Display Options:
Total: 1496
Small molecule
Approved
OTHER
ORAL
Osteomyelitis; Infections; Urinary Tract Infections
DNA inhibitor
Small molecule
Approved
OTHER
ORAL
Helminthiasis
Tubulin inhibitor
Small molecule
Approved
OTHER
ORAL
Diabetes Mellitus; Pain; Hemorrhage; Dysmenorrhea; Rheumatic Diseases
Cyclooxygenase inhibitor
Small molecule
Approved
DENTISTRY; OTHER
INJECTION; ORAL; PERIODONTAL
Malaria; Tennis Elbow; Graves Ophthalmopathy; Macular Degeneration; Mucositis; Telangiectasia, Hereditary Hemorrhagic; Chlamydia Infections; Periodontitis; Rosacea; Acne Vulgaris
Bacterial 70S ribosome inhibitor
Small molecule
Approved
OTHER
INJECTION; ORAL
Anxiety; Dementia; Depressive Disorder; Schizophrenia; Psychotic Disorders
Dopamine D2 receptor antagonist
Small molecule
Approved
OTHER
ORAL
Glaucoma; Urinary Bladder Neoplasms; Cardiovascular Diseases; Fibrosis; Heart Failure; Kidney Diseases; Nephrotic Syndrome; Pulmonary Edema
Sodium-(potassium)-chloride cotransporter 2 inhibitor
Small molecule
Approved
OTHER
ORAL
Erectile Dysfunction; Lymphoma, T-Cell, Cutaneous; Melanoma; Neurofibromatosis 2; Osteomyelitis; Rhinoscleroma; Adenomatous Polyposis Coli; Amyloid Neuropathies, Familial; Amyloidosis; Amyloidosis, Familial; Aneurysm; Aortic Aneurysm, Abdominal; Blepharitis; Carcinoma, Non-Small-Cell Lung; Colitis, Ulcerative; Colorectal Neoplasms; Crohn Disease; Cystic Fibrosis; Dermatitis; Diabetic Foot; Diabetic Retinopathy; Dry Eye Syndromes; Eczema; Emphysema; Eye Burns; Graves Ophthalmopathy; Immunoglobulin Light-chain Amyloidosis; Lichen Planus, Oral; Lung Diseases; Lymphoma, Follicular; Lymphoma, Non-Hodgkin; Mansonelliasis; Marfan Syndrome; Mycosis Fungoides; Myocardial Infarction; Neoplasms; Pain; Pancreatic Neoplasms; Parkinson Disease; Pelvic Inflammatory Disease; Periodontal Diseases; Plague; Reperfusion Injury; Seizures; Sezary Syndrome; Skin Diseases; Squamous Cell Carcinoma of Head and Neck; Alzheimer Disease; Arthritis, Reactive; Borrelia Infections; Chlamydia Infections; Elephantiasis, Filarial; Hemorrhage; Idiopathic Pulmonary Fibrosis; Leishmaniasis; Lyme Disease; Lymphoma; Osteoarthritis; Persian Gulf Syndrome; Pleural Effusion; Pulmonary Disease, Chronic Obstructive; Scrub Typhus; Severe Acute Respiratory Syndrome; Syphilis; Tuberculosis; Urethritis; Acne Vulgaris; Anthrax; Bacterial Infections; Brucellosis; Cholera; Gonorrhea; Infections; Malaria; Periodontitis; Pneumonia; Psittacosis; Rocky Mountain Spotted Fever; Rosacea; Spotted Fever Group Rickettsiosis; Tularemia; Typhus, Epidemic Louse-Borne
Bacterial 70S ribosome inhibitor
Small molecule
Approved
HEMATOLOGY; OTHER
ORAL
Hypertension, Pulmonary; Lung Neoplasms; Paraganglioma; beta-Thalassemia; Central Nervous System Neoplasms; Desmoid Tumors; Esophageal Neoplasms; Fibroma; Gliosarcoma; Head and Neck Neoplasms; Hemoglobin SC Disease; Leukemia, Myeloid, Acute; Lymphoma; Meningioma; Multiple Sclerosis; Muscular Atrophy, Spinal; Precursor Cell Lymphoblastic Leukemia-Lymphoma; Stomach Neoplasms; Thalassemia; Astrocytoma; Carcinoma; Glioblastoma; Hematologic Diseases; Hemochromatosis; Hemoglobinopathies; HIV Infections; Laryngeal Neoplasms; Leukemia; Leukemia, Promyelocytic, Acute; Mouth Neoplasms; Myelodysplastic Syndromes; Myeloproliferative Disorders; Paranasal Sinus Neoplasms; Pharyngeal Neoplasms; Polycythemia Vera; Primary Myelofibrosis; Stroke; Thrombocythemia, Essential; Anemia, Sickle Cell; Carcinoma, Squamous Cell; Leukemia, Myelogenous, Chronic, BCR-ABL Positive; Melanoma; Neoplasms
Ribonucleoside-diphosphate reductase RR1 inhibitor
Small molecule
Approved
OTHER
ORAL
Psychotic Disorders; Schizophrenia
Dopamine D2 receptor antagonist
Small molecule
Approved
OTHER
ORAL
Endometrial Neoplasms; Hemorrhage
Progesterone receptor agonist
Small molecule
Approved
OTHER
INJECTION; INTRAVENOUS; ORAL; RECTAL
Ankle Fractures; Arrhythmias, Cardiac; Brain Concussion; Cognition; Crohn Disease; Diabetes Mellitus; Diabetes Mellitus, Type 2; Drug-Related Side Effects and Adverse Reactions; Esophageal Neoplasms; Glaucoma; Glycogen Storage Disease Type II; Glycogen Storage Disease Type III; Hepatitis; Hepatitis B, Chronic; Immune System Diseases; Intervertebral Disc Degeneration; Leukemia, Lymphocytic, Chronic, B-Cell; Leukemia, Myelogenous, Chronic, BCR-ABL Positive; Mesothelioma; Nervous System Diseases; Obesity, Morbid; Parkinson Disease; Prostatic Neoplasms, Castration-Resistant; Pruritus; Purpura, Thrombocytopenic, Idiopathic; Tooth Diseases; Urinary Bladder Neoplasms; Anxiety; Arthritis, Rheumatoid; Borderline Personality Disorder; Brain Injuries; Breast Neoplasms; Carcinoma, Non-Small-Cell Lung; Cleft Palate; Diabetes Mellitus, Type 1; Digestive System Diseases; Fractures, Bone; Glioma; Graft vs Host Disease; Hypertension; Hypertrophy; Immunoglobulin G4-Related Disease; Kidney Neoplasms; Leukemia; Leukemia, Hairy Cell; Leukemia, Mast-Cell; Leukemia, Myeloid, Acute; Leukemia, T-Cell; Lymphoma; Lymphoma, Follicular; Lymphoma, Large B-Cell, Diffuse; Lymphoma, Non-Hodgkin; Melanoma; Mucositis; Myelodysplastic Syndromes; Neck Pain; Neuralgia; Precursor Cell Lymphoblastic Leukemia-Lymphoma; Precursor T-Cell Lymphoblastic Leukemia-Lymphoma; Pre-Eclampsia; Pulpitis; Rotator Cuff Injuries; Sinusitis; Tension-Type Headache; Tonsillitis; Abdominal Pain; Cancer Pain; Chronic Pain; Delirium; Diabetic Neuropathies; Ductus Arteriosus, Patent; Hemorrhage; HIV Infections; Hypospadias; Infections; Kidney Calculi; Kidney Diseases; Low Back Pain; Lupus Erythematosus, Systemic; Lupus Nephritis; Malaria; Malaria, Falciparum; Meningitis, Bacterial; Mucopolysaccharidosis I; Multiple Myeloma; Multiple Sclerosis; Myopia; Nausea; Neoplasms; Obesity; Osteoarthritis; Osteoarthritis, Hip; Osteoarthritis, Knee; Paget Disease, Extramammary; Pemphigus; Postoperative Nausea and Vomiting; Renal Colic; Respiratory Tract Infections; Scoliosis; Sepsis; Severe Acute Respiratory Syndrome; Streptococcal Infections; Vomiting; Wounds and Injuries; Acute Pain; Arthritis; Back Pain; Common Cold; Dysmenorrhea; Fever; Headache; Influenza, Human; Migraine Disorders; Muscle Cramp; Pain; Pharyngitis; Toothache
Anandamide amidohydrolase inhibitor
Small molecule
Approved
OTHER
ORAL
Dermatitis; Inflammatory Bowel Diseases; Mucopolysaccharidoses; Myelodysplastic Syndromes; Urticaria; Anemia, Sickle Cell; Gout; Hepatitis, Autoimmune; Idiopathic Pulmonary Fibrosis; Infertility; Leukemia, Myeloid, Acute; Lung Diseases; Lung Diseases, Interstitial; Pemphigoid, Bullous; Pemphigus; Precursor Cell Lymphoblastic Leukemia-Lymphoma; Anti-Neutrophil Cytoplasmic Antibody-Associated Vasculitis; Carcinoma, Hepatocellular; Cardiomyopathies; Churg-Strauss Syndrome; Colitis, Ulcerative; Crohn Disease; Eczema; Encephalomyelitis; Glomerulonephritis, IGA; Granulomatosis with Polyangiitis; Kidney Diseases; Lupus Erythematosus, Systemic; Lupus Nephritis; Microscopic Polyangiitis; Myasthenia Gravis; Neuromyelitis Optica; Pulmonary Fibrosis; Renal Insufficiency, Chronic; Takayasu Arteritis; Thrombocytopenia; Vasculitis; Arthritis, Rheumatoid; Delayed Graft Function; Immune System Diseases
Amidophosphoribosyltransferase inhibitor
Small molecule
Approved
NEUROLOGY DRUGS & NERVOUS SYSTEM; OTHER; PEDIATRICS
INTRAVENOUS; ORAL
Hepatitis B, Chronic; Parkinson Disease; Severe Acute Respiratory Syndrome; Cocaine-Related Disorders; Epilepsy, Reflex; HIV Infections; Nausea; Substance-Related Disorders; Anxiety; Dementia; Depressive Disorder; Schizophrenia; Bipolar Disorder; Epilepsies, Partial; Epilepsy; Glossopharyngeal Nerve Diseases; Seizures; Trigeminal Neuralgia
Sodium channel alpha subunit blocker
Small molecule
Approved
CANCER; NEUROLOGY DRUGS & NERVOUS SYSTEM; OTHER
BUCCAL; SUBLINGUAL; TRANSDERMAL
Burns; Opioid-Related Disorders; Respiratory Distress Syndrome; Brain Injuries; Breast Neoplasms; Delirium; Fractures, Bone; Hypospadias; Hypotension; Irritable Bowel Syndrome; Pregnancy; Pulpitis; Scoliosis; Subarachnoid Hemorrhage; Abscess; Adenoma; Aortic Coarctation; Diabetic Neuropathies; Liver Diseases; Low Back Pain; Lung Diseases; Migraine Disorders; Neoplasm Metastasis; Obesity; Obesity, Morbid; Osteoarthritis; Pancreatic Neoplasms; Renal Insufficiency, Chronic; Respiratory Insufficiency; Severe Acute Respiratory Syndrome; Sleep Apnea, Obstructive; Stomach Neoplasms; Acute Pain; Cancer Pain; Chronic Pain; Neoplasms; Pain
Mu opioid receptor agonist
Small molecule
Approved
OTHER
INJECTION
Brain Neoplasms; Glioblastoma; Leukemia, Plasma Cell; Paraganglioma; Polycythemia Vera; Primary Myelofibrosis; Thrombocythemia, Essential; Blast Crisis; Blastic Plasmacytoid Dendritic Cell Neoplasm; Burkitt Lymphoma; Central Nervous System Neoplasms; Hematologic Neoplasms; Leukemia, Lymphocytic, Chronic, B-Cell; Leukemia-Lymphoma, Adult T-Cell; Leukemia, Myelomonocytic, Juvenile; Lupus Erythematosus, Systemic; Lymphoma, AIDS-Related; Lymphoma, Large-Cell, Anaplastic; Lymphoma, T-Cell, Peripheral; Medulloblastoma; Meningitis, Aseptic; Multiple Sclerosis, Relapsing-Remitting; Myasthenia Gravis; Neoplasms, Plasma Cell; Neuromyelitis Optica; Neutropenia; Opsoclonus-Myoclonus Syndrome; Ovarian Neoplasms; Polyradiculoneuropathy, Chronic Inflammatory Demyelinating; Prostatic Neoplasms, Castration-Resistant; Sarcoma; Stiff-Person Syndrome; Anemia, Refractory; Anemia, Refractory, with Excess of Blasts; Breast Neoplasms; Graft vs Host Disease; Histiocytosis, Langerhans-Cell; Hodgkin Disease; Leukemia; Leukemia, Basophilic, Acute; Leukemia, Biphenotypic, Acute; Leukemia, Erythroblastic, Acute; Leukemia, Megakaryoblastic, Acute; Leukemia, Monocytic, Acute; Leukemia, Myelogenous, Chronic, BCR-ABL Positive; Leukemia, Myeloid; Leukemia, Myelomonocytic, Acute; Leukemia, Myelomonocytic, Chronic; Leukemia, Promyelocytic, Acute; Lymphoma; Lymphoma, Follicular; Lymphoma, Large B-Cell, Diffuse; Lymphoma, Mantle-Cell; Lymphoma, Non-Hodgkin; Malaria; Melanoma; Multiple Myeloma; Myelodysplastic Syndromes; Myeloproliferative Disorders; Precursor T-Cell Lymphoblastic Leukemia-Lymphoma; Sarcoma, Myeloid; Thrombosis; Leukemia, Lymphoid; Leukemia, Myeloid, Acute; Meningeal Carcinomatosis; Meningeal Neoplasms; Neoplasms; Precursor Cell Lymphoblastic Leukemia-Lymphoma
DNA inhibitor
Small molecule
Approved
OTHER
ORAL
Osteomyelitis; Bacterial Infections
70S ribosome inhibitor
Small molecule
Approved
OTHER
OPHTHALMIC
Unknown
Adrenergic receptor agonist
Small molecule
Approved
OTHER
ORAL
Unknown
Dopamine D2 receptor antagonist
Small molecule
Approved
OTHER
OPHTHALMIC
Eye Diseases
Glucocorticoid receptor agonist
Small molecule
Approved
OTHER
INJECTION; ORAL
Puberty, Precocious
Cytochrome P450 19A1 inhibitor
Unknown
Approved
OTHER
TOPICAL
Unknown
Unknown
Small molecule
Approved
OTHER
INJECTION
Arthritis, Rheumatoid; Joint Diseases; Pain; Osteoarthritis, Knee; Osteoarthritis
Glucocorticoid receptor agonist
Small molecule
Approved
OTHER
INJECTION; ORAL
Unknown
Dopamine D2 receptor antagonist
Small molecule
Approved
OTHER
ORAL
Central Nervous System Neoplasms; Head and Neck Neoplasms; Arthritis, Rheumatoid; Cystinuria; Hepatolenticular Degeneration; Inflammation; Rheumatic Diseases; Spondylitis
Copper chelating agent
Small molecule
Approved
OTHER
ORAL
Unknown
Bacterial penicillin-binding protein inhibitor
Small molecule
Approved
OTHER
INJECTION
Sarcoma; Sarcoma, Ewing; Neoplasms
DNA inhibitor
Small molecule
Approved
OTHER
ORAL
Prostatic Neoplasms, Castration-Resistant; Carcinoma; Adrenal Cortex Neoplasms; Neoplasms
Cytochrome P450 11A1 inhibitor
Small molecule
Approved
OTHER
INHALATION; ORAL
Amyotrophic Lateral Sclerosis; Asthma; Brain Injuries; Diabetic Retinopathy; Hypotension, Orthostatic; Tobacco Use Disorder; Tourette Syndrome; Albinism; Albinism, Oculocutaneous; Angelman Syndrome; Aphasia; Back Pain; Child Development Disorders, Pervasive; Chronic Pain; Cocaine-Related Disorders; Macular Degeneration; Pain; Retinitis Pigmentosa; Schizophrenia; Spinal Cord Injuries; Stress Disorders, Post-Traumatic; Amblyopia; Restless Legs Syndrome; Stroke; Parkinson Disease
Dopamine D3 receptor agonist
Small molecule
Approved
DERMATOLOGY; OTHER
ORAL; TOPICAL
Amyotrophic Lateral Sclerosis; Autistic Disorder; Glioblastoma; Hematologic Neoplasms; Hypercholesterolemia; Myelodysplastic-Myeloproliferative Diseases; Neoplasms, Plasma Cell; Anemia; Anti-Neutrophil Cytoplasmic Antibody-Associated Vasculitis; Carcinoma, Adenoid Cystic; Cholangitis, Sclerosing; Colorectal Neoplasms; Emphysema; Keratosis, Actinic; Kidney Neoplasms; Lung Neoplasms; Lymphoma; Melanoma; Multiple Myeloma; Neuroblastoma; Pancreatic Neoplasms; Prostatic Neoplasms; Prostatic Neoplasms, Castration-Resistant; Severe Acute Respiratory Syndrome; Small Cell Lung Carcinoma; Striae Distensae; Breast Neoplasms; Carcinoma, Basal Cell; Carcinoma, Non-Small-Cell Lung; Carcinoma, Squamous Cell; Leukemia; Leukemia, Myeloid, Acute; Myelodysplastic Syndromes; Myeloproliferative Disorders; Purpura, Thrombocytopenic, Idiopathic; Rosacea; Skin Neoplasms; Acne Vulgaris; Hyperpigmentation; Leukemia, Promyelocytic, Acute; Melanosis; Neoplasms
Retinoic acid receptor agonist
Small molecule
Approved
OTHER
ORAL
Astrocytoma; Brain Neoplasms; Carcinoma, Hepatocellular; Colorectal Neoplasms; Digestive System Neoplasms; Glioblastoma; Gliosarcoma; Neoplasms; Oligodendroglioma; Intracranial Hypertension; Meningitis, Cryptococcal; Candidiasis; Infections; Meningitis
Thymidylate synthase inhibitor
Small molecule
Approved
OTHER
ORAL
Adrenal Cortex Neoplasms; Carcinoma in Situ; Dementia; Head and Neck Neoplasms; HIV Wasting Syndrome; Pulmonary Disease, Chronic Obstructive; Uterine Neoplasms; Breast Neoplasms; Endometrial Neoplasms; Hot Flashes; Liver Neoplasms; Acquired Immunodeficiency Syndrome; Anorexia; Cachexia; Neoplasms; Primary Immunodeficiency Diseases
Progesterone receptor agonist
Small molecule
Approved
OTHER
ORAL
HIV Infections; Osteomyelitis; Acquired Immunodeficiency Syndrome; Meningitis; Tuberculosis, Multidrug-Resistant; Tuberculosis; Tuberculosis, Pulmonary
70S ribosome inhibitor
Small molecule
Approved
OTHER
TOPICAL
Psoriasis; Breast Neoplasms; Dermatitis, Atopic; Hemorrhoids; Skin Diseases
Glucocorticoid receptor agonist
Small molecule
Approved
OTHER
ORAL
Osteomyelitis; Bacterial Infections; Eye Infections
Bacterial dihydropteroate synthase inhibitor
Small molecule
Approved
OTHER
INJECTION; ORAL
Anti-Neutrophil Cytoplasmic Antibody-Associated Vasculitis; Arthritis, Rheumatoid; Carcinoma, Non-Small-Cell Lung; Constipation; Coronary Disease; Diabetes Mellitus; Diabetes Mellitus, Type 2; Endometriosis; Erectile Dysfunction; Essential Hypertension; Hematologic Neoplasms; Hepatitis B, Chronic; HIV Infections; Hodgkin Disease; Hypercalcemia; Hypertension, Pulmonary; Leukemia, Lymphocytic, Chronic, B-Cell; Lymphoma; Lymphoma, Non-Hodgkin; Melanoma; Mycoses; Nausea; Neoplasms; Non-alcoholic Fatty Liver Disease; Osteomyelitis; Pain; Parkinson Disease; Primary Myelofibrosis; Renal Insufficiency; Renal Insufficiency, Chronic; Respiratory Syncytial Virus Infections; Rhinoscleroma; Sepsis; Severe Acute Respiratory Syndrome; Thrombosis; Acquired Immunodeficiency Syndrome; Buruli Ulcer; Cystic Fibrosis; Multiple Sclerosis; Mycobacterium avium-intracellulare Infection; Onchocerciasis; Sarcoidosis; Alzheimer Disease; Arthritis, Reactive; Diarrhea; Endocarditis; Enterocolitis, Pseudomembranous; Infections; Leprosy; Meningitis; Multiple System Atrophy; Tuberculosis; Tuberculosis, Pulmonary
Bacterial DNA-directed RNA polymerase inhibitor