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Total: 10647
Small molecule
Approved
HEMATOLOGY; OTHER
ORAL
Hypertension, Pulmonary; Lung Neoplasms; beta-Thalassemia; Central Nervous System Neoplasms; Esophageal Neoplasms; Fibromatosis, Aggressive; Gliosarcoma; Head and Neck Neoplasms; Hemoglobin SC Disease; Leukemia, Myeloid, Acute; Lymphoma; Meningioma; Multiple Sclerosis; Muscular Atrophy, Spinal; Precursor Cell Lymphoblastic Leukemia-Lymphoma; Stomach Neoplasms; Carcinoma; Glioblastoma; Hematologic Diseases; Hemochromatosis; HIV Infections; Laryngeal Neoplasms; Leukemia; Leukemia, Promyelocytic, Acute; Mouth Neoplasms; Myelodysplastic Syndromes; Myeloproliferative Disorders; Paranasal Sinus Neoplasms; Pharyngeal Neoplasms; Polycythemia Vera; Primary Myelofibrosis; Stroke; Thrombocythemia, Essential; Anemia, Sickle Cell; Carcinoma, Squamous Cell; Leukemia, Myelogenous, Chronic, BCR-ABL Positive; Melanoma; Neoplasms
Ribonucleoside-diphosphate reductase RR1 inhibitor
Small molecule
Approved
OTHER
INJECTION; ORAL
Anxiety; Dementia; Depressive Disorder; Schizophrenia; Psychotic Disorders
Dopamine D2 receptor antagonist
Small molecule
Approved
Unknown
Unknown
Carcinoma, Hepatocellular; Thalassemia; Acute Kidney Injury; Anemia, Sickle Cell; Cerebral Hemorrhage; Diabetic Foot; Ischemic Stroke; Subarachnoid Hemorrhage; beta-Thalassemia; Hemochromatosis; Severe Acute Respiratory Syndrome
Unknown
Small molecule
Approved
Unknown
Unknown
Hordeolum
Cell membrane inhibitor
Small molecule
Approved
Unknown
Unknown
Osteomyelitis; Bacteremia; Gram-Positive Bacterial Infections; Bacterial Infections
Unknown
Small molecule
Approved
OTHER
ORAL
Inflammatory Bowel Diseases; Mucopolysaccharidoses; Myelodysplastic Syndromes; Urticaria; Anemia, Sickle Cell; Gout; Hepatitis, Autoimmune; Idiopathic Pulmonary Fibrosis; Infertility; Leukemia, Myeloid, Acute; Lung Diseases; Lung Diseases, Interstitial; Pemphigoid, Bullous; Pemphigus; Anti-Neutrophil Cytoplasmic Antibody-Associated Vasculitis; Carcinoma, Hepatocellular; Cardiomyopathies; Churg-Strauss Syndrome; Colitis, Ulcerative; Crohn Disease; Eczema; Glomerulonephritis, IGA; Granulomatosis with Polyangiitis; Lupus Erythematosus, Systemic; Lupus Nephritis; Microscopic Polyangiitis; Myasthenia Gravis; Neuromyelitis Optica; Pulmonary Fibrosis; Renal Insufficiency, Chronic; Takayasu Arteritis; Thrombocytopenia; Vasculitis; Arthritis, Rheumatoid; Immune System Diseases
Amidophosphoribosyltransferase inhibitor
Small molecule
Approved
CANCER; NEUROLOGY DRUGS & NERVOUS SYSTEM; OTHER
BUCCAL; SUBLINGUAL; TRANSDERMAL
Opioid-Related Disorders; Respiratory Distress Syndrome; Brain Injuries; Breast Neoplasms; Bronchial Spasm; Delirium; Fractures, Bone; Hypospadias; Hypotension; Irritable Bowel Syndrome; Pulpitis; Scoliosis; Subarachnoid Hemorrhage; Abscess; Adenoma; Diabetic Neuropathies; Liver Diseases; Low Back Pain; Neoplasm Metastasis; Obesity; Obesity, Morbid; Osteoarthritis; Pancreatic Neoplasms; Renal Insufficiency, Chronic; Respiratory Insufficiency; Sleep Apnea, Obstructive; Stomach Neoplasms; Acute Pain; Cancer Pain; Chronic Pain; Migraine Disorders; Neoplasms; Pain
Mu opioid receptor agonist
Small molecule
Approved
Unknown
Unknown
Brain Injuries; Mood Disorders; Attention Deficit Disorder with Hyperactivity; Cerebral Infarction; Cocaine-Related Disorders; Diabetes Mellitus, Type 2; Hepatitis C; Infections; Influenza, Human; Pain; Hepatitis C, Chronic; Multiple Sclerosis; Psychotic Disorders; Schizophrenia; Severe Acute Respiratory Syndrome; Parkinson Disease
Unknown
Small molecule
Approved
OTHER
INJECTION; INTRAVENOUS; ORAL; RECTAL
Ankle Fractures; Brain Concussion; Delirium; Glaucoma; Tooth Diseases; Anemia, Hemolytic, Autoimmune; Arrhythmias, Cardiac; Crohn Disease; Diabetes Mellitus, Type 2; Glycogen Storage Disease Type II; Hepatitis B, Chronic; Immune System Diseases; Intervertebral Disc Degeneration; Leukemia, Lymphocytic, Chronic, B-Cell; Leukemia, Myelogenous, Chronic, BCR-ABL Positive; Leukemia, Myeloid, Acute; Neoplasms; Nervous System Diseases; Obesity, Morbid; Parkinson Disease; Pruritus; Purpura, Thrombocytopenic, Idiopathic; Anxiety; Arthritis, Rheumatoid; Borderline Personality Disorder; Brain Injuries; Breast Neoplasms; Carcinoma, Non-Small-Cell Lung; Cleft Palate; Diabetes Mellitus, Type 1; Digestive System Diseases; Fractures, Bone; Glioma; Graft vs Host Disease; Hypertension; Hypertrophy; Immunoglobulin G4-Related Disease; Leukemia, Mast-Cell; Leukemia, T-Cell; Lymphoma; Lymphoma, Follicular; Lymphoma, Large B-Cell, Diffuse; Lymphoma, Non-Hodgkin; Melanoma; Mucositis; Neck Pain; Neuralgia; Precursor Cell Lymphoblastic Leukemia-Lymphoma; Precursor T-Cell Lymphoblastic Leukemia-Lymphoma; Pre-Eclampsia; Pulpitis; Renal Colic; Rotator Cuff Injuries; Sinusitis; Tension-Type Headache; Tonsillitis; Abdominal Pain; Chronic Pain; Diabetic Neuropathies; Ductus Arteriosus, Patent; Hemorrhage; HIV Infections; Hypospadias; Infections; Kidney Calculi; Kidney Diseases; Low Back Pain; Lupus Erythematosus, Systemic; Lupus Nephritis; Malaria; Meningitis, Bacterial; Multiple Myeloma; Multiple Sclerosis; Myopia; Nausea; Obesity; Osteoarthritis; Osteoarthritis, Hip; Osteoarthritis, Knee; Paget Disease, Extramammary; Pemphigus; Postoperative Nausea and Vomiting; Respiratory Tract Infections; Scoliosis; Sepsis; Severe Acute Respiratory Syndrome; Streptococcal Infections; Vomiting; Wounds and Injuries; Acute Pain; Arthritis; Back Pain; Common Cold; Dysmenorrhea; Fever; Headache; Influenza, Human; Migraine Disorders; Muscle Cramp; Pain; Pharyngitis; Toothache
Anandamide amidohydrolase inhibitor
Small molecule
Approved
NEUROLOGY DRUGS & NERVOUS SYSTEM; OTHER; PEDIATRICS
INTRAVENOUS; ORAL
Hepatitis B, Chronic; Cocaine-Related Disorders; Epilepsy, Reflex; HIV Infections; Nausea; Anxiety; Dementia; Depressive Disorder; Schizophrenia; Bipolar Disorder; Epilepsies, Partial; Epilepsy; Glossopharyngeal Nerve Diseases; Seizures; Trigeminal Neuralgia
Sodium channel alpha subunit blocker
Small molecule
Approved
OTHER
ORAL
Endometrial Neoplasms; Hemorrhage
Progesterone receptor agonist
Unknown
Approved
OTHER
TOPICAL
Unknown
Unknown
Small molecule
Approved
OTHER
OPHTHALMIC
Eye Diseases
Glucocorticoid receptor agonist
Small molecule
Unknown
Unknown
Unknown
Astrocytoma; Glioblastoma; Lymphoma, AIDS-Related; Brain Neoplasms; Central Nervous System Neoplasms; Lymphoma
DNA inhibitor
Small molecule
Approved
OTHER
INJECTION
Alopecia; Brain Neoplasms; Glioblastoma; Leukemia, Plasma Cell; Polycythemia Vera; Primary Myelofibrosis; Thrombocythemia, Essential; Blast Crisis; Burkitt Lymphoma; Central Nervous System Neoplasms; Hematologic Neoplasms; Leukemia, Lymphocytic, Chronic, B-Cell; Leukemia-Lymphoma, Adult T-Cell; Leukemia, Myelomonocytic, Juvenile; Lupus Erythematosus, Systemic; Lymphoma, AIDS-Related; Lymphoma, Large-Cell, Anaplastic; Lymphoma, T-Cell, Peripheral; Medulloblastoma; Meningitis, Aseptic; Multiple Sclerosis, Relapsing-Remitting; Myasthenia Gravis; Neuromyelitis Optica; Neutropenia; Opsoclonus-Myoclonus Syndrome; Ovarian Neoplasms; Polyradiculoneuropathy, Chronic Inflammatory Demyelinating; Prostatic Neoplasms, Castration-Resistant; Sarcoma; Stiff-Person Syndrome; Urinary Bladder, Overactive; Anemia, Refractory; Anemia, Refractory, with Excess of Blasts; Breast Neoplasms; Graft vs Host Disease; Histiocytosis, Langerhans-Cell; Hodgkin Disease; Leukemia; Leukemia, Basophilic, Acute; Leukemia, Biphenotypic, Acute; Leukemia, Erythroblastic, Acute; Leukemia, Megakaryoblastic, Acute; Leukemia, Monocytic, Acute; Leukemia, Myelogenous, Chronic, BCR-ABL Positive; Leukemia, Myelomonocytic, Acute; Leukemia, Myelomonocytic, Chronic; Leukemia, Promyelocytic, Acute; Lymphoma; Lymphoma, Follicular; Lymphoma, Large B-Cell, Diffuse; Lymphoma, Mantle-Cell; Lymphoma, Non-Hodgkin; Malaria; Melanoma; Multiple Myeloma; Myelodysplastic Syndromes; Myeloproliferative Disorders; Precursor T-Cell Lymphoblastic Leukemia-Lymphoma; Renal Insufficiency, Chronic; Sarcoma, Myeloid; Leukemia, Lymphoid; Leukemia, Myeloid, Acute; Meningeal Carcinomatosis; Neoplasms; Precursor Cell Lymphoblastic Leukemia-Lymphoma
DNA inhibitor
Small molecule
Approved
OTHER
INJECTION
Arthritis, Rheumatoid; Pain; Eye Diseases; Hemorrhoids; Lung Diseases, Obstructive; Nasal Obstruction; Osteoarthritis
Glucocorticoid receptor agonist
Small molecule
Approved
Unknown
Unknown
Glioblastoma; Central Nervous System Neoplasms; Hodgkin Disease; Lymphoma; Neoplasms
Unknown
Small molecule
Approved
OTHER
INJECTION; ORAL
Puberty, Precocious
Cytochrome P450 19A1 inhibitor
Small molecule
Approved
Unknown
Unknown
Osteomyelitis
Unknown
Small molecule
Approved
OTHER
ORAL
Unknown
Unknown
Small molecule
Approved
Unknown
Unknown
Osteomyelitis; Leishmaniasis; Leishmaniasis, Cutaneous; Leishmaniasis, Visceral
Unknown
Small molecule
Approved
Unknown
Unknown
Breast Neoplasms; Irritable Bowel Syndrome; Sleep Initiation and Maintenance Disorders; Anxiety; Dementia; Schizophrenia; Depressive Disorder; Pruritus
Unknown
Small molecule
Approved
Unknown
Unknown
Unknown
Unknown
Small molecule
Approved
Unknown
Unknown
Unknown
Unknown
Small molecule
Approved
OTHER
ORAL
Osteomyelitis; Bacterial Infections
70S ribosome inhibitor
Small molecule
Approved
OTHER
OPHTHALMIC
Unknown
Adrenergic receptor agonist
Small molecule
Approved
OTHER
INJECTION; ORAL
Unknown
Dopamine D2 receptor antagonist
Small molecule
Approved
OTHER
INJECTION
Sarcoma, Ewing; Neoplasms
DNA inhibitor
Small molecule
Approved
OTHER
ORAL
Central Nervous System Neoplasms; Arthritis, Rheumatoid; Cystinuria; Hepatolenticular Degeneration; Inflammation; Rheumatic Diseases; Spondylitis
Copper chelating agent
Small molecule
Approved
OTHER
ORAL
Unknown
Bacterial penicillin-binding protein inhibitor
Small molecule
Approved
Unknown
Unknown
Osteomyelitis; Dermatitis, Atopic; Epidermolysis Bullosa Dystrophica; Muscular Dystrophy, Duchenne; Pneumonia, Ventilator-Associated; Chorioamnionitis; Cystic Fibrosis; Diabetic Foot; Folliculitis; Leishmaniasis; Leishmaniasis, Cutaneous; Meniere Disease; Neoplasms; Plague; Breast Neoplasms; Cat-Scratch Disease; Colonic Neoplasms; Eczema; Infections; Pain; Rectal Neoplasms; Sepsis; Bacterial Infections; Eye Infections
Unknown
Small molecule
Unknown
Unknown
Unknown
Psychotic Disorders
Unknown
Small molecule
Approved
Unknown
Unknown
Hemorrhoids; Phobia, Social; Radius Fractures; Cognitive Dysfunction; Fatigue; Heart Arrest; Marijuana Abuse; Mental Disorders; Opioid-Related Disorders; Perceptual Disorders; Schizophrenia; Sepsis; Stroke; Substance-Related Disorders; Tobacco Use Disorder; Borderline Personality Disorder; Brain Injuries; Breast Neoplasms; Bronchial Spasm; Child Development Disorders, Pervasive; Cocaine-Related Disorders; Complex Regional Pain Syndromes; Coronavirus Infections; Depressive Disorder, Treatment-Resistant; Epilepsy; Fractures, Multiple; Heart Septal Defects, Ventricular; Hypertrophy; Ischemic Stroke; Lung Neoplasms; Obsessive-Compulsive Disorder; Paget Disease, Extramammary; Respiratory Distress Syndrome; Rett Syndrome; Severe Acute Respiratory Syndrome; Strabismus; Stress Disorders, Post-Traumatic; Subarachnoid Hemorrhage; Temporomandibular Joint Disorders; Alcoholism; Anemia, Sickle Cell; Bipolar Disorder; Chronic Pain; Delirium; Depression, Postpartum; Depressive Disorder; Depressive Disorder, Major; Fractures, Bone; Headache; Mucositis; Neoplasms; Neuralgia; Obesity, Morbid; Pain; Pharyngitis; Postoperative Complications; Renal Colic; Rib Fractures; Shock, Septic; Status Asthmaticus; Status Epilepticus; Suicidal Ideation; Wounds and Injuries
Unknown
Small molecule
Unknown
Unknown
Unknown
Pain; Postoperative Nausea and Vomiting; Psychotic Disorders
D2-like dopamine receptor antagonist
Small molecule
Approved
OTHER
INHALATION; ORAL
Brain Injuries; Amyotrophic Lateral Sclerosis; Asthma; Hypotension, Orthostatic; Tobacco Use Disorder; Tourette Syndrome; Albinism; Albinism, Oculocutaneous; Angelman Syndrome; Aphasia; Back Pain; Child Development Disorders, Pervasive; Cocaine-Related Disorders; Macular Degeneration; Pain; Retinitis Pigmentosa; Schizophrenia; Spinal Cord Injuries; Stress Disorders, Post-Traumatic; Amblyopia; Restless Legs Syndrome; Stroke; Parkinson Disease
Dopamine D3 receptor agonist