; Carcinoma, Renal Cell; Carcinoma, Squamous Cell; Colorectal Neoplasms; Endometrial Neoplasms; Esophageal Neoplasms; Fallopian Tube Neoplasms; Melanoma; Mesothelioma; Ovarian Neoplasms; Peritoneal Neoplasms; Prostatic Neoplasms; Urinary Bladder Neoplasms; Urogenital Neoplasms; Uterine Cervical Neoplasms; Breast Neoplasms; Carcinoma, Non-Small-Cell Lung; Carcinoma, Transitional Cell; Lung Neoplasms; Neoplasms; Small Cell Lung Carcinoma; Triple Negative Breast Neoplasms; Urologic Neoplasms
Programmed cell death 1 ligand 1 inhibitor
Unknown
Approved
Unknown
Unknown
Heart Failure
Unknown
Small molecule
Approved
Unknown
OPHTHALMIC
Graft vs Host Disease; Conjunctivitis, Allergic; Dry Eye Syndromes; Eye Diseases
Integrin alpha-L/beta-2 (LFA-1) antagonist
Antibody
Approved
Unknown
INJECTION
Bronchitis; Hypereosinophilic Syndrome; Loiasis; Eosinophilic Esophagitis; Sinusitis; Substance-Related Disorders; Asthma; Lung Diseases, Obstructive
Interleukin-5 inhibitor
Antibody
Approved
Unknown
INJECTION
Anthrax
Protective antigen binding agent
Antibody
Approved
Unknown
INJECTION
Lichen Planus; Arthritis, Rheumatoid; Constriction, Pathologic; Depressive Disorder, Major; Diabetes Mellitus, Type 1; Guttate Psoriasis; Pemphigoid, Bullous; Pityriasis Rubra Pilaris; Pyoderma; Severe Acute Respiratory Syndrome; Spondylitis, Ankylosing; Arthritis, Psoriatic; Immune System Diseases; Psoriasis
Interleukin 17A inhibitor
Oligonucleotide
Approved
Unknown
Unknown
Muscular Atrophy, Spinal
Unknown
Small molecule
Approved
Unknown
INTRAVENOUS
Glucosephosphate Dehydrogenase Deficiency; Jaundice; Sepsis; Abscess; Malaria; Malaria, Falciparum; Severe Acute Respiratory Syndrome; Stress Disorders, Post-Traumatic; Tooth Diseases; Wounds and Injuries; Bipolar Disorder; Dysuria; Shock, Septic; Urinary Tract Infections
Reducing agent
Small molecule
Approved
Unknown
Unknown
Carcinoma, Non-Small-Cell Lung; Small Cell Lung Carcinoma; Biliary Tract Neoplasms; Breast Neoplasms; Carcinoma, Pancreatic Ductal; Endometrial Neoplasms; Hereditary Breast and Ovarian Cancer Syndrome; Leiomyosarcoma; Mesothelioma; Pancreatic Neoplasms; Retroviridae Infections; Stomach Neoplasms; Uterine Cervical Neoplasms; Fallopian Tube Neoplasms; Ovarian Neoplasms; Peritoneal Neoplasms; Prostatic Neoplasms, Castration-Resistant; Neoplasms
PARP 1, 2 and 3 inhibitor
Unknown
Approved
Unknown
Unknown
Aging; Breast Neoplasms; Diabetic Neuropathies; Kidney Diseases; Brain Concussion; Depressive Disorder, Major; Epilepsy; Fatty Liver; Inflammation; Liver Diseases; Lupus Erythematosus, Systemic; Multiple Sclerosis; Neoplasms; Non-alcoholic Fatty Liver Disease; Phobia, Social; Renal Insufficiency, Chronic; Arthritis, Rheumatoid; Asthma; Cardiovascular Diseases; Cholestasis; Coronary Disease; Depressive Disorder; Intestinal Diseases; Lipid Metabolism Disorders; Obesity
Supplement
Small molecule
Approved
Unknown
INTRAVENOUS; ORAL
Brain Neoplasms; Spinal Cord Injuries; Neuralgia, Postherpetic; Epilepsy, Absence; Unverricht-Lundborg Syndrome; Epilepsy; Seizures
Synaptic vesicle glycoprotein 2A modulator
Protein
Approved
Unknown
SUBCUTANEOUS
Diabetes Mellitus, Type 1; Parkinson Disease; Acute Coronary Syndrome; Diabetes Mellitus; Diabetes Mellitus, Type 2
Glucagon-like peptide 1 receptor agonist
Small molecule
Approved
Unknown
Unknown
Unknown
Unknown
Small molecule
Approved
Unknown
Unknown
Virus Diseases
Unknown
Protein
Approved
Unknown
Unknown
Unknown
Unknown
Small molecule
Approved
Unknown
ORAL
Amyloidosis, Familial; Burkitt Lymphoma; Carcinoma, Non-Small-Cell Lung; HIV Infections; Idiopathic Pulmonary Fibrosis; Kidney Diseases; Leukemia, Myelomonocytic, Chronic; Leukemia, Prolymphocytic; Lymphohistiocytosis, Hemophagocytic; Lymphoma, T-Cell, Cutaneous; Prostatic Neoplasms; Small Cell Lung Carcinoma; Amyloidosis; Blastic Plasmacytoid Dendritic Cell Neoplasm; Breast Neoplasms; Hematologic Neoplasms; Leukemia; Leukemia, Biphenotypic, Acute; Leukemia, Lymphoid; Leukemia, Monocytic, Acute; Leukemia, Myelogenous, Chronic, BCR-ABL Positive; Leukemia, Prolymphocytic, T-Cell; Leukemia, Promyelocytic, Acute; Lymphoma; Lymphoma, B-Cell, Marginal Zone; Lymphoma, Follicular; Lymphoma, Large B-Cell, Diffuse; Lymphoma, Large-Cell, Anaplastic; Lymphoma, Non-Hodgkin; Myeloproliferative Disorders; Precursor Cell Lymphoblastic Leukemia-Lymphoma; Precursor T-Cell Lymphoblastic Leukemia-Lymphoma; Waldenstrom Macroglobulinemia; Leukemia, Myeloid; Leukemia, Myeloid, Acute; Lymphoma, Mantle-Cell; Multiple Myeloma; Myelodysplastic Syndromes; Leukemia, Lymphocytic, Chronic, B-Cell; Neoplasms
Apoptosis regulator Bcl-2 inhibitor
Small molecule
Approved
Unknown
Unknown
Hepatitis C; Hepatitis C, Chronic
Nonstructural protein 5A inhibitor